Company lists · Data refreshed September 2026
Top 25 Genetic disorder therapeutic companies based in Boston, United States
RevenueBase identified 36 genetic disorder therapeutic companies headquartered in Boston, United States as of September 2026 and tracks 10,044 professional contacts across them, including 6,825 with verified work emails. Cambridge is the largest hub.
This list covers genetic disorder therapeutic companies headquartered in Boston, United States, matched on what each company actually does as described in its own words. Ranked by team size, largest first. Every row shows the company's own description, its RevenueBase Smart Search rating, and when it was last checked. Data refreshed September 19, 2026.
Published by RevenueBase, a B2B data infrastructure company. This list was built with RevenueBase Smart Search, the natural-language company search RevenueBase customers use to build their own targeted lists and unlock verified emails and direct dials at the companies on them. How these lists are built and judged.
The 25 largest genetic disorder therapeutic companies based in Boston, United States
Ranked by team size| # | Company | Contacts | |||
|---|---|---|---|---|---|
| 1 | 8,099 contacts → | ||||
Indirect evidence “Vertex is a global biotechnology company that invests in scientific innovation to create transformative medicines for people with serious diseases and has made significant…” Source: RevenueBase Database · checked Sep 19, 2026Thanks. The Data Team will review it. | |||||
| 2 | 373 contacts → | ||||
Partial evidence “Since its inception over a decade ago, CRISPR Therapeutics has evolved from a research-stage company advancing gene editing programs into a leader that celebrated the historic…” Source: RevenueBase Database · checked Sep 19, 2026Thanks. The Data Team will review it. | |||||
| 3 | 239 contacts → | ||||
Partial evidence “Headquartered in Boston’s Seaport community, Entrada Therapeutics is a clinical-stage biopharmaceutical company aiming to transform the lives of patients by establishing a new…” Source: RevenueBase Database · checked Sep 19, 2026Thanks. The Data Team will review it. | |||||
| 4 | 189 contacts → | ||||
Strong evidence “Verve Therapeutics, a wholly owned subsidiary of Eli Lilly and Company, is developing a new class of genetic medicines for cardiovascular disease with the potential to transform…” Source: RevenueBase Database · checked Sep 19, 2026Thanks. The Data Team will review it. | |||||
| 5 | 173 contacts → | ||||
Partial evidence “Tango Therapeutics is a clinical-stage biotechnology company dedicated to discovering novel drug targets and delivering the next generation of precision medicine for the treatment…” Source: RevenueBase Database · checked Sep 19, 2026Thanks. The Data Team will review it. | |||||
| 6 | 160 contacts → | ||||
Partial evidence “Solid Biosciences is a precision genetic medicine company focused on advancing a portfolio of gene therapy candidates targeting rare neuromuscular and cardiac diseases, including…” Source: RevenueBase Database · checked Sep 19, 2026Thanks. The Data Team will review it. | |||||
| 7 | 100 contacts → | ||||
Partial evidence “enGene (Nasdaq: ENGN) is a clinical-stage biotechnology company mainstreaming non-viral genetic medicines that can be delivered locally to the site of disease-starting with…” Source: RevenueBase Database · checked Sep 19, 2026Thanks. The Data Team will review it. | |||||
| 8 | 91 contacts → | ||||
Partial evidence “Jnana Therapeutics is a clinical-stage biotechnology company leveraging its next-generation chemoproteomics RAPID platform to discover medicines for highly validated…” Source: RevenueBase Database · checked Sep 19, 2026Thanks. The Data Team will review it. | |||||
| 9 | 69 contacts → | ||||
Partial evidence “Driven by our proprietary Enhanced Delivery Oligonucleotide (EDO) platform, we are creating a pipeline of disease-modifying therapeutics with the potential to safely and…” Source: RevenueBase Database · checked Sep 19, 2026Thanks. The Data Team will review it. | |||||
| 10 | 66 contacts → | ||||
Partial evidence “Kelonia is pioneering a new wave of genetic medicines using its next generation gene delivery platform.” Source: RevenueBase Database · checked Sep 19, 2026Thanks. The Data Team will review it. | |||||
| 11 | 62 contacts → | ||||
Partial evidence “We are a life sciences company that is building on over a decade of extensive research on the genetic mutations associated with cystic fibrosis.” Source: RevenueBase Database · checked Sep 19, 2026Thanks. The Data Team will review it. | |||||
| 12 | 55 contacts → | ||||
Partial evidence “Ascidian Therapeutics is redefining the treatment of disease by rewriting RNA.” Source: RevenueBase Database · checked Sep 19, 2026Thanks. The Data Team will review it. | |||||
| 13 | 53 contacts → | ||||
Partial evidence “Prilenia is a clinical-stage biotech company focused on developing novel treatments for neurodegenerative and neurodevelopmental disorders.” Source: RevenueBase Database · checked Sep 19, 2026Thanks. The Data Team will review it. | |||||
| 14 | 48 contacts → | ||||
Partial evidence “We are a biopharmaceutical company specializing in the development of novel therapeutics to treat rare metabolic diseases.” Source: RevenueBase Database · checked Sep 19, 2026Thanks. The Data Team will review it. | |||||
| 15 | 43 contacts → | ||||
Indirect evidence “Our mission is to develop groundbreaking therapies to reverse mitochondrial dysfunction by leveraging a deep mechanistic understanding of mitochondrial biology.” Source: RevenueBase Database · checked Sep 19, 2026Thanks. The Data Team will review it. | |||||
| 16 | 42 contacts → | ||||
Indirect evidence Source: RevenueBase Database · checked Sep 19, 2026Thanks. The Data Team will review it. | |||||
| 17 | 23 contacts → | ||||
Partial evidence “NextRNA Therapeutics, Inc.” Source: RevenueBase Database · checked Sep 19, 2026Thanks. The Data Team will review it. | |||||
| 18 | 18 contacts → | ||||
Strong evidence “ROME Therapeutics is developing novel therapies for cancer and autoimmune diseases by harnessing the power of the repeatome – vast stretches of uncharted genetic material that…” Source: RevenueBase Database · checked Sep 19, 2026Thanks. The Data Team will review it. | |||||
| 19 | 16 contacts → | ||||
Partial evidence “Expanding Therapeutic Potential with Novel Parvovirus Gene Therapy” Source: RevenueBase Database · checked Sep 19, 2026Thanks. The Data Team will review it. | |||||
| 20 | 14 contacts → | ||||
Partial evidence “Combining cutting edge science, experienced business leaders and innovators, Regel Therapeutics is leveraging its Targeted EpiEditing platform transform the lives of people living…” Source: RevenueBase Database · checked Sep 19, 2026Thanks. The Data Team will review it. | |||||
| 21 | 10 contacts → | ||||
Partial evidence “EveryONE Medicines is committed to developing individualized precision medicines targeting genetic variants causing fatal, neurodegenerative diseases unique to just a few or even…” Source: RevenueBase Database · checked Sep 19, 2026Thanks. The Data Team will review it. | |||||
| 22 | 9 contacts → | ||||
Partial evidence “Khora Therapeutics is a clinical stage precision oncology company focused on bringing transformative therapies to highest need patients around the world with a particular focus on…” Source: RevenueBase Database · checked Sep 19, 2026Thanks. The Data Team will review it. | |||||
| 23 | 7 contacts → | ||||
Indirect evidence “NIVIRON is a next-generation biotechnology company developing gene therapy technologies using artificial intelligence, which we integrate into all scientific and business…” Source: RevenueBase Database · checked Sep 19, 2026Thanks. The Data Team will review it. | |||||
| 24 | 3 contacts → | ||||
Indirect evidence “Neoclease is a biotechnology company pioneering AI-designed gene-editing therapies optimized for individual genes.” Source: RevenueBase Database · checked Sep 19, 2026Thanks. The Data Team will review it. | |||||
| 25 | 1 contacts → | ||||
Partial evidence “Novelion Therapeutics is a biopharmaceutical company dedicated to developing new standards of care for individuals living with rare diseases.” Source: RevenueBase Database · checked Sep 19, 2026Thanks. The Data Team will review it. | |||||
RevenueBase Smart Search
RevenueBase Smart Search assesses information from a company’s LinkedIn profile, information supplied directly by the company, its website, and other publicly available sources. It uses that information to rate how closely the company relates to this list’s category: genetic disorder therapeutic companies. Every row carries its rating and the description the rating was read from, so each one can be checked rather than taken on trust.
- Strong evidence
- The company's own public description of its business names genetic disorder therapeutic companies.
- Partial evidence
- Its own public description names part of genetic disorder therapeutic companies, so it works in or next to the category without describing itself that way.
- Indirect evidence
- The description shown does not name genetic disorder therapeutic companies. The match rests on the rest of the company's public profile rather than the one sentence quoted here, so this is the rating to check first.
RevenueBase Smart Search is how these lists are built: RevenueBase's data engine and AI assemble the companies that match a category defined in a user's own words, so a list can be about what companies actually do rather than about whichever industry code they were filed under.
Showing 25 of 36 genetic disorder therapeutic companies based in Boston, United States
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Genetic disorder therapeutic companies based in Boston, United States at a glance
As of Sep 19, 2026Companies by employee count
Email recency for this list is measured across the whole United States list rather than for Boston, so it is reported there. Company counts and contact totals on this page are exact for Boston, over 36 companies.
How this list was built
Company categories are rarely black and white. RevenueBase reads each company's own description of its business to decide whether it belongs among genetic disorder therapeutic companies, so some rows will be adjacent to the category rather than pure plays. The description and RevenueBase Smart Search rating on every row are there so you can check each match yourself.
- Source
- The RevenueBase company graph: 60 million companies and 398.9 million professional contacts resolved from primary sources, queried with RevenueBase Smart Search, the natural-language company search available to every RevenueBase user.
- What qualifies
- Companies headquartered in Boston, United States whose own description of what they do matches “genetic disorder therapeutic companies”. Matching reads each company's description, not its industry code or its name.
- RevenueBase Smart Search
- RevenueBase Smart Search is how this list is assembled and how each row is rated. RevenueBase's data engine and AI assess a company's LinkedIn profile, information supplied directly by the company, its website and other publicly available information, then relate it to a category defined in a user's own words. Each row is rated strong evidence (its own description names genetic disorder therapeutic companies), partial evidence (it names part of the category) or indirect evidence (the description shown names none of it and the match rests on the rest of the company's profile). The description supporting each rating is quoted on the row.
- What we exclude
- Companies whose own description does not clearly place them among genetic disorder therapeutic companies, and records with no verified work email. Companies headquartered outside Boston are excluded even when they keep an office there.
- Match quality
- In blind human judging of this matching method, 86% of matched companies were on target. Expect roughly 1 in 7 rows to be adjacent to the category rather than a pure play. Every row shows the company's own description and its RevenueBase Smart Search rating so you can judge each match yourself. Read the full methodology: how the lists are built, how the judging worked, and what the figure means.
- Ranking
- Team size, largest first: companies are ordered by the number of professionals RevenueBase tracks at each one. Employee ranges shown are reported bands, for context.
- Verification
- Every listed company carries at least one verified work email, 6,825 across the full list. Contacts re-verify on a rolling cadence, and each contact's own verification date is shown inside RevenueBase.
- Refresh
- This page's figures were pulled from the company graph on September 19, 2026. Lists refresh periodically as the graph is re-checked.
- Corrections
- Wrong category, wrong headquarters, or a company that has closed? Use “Report an issue” on any row. Reports go to the RevenueBase Data Team and feed back into the company graph.
Genetic disorder therapeutic companies by metro in the United States
- Genetic disorder therapeutic companies in Cambridge47
- Genetic disorder therapeutic companies in Boston36
- Genetic disorder therapeutic companies in San Diego35
Frequently asked
What is RevenueBase Smart Search?
RevenueBase Smart Search is how RevenueBase decides which companies belong on this list and how strongly each one fits. Its data engine and AI assess a company's LinkedIn profile, information supplied directly by the company, its website and other publicly available information, then relate it to the category the list is about. Each row is rated strong evidence when the company's own description names genetic disorder therapeutic companies, partial evidence when it names part of the category, and indirect evidence when the description shown names none of it and the match rests on the rest of the company's profile.
How many genetic disorder therapeutic companies are there based in Boston, United States?
RevenueBase identified 36 genetic disorder therapeutic companies headquartered in Boston, United States as of September 2026, matched on each company's own description of what it does rather than its industry code.
What is the largest company on this list?
Vertex Pharmaceuticals, headquartered in Boston, tops this list with the largest team on record.
Which city has the most genetic disorder therapeutic companies?
Cambridge leads with 47 headquartered companies, followed by Boston (36) and San Diego (35).
How do I get contact information for these companies?
A free RevenueBase account lets you run this exact search and work the top results, verified emails and direct dials included. Upgrading unlocks all 6,825 verified decision-maker contacts tracked across these 36 companies.
How current is this list?
The list refreshes periodically as the company graph is re-checked. This page's figures were pulled on September 19, 2026.
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Genetic disorder therapeutic companies by geography
- Genetic disorder therapeutic companies based in Cambridge, United States
- Genetic disorder therapeutic companies based in San Diego, United States
- Genetic disorder therapeutic companies based in Canada
- Genetic disorder therapeutic companies based in China
- Genetic disorder therapeutic companies based in France
- Genetic disorder therapeutic companies based in Spain
- Genetic disorder therapeutic companies based in Switzerland
- Genetic disorder therapeutic companies based in the United Kingdom
- Genetic disorder therapeutic companies based in the United States
About this data
RevenueBase is a B2B data infrastructure company. Its company graph covers 60 million companies and 398.9 million professional contacts, with emails verified on a rolling cadence rather than scraped once and left to decay. These company lists are generated directly from that graph with RevenueBase Smart Search, the same natural-language company search every RevenueBase user has: describe a market in plain words, get the companies that match, and add verified emails and direct dials for the people at them. It is the same data that powers RevenueBase's B2B data products, and a free account includes 500 credits to start. How these lists are built and judged.
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- Genetic disorder therapeutic companies based in Cambridge, United States
- Genetic disorder therapeutic companies based in San Diego, United States
- Genetic disorder therapeutic companies based in Canada
- Genetic disorder therapeutic companies based in China
- Genetic disorder therapeutic companies based in France
- Genetic disorder therapeutic companies based in Spain