Company lists · Data refreshed September 2026

Top 25 Genetic disorder therapeutic companies based in the United Kingdom

RevenueBase identified 48 genetic disorder therapeutic companies headquartered in the United Kingdom as of September 2026 and tracks 1,680 professional contacts across them, including 1,074 with verified work emails. London is the largest hub.

This list covers genetic disorder therapeutic companies headquartered in the United Kingdom, matched on what each company actually does as described in its own words. Ranked by team size, largest first. Every row shows the company's own description, its RevenueBase Smart Search rating, and when it was last checked. Data refreshed September 20, 2026.

Published by RevenueBase, a B2B data infrastructure company. This list was built with RevenueBase Smart Search, the natural-language company search RevenueBase customers use to build their own targeted lists and unlock verified emails and direct dials at the companies on them. How these lists are built and judged.

How to read this list HQ checked on every row RevenueBase Smart Search rating on every row Refreshed Sep 20, 2026 86% judged on-target in blind review
48Companies
1,680Contacts tracked
1,074Verified emails
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The 25 largest genetic disorder therapeutic companies based in the United Kingdom

Ranked by team size
Top 25 of 48 genetic disorder therapeutic companies based in the United Kingdom, ranked by team size, largest first. Data refreshed Sep 20, 2026. RevenueBase Smart Search rates how each company's information relates to genetic disorder therapeutic companies: strong evidence (its own description names it), partial (names part of it), indirect (matched on the rest of its profile rather than the description shown). Click a contact count to view that company's people.
#CompanyRevenueBase Smart SearchHeadquartersEmployeesContacts
1Partial evidenceLondon/new York, United KingdomHQ checked Sep 20, 202651-200398 contacts →

Partial evidence

“MeiraGTx (Nasdaq: MGTX) is a vertically integrated, clinical-stage genetic medicine company with a broad pipeline of late-stage clinical programs supported by end-to-end…”

Source: RevenueBase Database · checked Sep 20, 2026
2Strong evidenceLondon, United KingdomHQ checked Sep 20, 202651-200221 contacts →

Strong evidence

“Orchard Therapeutics, a Kyowa Kirin company, is a global gene therapy leader focused on ending the devastation caused by genetic and other severe diseases by discovering…”

Source: RevenueBase Database · checked Sep 20, 2026
3Indirect evidenceCambridge, United KingdomHQ checked Sep 20, 202651-200196 contacts →

Indirect evidence

“We’re committed to supporting patients and their caregivers in every way we can.”

Source: RevenueBase Database · checked Sep 20, 2026
4Partial evidenceStevenage, United KingdomHQ checked Sep 20, 202611-5098 contacts →

Partial evidence

“Spur Therapeutics is a clinical-stage biotechnology company focused on developing life-changing gene therapies for debilitating chronic conditions.”

Source: RevenueBase Database · checked Sep 20, 2026
5Indirect evidenceLondon, United KingdomHQ checked Sep 20, 202651-20092 contacts →

Indirect evidence

“Our 20-plus years of RNAi experience together with our validated mRNAi GOLD™ platform make us a partner of choice for pharmaceutical companies looking to access the benefits of…”

Source: RevenueBase Database · checked Sep 20, 2026
6Indirect evidenceCambridge, United KingdomHQ checked Sep 20, 2026201-50091 contacts →

Indirect evidence

“Horizon Discovery, formerly of PerkinElmer, and now part of the Revvity family, drives the application of gene editing and gene modulation to enable world-leading academic…”

Source: RevenueBase Database · checked Sep 20, 2026
7Partial evidenceLondon, United KingdomHQ checked Sep 20, 202651-20086 contacts →

Partial evidence

“Beacon Therapeutics is a clinical-stage biotechnology company dedicated to saving and restoring sight for people living with rare and prevalent ocular diseases.”

Source: RevenueBase Database · checked Sep 20, 2026
8Indirect evidenceHemel Hempstead, United KingdomHQ checked Sep 20, 2026201-50070 contacts →

Indirect evidence

“We are committed to transforming the lives of people affected by cancer or rare disease, globally.”

Source: RevenueBase Database · checked Sep 20, 2026
9Indirect evidenceLondon, United KingdomHQ checked Sep 20, 202611-5063 contacts →

Indirect evidence

“At AviadoBio, we are relentlessly chasing cures by translating groundbreaking science and precision delivery into life-changing medicines for people living with frontotemporal…”

Source: RevenueBase Database · checked Sep 20, 2026
10Indirect evidenceCambridge, United KingdomHQ checked Sep 20, 202651-20060 contacts →

Indirect evidence

“Healx is a mission-driven technology company pioneering the next generation of drug discovery in order to bring novel, effective treatments to rare disease patients around the…”

Source: RevenueBase Database · checked Sep 20, 2026
11Indirect evidenceOxford, United KingdomHQ checked Sep 20, 202611-5051 contacts →

Indirect evidence

“Nucleome was founded in 2019.”

Source: RevenueBase Database · checked Sep 20, 2026
12Strong evidenceLondon, United KingdomHQ checked Sep 20, 202611-5037 contacts →

Strong evidence

“Peptone is a therapeutics company that uses AI and an experimental physics product engine to design small molecules targeting the 6,200 intrinsically disordered human proteins…”

Source: RevenueBase Database · checked Sep 20, 2026
13Partial evidenceLondon, United KingdomHQ checked Sep 20, 202611-5026 contacts →

Partial evidence

“Harnessing an innate mechanism of gene activation, MiNA Therapeutics' platform enables the development of new medicines that restore normal function to patients’ cells.”

Source: RevenueBase Database · checked Sep 20, 2026
14Indirect evidenceCardiff, United KingdomHQ checked Sep 20, 202611-5021 contacts →

Indirect evidence

“Biodexa Pharmaceuticals PLC (listed on NASDAQ: BDRX) is a clinical stage biopharmaceutical company developing innovative products focused on the treatment or prevention of…”

Source: RevenueBase Database · checked Sep 20, 2026
15Partial evidenceAlderley Park, United KingdomHQ checked Sep 20, 20261-1016 contacts →

Partial evidence

“Pencil Biosciences is developing a truly innovative gene modulation technology that can have an impact across a range of applications, including new therapeutic options for…”

Source: RevenueBase Database · checked Sep 20, 2026
16Indirect evidenceStevenage, United KingdomHQ checked Sep 20, 202651-20013 contacts →

Indirect evidence

“Freeline is a clinical-stage biotechnology company focused on developing transformative gene therapies for chronic debilitating diseases.”

Source: RevenueBase Database · checked Sep 20, 2026
17Indirect evidenceGlasgow, United KingdomHQ checked Sep 20, 202611-5011 contacts →

Indirect evidence

“Mironid Limited is an innovative new drug discovery company that develops proprietary drug candidate molecules by modulating the activity of key cell signalling proteins.”

Source: RevenueBase Database · checked Sep 20, 2026
18Indirect evidenceStevenage, United KingdomHQ checked Sep 20, 20261-1010 contacts →

Indirect evidence

“Vaso Dynamics is a clinical stage biotech and pharmaceutical development company based in Stevenage and London, UK, focusing on developing innovative pharmaceutical products for…”

Source: RevenueBase Database · checked Sep 20, 2026
19Indirect evidenceStevenage, United KingdomHQ checked Sep 20, 202611-509 contacts →

Indirect evidence

“Plasticell is a biotechnology company that develops novel therapies through precise manipulation of stem cells and more differentiated cell types using award-winning combinatorial…”

Source: RevenueBase Database · checked Sep 20, 2026
20Partial evidenceLondon, United KingdomHQ checked Sep 20, 202611-508 contacts →

Partial evidence

“Axovia Therapeutics is dedicated to the research and development of novel AAV gene therapies that target key aspects of ciliopathies, addressing the devastating impact of the…”

Source: RevenueBase Database · checked Sep 20, 2026
21Partial evidenceOxford, United KingdomHQ checked Sep 20, 20261-108 contacts →

Partial evidence

“Oxford Drug Design, an advanced spinout from Oxford University, is an innovative biotechnology company discovering and developing novel therapeutics supported by pioneering…”

Source: RevenueBase Database · checked Sep 20, 2026
22Indirect evidenceOxford, United KingdomHQ checked Sep 20, 20261-107 contacts →

Indirect evidence

“Overview SynaptixBio is a rare disease biotech company that is pioneering ground-breaking treatments for severe leukodystrophies and other childhood neurodegenerative diseases.”

Source: RevenueBase Database · checked Sep 20, 2026
23Indirect evidenceMacclesfield, United KingdomHQ checked Sep 20, 20261-107 contacts →

Indirect evidence

“Nodus oncology is developing first and best-in-class molecules inhibiting novel targets within the DNA damage response and replication stress response.”

Source: RevenueBase Database · checked Sep 20, 2026
24Partial evidenceNewcastle Upon Tyne, United KingdomHQ checked Sep 20, 20261-105 contacts →

Partial evidence

“Mantara Health Ltd is a pharmacogenomics company which launched its genetic testing service in the UK in June 2022.”

Source: RevenueBase Database · checked Sep 20, 2026
25Indirect evidenceCambridge, United KingdomHQ checked Sep 20, 20261-105 contacts →

Indirect evidence

“EpilepsyGTx is a late preclinical-stage biotech developing cutting-edge gene therapies that will transform the management of focal refractory epilepsy (FRE).”

Source: RevenueBase Database · checked Sep 20, 2026

Showing 25 of 48 genetic disorder therapeutic companies based in the United Kingdom

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Genetic disorder therapeutic companies based in the United Kingdom at a glance

As of Sep 20, 2026
63.9%Verified-email coverage
35.0Average contacts per company
1-10Median size (employees)
31.2%Largest-city concentration · London
Sep 20, 2026Page data refreshed

Companies by employee count

1-10
24
11-50
11
51-200
9
201-500
4

Email recency for this list is measured worldwide rather than for United Kingdom, so it is reported there. Company counts and contact totals on this page are exact for United Kingdom, over 48 companies.

How this list was built

Company categories are rarely black and white. RevenueBase reads each company's own description of its business to decide whether it belongs among genetic disorder therapeutic companies, so some rows will be adjacent to the category rather than pure plays. The description and RevenueBase Smart Search rating on every row are there so you can check each match yourself.

Source
The RevenueBase company graph: 60 million companies and 398.9 million professional contacts resolved from primary sources, queried with RevenueBase Smart Search, the natural-language company search available to every RevenueBase user.
What qualifies
Companies headquartered in the United Kingdom whose own description of what they do matches “genetic disorder therapeutic companies”. Matching reads each company's description, not its industry code or its name.
RevenueBase Smart Search
RevenueBase Smart Search is how this list is assembled and how each row is rated. RevenueBase's data engine and AI assess a company's LinkedIn profile, information supplied directly by the company, its website and other publicly available information, then relate it to a category defined in a user's own words. Each row is rated strong evidence (its own description names genetic disorder therapeutic companies), partial evidence (it names part of the category) or indirect evidence (the description shown names none of it and the match rests on the rest of the company's profile). The description supporting each rating is quoted on the row.
What we exclude
Companies whose own description does not clearly place them among genetic disorder therapeutic companies, and records with no verified work email. Companies headquartered outside United Kingdom are excluded even when they keep an office there.
Match quality
In blind human judging of this matching method, 86% of matched companies were on target. Expect roughly 1 in 7 rows to be adjacent to the category rather than a pure play. Every row shows the company's own description and its RevenueBase Smart Search rating so you can judge each match yourself. Read the full methodology: how the lists are built, how the judging worked, and what the figure means.
Ranking
Team size, largest first: companies are ordered by the number of professionals RevenueBase tracks at each one. Employee ranges shown are reported bands, for context.
Verification
Every listed company carries at least one verified work email, 1,074 across the full list. Contacts re-verify on a rolling cadence, and each contact's own verification date is shown inside RevenueBase.
Refresh
This page's figures were pulled from the company graph on September 20, 2026. Lists refresh periodically as the graph is re-checked.
Corrections
Wrong category, wrong headquarters, or a company that has closed? Use “Report an issue” on any row. Reports go to the RevenueBase Data Team and feed back into the company graph.

Frequently asked

What is RevenueBase Smart Search?

RevenueBase Smart Search is how RevenueBase decides which companies belong on this list and how strongly each one fits. Its data engine and AI assess a company's LinkedIn profile, information supplied directly by the company, its website and other publicly available information, then relate it to the category the list is about. Each row is rated strong evidence when the company's own description names genetic disorder therapeutic companies, partial evidence when it names part of the category, and indirect evidence when the description shown names none of it and the match rests on the rest of the company's profile.

How many genetic disorder therapeutic companies are there based in the United Kingdom?

RevenueBase identified 48 genetic disorder therapeutic companies headquartered in the United Kingdom as of September 2026, matched on each company's own description of what it does rather than its industry code.

What is the largest company on this list?

Meiragtx, headquartered in York, tops this list with the largest team on record.

Which city has the most genetic disorder therapeutic companies?

London leads with 15 headquartered companies, followed by Cambridge (7) and Oxford (4).

How do I get contact information for these companies?

A free RevenueBase account lets you run this exact search and work the top results, verified emails and direct dials included. Upgrading unlocks all 1,074 verified decision-maker contacts tracked across these 48 companies.

How current is this list?

The list refreshes periodically as the company graph is re-checked. This page's figures were pulled on September 20, 2026.

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About this data

RevenueBase is a B2B data infrastructure company. Its company graph covers 60 million companies and 398.9 million professional contacts, with emails verified on a rolling cadence rather than scraped once and left to decay. These company lists are generated directly from that graph with RevenueBase Smart Search, the same natural-language company search every RevenueBase user has: describe a market in plain words, get the companies that match, and add verified emails and direct dials for the people at them. It is the same data that powers RevenueBase's B2B data products, and a free account includes 500 credits to start. How these lists are built and judged.