Company lists · Data refreshed September 2026

Top 24 Genetic disorder therapeutic companies based in Cambridge, United States

RevenueBase identified 41 genetic disorder therapeutic companies headquartered in Cambridge, United States as of September 2026 and tracks 4,373 professional contacts across them, including 2,954 with verified work emails. Cambridge is the largest hub.

This list covers genetic disorder therapeutic companies headquartered in Cambridge, United States, matched on what each company actually does as described in its own words. Ranked by team size, largest first. Every row shows the company's own description, its RevenueBase Smart Search rating, and when it was last checked. Data refreshed September 20, 2026.

Published by RevenueBase, a B2B data infrastructure company. This list was built with RevenueBase Smart Search, the natural-language company search RevenueBase customers use to build their own targeted lists and unlock verified emails and direct dials at the companies on them. How these lists are built and judged.

How to read this list HQ checked on every row RevenueBase Smart Search rating on every row Refreshed Sep 20, 2026 86% judged on-target in blind review
41Companies
4,373Contacts tracked
2,954Verified emails
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The 24 largest genetic disorder therapeutic companies based in Cambridge, United States

Ranked by team size
Top 24 of 41 genetic disorder therapeutic companies based in Cambridge, United States, ranked by team size, largest first. Data refreshed Sep 20, 2026. RevenueBase Smart Search rates how each company's information relates to genetic disorder therapeutic companies: strong evidence (its own description names it), partial (names part of it), indirect (matched on the rest of its profile rather than the description shown). Click a contact count to view that company's people.
#CompanyRevenueBase Smart SearchHeadquartersEmployeesContacts
1Strong evidenceCambridge, MA, United StatesHQ checked Sep 20, 2026501-1,0001,359 contacts →

Strong evidence

“Sarepta Therapeutics, headquartered in Cambridge, Massachusetts, is a global biotechnology company on an urgent mission: engineer precision genetic medicine for rare diseases that…”

Source: RevenueBase Database · checked Sep 20, 2026
2Strong evidenceCambridge, MA, United StatesHQ checked Sep 20, 2026501-1,000605 contacts →

Strong evidence

“Beam Therapeutics, launched in 2018, is pioneering the use of CRISPR base editing to develop a broad portfolio of advanced genetic medicines.”

Source: RevenueBase Database · checked Sep 20, 2026
3Partial evidenceCambridge, MA, United StatesHQ checked Sep 20, 2026201-500474 contacts →

Partial evidence

“Intellia Therapeutics is a leading clinical-stage biopharmaceutical company focused on revolutionizing medicine leveraging CRISPR gene editing and other core technologies.”

Source: RevenueBase Database · checked Sep 20, 2026
4Indirect evidenceCambridge, MA, United StatesHQ checked Sep 20, 202651-200325 contacts →

Indirect evidence

“Scholar Rock is a biopharmaceutical company that discovers, develops, and delivers life-changing therapies for people with serious diseases that have high unmet need.”

Source: RevenueBase Database · checked Sep 20, 2026
5Indirect evidenceCambridge, MA, United StatesHQ checked Sep 20, 2026201-500232 contacts →

Indirect evidence

“Prime Medicine was founded to bring the promise of gene editing to patients.”

Source: RevenueBase Database · checked Sep 20, 2026
6Indirect evidenceCambridge, MA, United StatesHQ checked Sep 20, 202651-200125 contacts →

Indirect evidence

“Arbor Biotechnologies is a next-generation gene editing company focused on discovering and developing potentially curative genomic medicines, with the most extensive toolbox of…”

Source: RevenueBase Database · checked Sep 20, 2026
7Partial evidenceCambridge, MA, United StatesHQ checked Sep 20, 202651-200115 contacts →

Partial evidence

“Obsidian Therapeutics is pioneering controllable cell and gene therapies to deliver transformative outcomes for patients with intractable diseases.”

Source: RevenueBase Database · checked Sep 20, 2026
8Indirect evidenceCambridge, MA, United StatesHQ checked Sep 20, 202651-200111 contacts →

Indirect evidence

“Korro Bio was founded to turn extraordinary scientific insights into life-altering new treatments for patients.”

Source: RevenueBase Database · checked Sep 20, 2026
9Partial evidenceCambridge, MA, United StatesHQ checked Sep 20, 202651-20084 contacts →

Partial evidence

“We are a clinical-stage biopharmaceutical company focused on improving the lives of patients with genetically defined diseases in areas of high unmet medical need, with an initial…”

Source: RevenueBase Database · checked Sep 20, 2026
10Partial evidenceCambridge, MA, United StatesHQ checked Sep 20, 202651-20063 contacts →

Partial evidence

“LifeMine Therapeutics is a clinical-stage biopharmaceutical company pioneering Top-Down Drug DiscoveryTM, which leverages evolutionary insights from fungi to unearth…”

Source: RevenueBase Database · checked Sep 20, 2026
11Partial evidenceCambridge, MA, United StatesHQ checked Sep 20, 202611-5046 contacts →

Partial evidence

“Spero Therapeutics is a clinical-stage biopharmaceutical company focused on advancing next-generation medicines in immunology and inflammation for patients with serious diseases…”

Source: RevenueBase Database · checked Sep 20, 2026
12Partial evidenceCambridge, MA, United StatesHQ checked Sep 20, 202611-5046 contacts →

Partial evidence

“Stylus Medicine is developing transformative in vivo genetic medicines to unlock cures.”

Source: RevenueBase Database · checked Sep 20, 2026
13Indirect evidenceCambridge, MA, United StatesHQ checked Sep 20, 202611-5038 contacts →

Indirect evidence

“Kytopen is focused on the development and commercialization of groundbreaking genome engineering platforms for expediting the discovery, development, and manufacture of…”

Source: RevenueBase Database · checked Sep 20, 2026
14Partial evidenceCambridge, MA, United StatesHQ checked Sep 20, 202611-5036 contacts →

Partial evidence

“Atavistik Bio is a clinical stage biotechnology company developing novel allosteric therapeutics, with an internal focus on rare hematology.”

Source: RevenueBase Database · checked Sep 20, 2026
15Indirect evidenceCambridge, MA, United StatesHQ checked Sep 20, 202651-20034 contacts →

Indirect evidence

“Syros is committed to developing new standards of care for the frontline treatment of patients with hematologic malignancies.”

Source: RevenueBase Database · checked Sep 20, 2026
16Strong evidenceCambridge, MA, United StatesHQ checked Sep 20, 202611-5025 contacts →

Strong evidence

“Modalis Therapeutics Corporation (Tokyo Mothers 4883) is developing precision genetic medicines through epigenetic gene modulation.”

Source: RevenueBase Database · checked Sep 20, 2026
17Indirect evidenceCambridge, MA, United StatesHQ checked Sep 20, 202651-20022 contacts →

Indirect evidence

“Synlogic is a clinical-stage biotechnology company advancing novel, oral, non-systemically absorbed biotherapeutics to transform the care of serious diseases in need of new…”

Source: RevenueBase Database · checked Sep 20, 2026
18Indirect evidenceCambridge, MA, United StatesHQ checked Sep 20, 202651-20020 contacts →

Indirect evidence

“Our vision is to bring personalized gene therapy to the world.”

Source: RevenueBase Database · checked Sep 20, 2026
19Indirect evidenceCambridge, MA, United StatesHQ checked Sep 20, 202611-5018 contacts →

Indirect evidence

“Targeting enzymes that control cancer cell state and fitness make cancer cells susceptible to intrinsic and immune-mediated killing but drugging these pathways has been limited by…”

Source: RevenueBase Database · checked Sep 20, 2026
20Indirect evidenceCambridge, MA, United StatesHQ checked Sep 20, 20261-1013 contacts →

Indirect evidence

“Skylark Bio Gene Therapy Hearing Solutions: We believe in the power of innovative medicines to improve human lives by eliminating sensory limitations.”

Source: RevenueBase Database · checked Sep 20, 2026
21Partial evidenceCambridge, MA, United StatesHQ checked Sep 20, 202611-506 contacts →

Partial evidence

“We are now Sumitomo Pharma America (SMPA), a science-based, technology-driven biopharmaceutical company focused on delivering therapeutic and scientific breakthroughs in areas of…”

Source: RevenueBase Database · checked Sep 20, 2026
22Strong evidenceCambridge, MA, United StatesHQ checked Sep 20, 202611-506 contacts →

Strong evidence

“Full Circles Therapeutics is transforming genome engineering with our unique, nonviral, targeted genomic integration technology to treat genetic diseases and cancer.”

Source: RevenueBase Database · checked Sep 20, 2026
23Indirect evidenceCambridge, MA, United StatesHQ checked Sep 20, 202651-2004 contacts →

Indirect evidence

“AavantiBio is a gene therapy company backed by a premier syndicate of life sciences investors including Perceptive Advisors, Bain Capital Life Sciences, and RA Capital Management…”

Source: RevenueBase Database · checked Sep 20, 2026
24Partial evidenceCambridge, MA, United StatesHQ checked Sep 20, 20261-104 contacts →

Partial evidence

“Headquartered in Cambridge, Massachusetts, Hunterian Medicine LLC is a gene-editing company working to cure genetic diseases by correcting DNA mutations using its innovative…”

Source: RevenueBase Database · checked Sep 20, 2026

Showing 24 of 41 genetic disorder therapeutic companies based in Cambridge, United States

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Genetic disorder therapeutic companies based in Cambridge, United States at a glance

As of Sep 20, 2026
67.6%Verified-email coverage
106.7Average contacts per company
11-50Median size (employees)
100.0%Largest-city concentration · Cambridge
Sep 20, 2026Page data refreshed

Companies by employee count

1-10
7
11-50
17
51-200
12
201-500
3
501-1,000
2

Email recency for this list is measured across the whole United States list rather than for Cambridge, so it is reported there. Company counts and contact totals on this page are exact for Cambridge, over 41 companies.

How this list was built

Company categories are rarely black and white. RevenueBase reads each company's own description of its business to decide whether it belongs among genetic disorder therapeutic companies, so some rows will be adjacent to the category rather than pure plays. The description and RevenueBase Smart Search rating on every row are there so you can check each match yourself.

Source
The RevenueBase company graph: 60 million companies and 398.9 million professional contacts resolved from primary sources, queried with RevenueBase Smart Search, the natural-language company search available to every RevenueBase user.
What qualifies
Companies headquartered in Cambridge, United States whose own description of what they do matches “genetic disorder therapeutic companies”. Matching reads each company's description, not its industry code or its name.
RevenueBase Smart Search
RevenueBase Smart Search is how this list is assembled and how each row is rated. RevenueBase's data engine and AI assess a company's LinkedIn profile, information supplied directly by the company, its website and other publicly available information, then relate it to a category defined in a user's own words. Each row is rated strong evidence (its own description names genetic disorder therapeutic companies), partial evidence (it names part of the category) or indirect evidence (the description shown names none of it and the match rests on the rest of the company's profile). The description supporting each rating is quoted on the row.
What we exclude
Companies whose own description does not clearly place them among genetic disorder therapeutic companies, and records with no verified work email. Companies headquartered outside Cambridge are excluded even when they keep an office there.
Match quality
In blind human judging of this matching method, 86% of matched companies were on target. Expect roughly 1 in 7 rows to be adjacent to the category rather than a pure play. Every row shows the company's own description and its RevenueBase Smart Search rating so you can judge each match yourself. Read the full methodology: how the lists are built, how the judging worked, and what the figure means.
Ranking
Team size, largest first: companies are ordered by the number of professionals RevenueBase tracks at each one. Employee ranges shown are reported bands, for context.
Verification
Every listed company carries at least one verified work email, 2,954 across the full list. Contacts re-verify on a rolling cadence, and each contact's own verification date is shown inside RevenueBase.
Refresh
This page's figures were pulled from the company graph on September 20, 2026. Lists refresh periodically as the graph is re-checked.
Corrections
Wrong category, wrong headquarters, or a company that has closed? Use “Report an issue” on any row. Reports go to the RevenueBase Data Team and feed back into the company graph.

Genetic disorder therapeutic companies by metro in the United States

Frequently asked

What is RevenueBase Smart Search?

RevenueBase Smart Search is how RevenueBase decides which companies belong on this list and how strongly each one fits. Its data engine and AI assess a company's LinkedIn profile, information supplied directly by the company, its website and other publicly available information, then relate it to the category the list is about. Each row is rated strong evidence when the company's own description names genetic disorder therapeutic companies, partial evidence when it names part of the category, and indirect evidence when the description shown names none of it and the match rests on the rest of the company's profile.

How many genetic disorder therapeutic companies are there based in Cambridge, United States?

RevenueBase identified 41 genetic disorder therapeutic companies headquartered in Cambridge, United States as of September 2026, matched on each company's own description of what it does rather than its industry code.

What is the largest company on this list?

Sarepta Therapeutics, headquartered in Cambridge, tops this list with the largest team on record.

Which city has the most genetic disorder therapeutic companies?

Cambridge leads with 41 headquartered companies, followed by Boston (36) and San Diego (33).

How do I get contact information for these companies?

A free RevenueBase account lets you run this exact search and work the top results, verified emails and direct dials included. Upgrading unlocks all 2,954 verified decision-maker contacts tracked across these 41 companies.

How current is this list?

The list refreshes periodically as the company graph is re-checked. This page's figures were pulled on September 20, 2026.

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About this data

RevenueBase is a B2B data infrastructure company. Its company graph covers 60 million companies and 398.9 million professional contacts, with emails verified on a rolling cadence rather than scraped once and left to decay. These company lists are generated directly from that graph with RevenueBase Smart Search, the same natural-language company search every RevenueBase user has: describe a market in plain words, get the companies that match, and add verified emails and direct dials for the people at them. It is the same data that powers RevenueBase's B2B data products, and a free account includes 500 credits to start. How these lists are built and judged.