Company lists · Data refreshed September 2026
Top 25 Sickle cell disease therapy companies based in the United States
RevenueBase identified 87 company matches for sickle cell disease therapy companies associated with the United States as of September 2026 and tracks 12,487 professional contacts across them, including 7,073 with verified work emails. Cambridge is the largest hub.
This list covers company matches for sickle cell disease therapy companies associated with the United States, found by RevenueBase SmartSearch using the meaning of business descriptions in its company graph at Exact. Ranked by professionals tracked, largest first. Rows show recorded descriptions where available, Exact search membership and the snapshot date. Data refreshed September 22, 2026.
Published by RevenueBase, a B2B data infrastructure company. This list was built with RevenueBase SmartSearch, the natural-language company search RevenueBase customers use to build their own targeted lists and unlock verified emails and direct dials at the companies on them. How these lists are built and judged.
The 25 largest sickle cell disease therapy companies based in the United States
Ranked by team size| # | Company | Contacts | |||
|---|---|---|---|---|---|
| 1 | 8,099 contacts → | ||||
Exact match “Vertex is a global biotechnology company that invests in scientific innovation to create transformative medicines for people with serious diseases and has made significant…” Recorded in the RevenueBase company graph · Sep 22, 2026 · View company records in RevenueBase | |||||
| 2 | 1,313 contacts → | ||||
Exact match “For three decades, Ionis has invented medicines that bring better futures to people with serious diseases.” Recorded in the RevenueBase company graph · Sep 22, 2026 · View company records in RevenueBase | |||||
| 3 | 474 contacts → | ||||
Exact match “Intellia Therapeutics is a leading clinical-stage biopharmaceutical company focused on revolutionizing medicine leveraging CRISPR gene editing and other core technologies.” Recorded in the RevenueBase company graph · Sep 22, 2026 · View company records in RevenueBase | |||||
| 4 | 287 contacts → | ||||
Exact match “Sana Biotechnology is focused on utilizing engineered cells as medicines for patients.” Recorded in the RevenueBase company graph · Sep 22, 2026 · View company records in RevenueBase | |||||
| 5 | 236 contacts → | ||||
Exact match “4DMT is a leading late-stage biotechnology company advancing durable and disease-targeted therapeutics with potential to transform treatment paradigms and provide unprecedented…” Recorded in the RevenueBase company graph · Sep 22, 2026 · View company records in RevenueBase | |||||
| 6 | 139 contacts → | ||||
Exact match “Disc Medicine is a biopharmaceutical company dedicated to transforming the lives of patients with hematologic disorders.” Recorded in the RevenueBase company graph · Sep 22, 2026 · View company records in RevenueBase | |||||
| 7 | 125 contacts → | ||||
Exact match “Arbor Biotechnologies is a next-generation gene editing company focused on discovering and developing potentially curative genomic medicines, with the most extensive toolbox of…” Recorded in the RevenueBase company graph · Sep 22, 2026 · View company records in RevenueBase | |||||
| 8 | 111 contacts → | ||||
Exact match “Korro Bio was founded to turn extraordinary scientific insights into life-altering new treatments for patients.” Recorded in the RevenueBase company graph · Sep 22, 2026 · View company records in RevenueBase | |||||
| 9 | 82 contacts → | ||||
Exact match “Global Blood Therapeutics (GBT) is now part of Pfizer, and we look forward to continuing our mission on behalf of people living with sickle cell disease.” Recorded in the RevenueBase company graph · Sep 22, 2026 · View company records in RevenueBase | |||||
| 10 | 62 contacts → | ||||
Exact match “We are a team with decades of proven success in translating science from bench to bedside across many companies and medicines, in gene therapy and beyond.” Recorded in the RevenueBase company graph · Sep 22, 2026 · View company records in RevenueBase | |||||
| 11 | 56 contacts → | ||||
Exact match “Jasper Therapeutics is a biotechnology company on a mission to make safer and potentially curative therapy possible for more patients in need.” Recorded in the RevenueBase company graph · Sep 22, 2026 · View company records in RevenueBase | |||||
| 12 | 55 contacts → | ||||
Exact match “Ascidian Therapeutics is redefining the treatment of disease by rewriting RNA.” Recorded in the RevenueBase company graph · Sep 22, 2026 · View company records in RevenueBase | |||||
| 13 | 53 contacts → | ||||
Exact match “Jaguar Gene Therapy, LLC is dedicated to accelerating breakthroughs in gene therapy for patients suffering from severe genetic diseases including those that impact sizeable…” Recorded in the RevenueBase company graph · Sep 22, 2026 · View company records in RevenueBase | |||||
| 14 | 37 contacts → | ||||
Exact match Recorded description not available. Recorded in the RevenueBase company graph · Sep 22, 2026 · View company records in RevenueBase | |||||
| 15 | 36 contacts → | ||||
Exact match “Atavistik Bio is a clinical stage biotechnology company developing novel allosteric therapeutics, with an internal focus on rare hematology.” Recorded in the RevenueBase company graph · Sep 22, 2026 · View company records in RevenueBase | |||||
| 16 | 35 contacts → | ||||
Exact match “Novartis Gene Therapies (formerly AveXis) is reimagining medicine to transform the lives of people living with rare genetic diseases.” Recorded in the RevenueBase company graph · Sep 22, 2026 · View company records in RevenueBase | |||||
| 17 | 34 contacts → | ||||
Exact match “Syros is committed to developing new standards of care for the frontline treatment of patients with hematologic malignancies.” Recorded in the RevenueBase company graph · Sep 22, 2026 · View company records in RevenueBase | |||||
| 18 | 34 contacts → | ||||
Exact match “Immix Biopharma, Inc.(ImmixBio)(Nasdaq: IMMX) is a clinical-stage biopharmaceutical company trailblazing cell therapies in AL Amyloidosis and other autoimmune diseases.” Recorded in the RevenueBase company graph · Sep 22, 2026 · View company records in RevenueBase | |||||
| 19 | 33 contacts → | ||||
Exact match “American Gene Technologies® International Inc.(AGT™) is a private biotechnology company pursuing cures and treatments for infectious diseases, cancers, and monogenic disorders.” Recorded in the RevenueBase company graph · Sep 22, 2026 · View company records in RevenueBase | |||||
| 20 | 24 contacts → | ||||
Exact match “Headquartered in South Plainfield, New Jersey, Prolong Pharmaceuticals, LLC is developing products to treat several diseases and their debilitating comorbidities which cause…” Recorded in the RevenueBase company graph · Sep 22, 2026 · View company records in RevenueBase | |||||
| 21 | 21 contacts → | ||||
Exact match “ASC Therapeutics focuses on the development of curative therapies for rare diseases.” Recorded in the RevenueBase company graph · Sep 22, 2026 · View company records in RevenueBase | |||||
| 22 | 20 contacts → | ||||
Exact match “Our vision is to bring personalized gene therapy to the world.” Recorded in the RevenueBase company graph · Sep 22, 2026 · View company records in RevenueBase | |||||
| 23 | 19 contacts → | ||||
Exact match Recorded description not available. Recorded in the RevenueBase company graph · Sep 22, 2026 · View company records in RevenueBase | |||||
| 24 | 17 contacts → | ||||
Exact match “Homology Medicines is a genetic medicines company translating proprietary gene editing and gene therapy technologies into novel treatments for patients with rare diseases.” Recorded in the RevenueBase company graph · Sep 22, 2026 · View company records in RevenueBase | |||||
| 25 | 16 contacts → | ||||
Exact match “The Foundation for Sickle Cell Disease Research (FSCDR) is the first outpatient center in the United States exclusively dedicated to on treating patients living with sickle cell…” Recorded in the RevenueBase company graph · Sep 22, 2026 · View company records in RevenueBase | |||||
RevenueBase SmartSearch
Describe a niche business in your own words. RevenueBase SmartSearch compares the meaning of your description with company business descriptions compiled in the RevenueBase company graph. Exact, Similar, Related and Broad control how closely companies must fit.
This list uses Exact for “sickle cell disease therapy companies”. Each Exact match badge shows membership in that saved search; it is not an individual similarity score or a service-quality rating. Recorded descriptions are shown where available.
Showing 25 of 87 sickle cell disease therapy companies based in the United States
See the full list, filter by size, metro and specialty, and access 7,073 tracked professional contacts with verified work emails. Direct dials are available where recorded.
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Sickle cell disease therapy companies based in the United States at a glance
As of Sep 22, 2026Companies by employee count
Email recency for this list is measured worldwide rather than for United States, so it is reported there. Company counts and contact totals on this page are exact for United States, over 87 companies.
How this list was built
The recorded descriptions help you assess these company matches. Check a company’s website for its current services and locations.
- Source
- The RevenueBase company graph: 60 million companies and 398.9 million professional contacts resolved from primary sources, queried with RevenueBase SmartSearch, the natural-language company search available to every RevenueBase user.
- What qualifies
- Company records associated with the United States whose business descriptions match “sickle cell disease therapy companies” by meaning at the Exact setting. Descriptions are compiled in the RevenueBase company graph from public websites, profiles and company information where available; they are not guaranteed quotations from the company's website.
- RevenueBase SmartSearch
- Describe a niche company in your own words to find businesses by meaning. Exact, Similar, Related and Broad control the breadth of RevenueBase SmartSearch. This saved list uses Exact. Each row's Exact match badge shows inclusion in that search, not an individual score or a service-quality judgment.
- Public preview
- The public preview omits records without a verified work email. Where headquarters information is recorded, preview rows are also filtered to this page’s location. Dataset totals and geographic summaries describe the full matched records before these preview filters.
- Match quality
- RevenueBase's August 25, 2026 study assessed 4,198 description/company pairs across matching settings. The publisher reports 86% good or better at Exact. This evaluates the method across queries; it does not audit this individual list. Recorded company descriptions, where available, help you judge each match yourself. Read the full methodology: how the lists are built and what the study measures.
- Ranking
- Team size, largest first: companies are ordered by the number of professionals RevenueBase tracks at each one. Employee ranges shown are reported bands, for context.
- Verification
- Every displayed company carries at least one verified work email. RevenueBase tracks 7,073 professional contacts with verified work emails across the full matched dataset. Contacts re-verify on a rolling cadence, and each contact's own verification date is shown inside RevenueBase.
- Refresh
- This page's figures were pulled from the company graph on September 22, 2026. Lists refresh periodically as the graph is re-checked.
- Record context
- Company records and descriptions can change. Check the company's website for its current services and locations.
Frequently asked
What is RevenueBase SmartSearch?
RevenueBase SmartSearch finds niche companies by the meaning of their business descriptions in the RevenueBase company graph. Exact, Similar, Related and Broad control how closely companies must fit your description. This list uses Exact for “sickle cell disease therapy companies”; each Exact match badge shows search membership, not an individual similarity or quality score.
How many sickle cell disease therapy companies are there based in the United States?
RevenueBase identified 87 company matches for sickle cell disease therapy companies associated with the United States as of September 2026, using the meaning of business descriptions at Exact. This is the recorded matched set in the RevenueBase company graph.
What is the largest company on this list?
Vertex Pharmaceuticals tops the displayed preview by professional contacts tracked in RevenueBase. Recorded headquarters appear in the company rows.
Which city has the most sickle cell disease therapy companies?
Cambridge leads with 6 company records, followed by San Francisco (4) and Boston (3).
How do I get contact information for these companies?
A free RevenueBase account lets you run this exact search and work limited free results with 500 credits to start. Upgrading provides access to the 7,073 professional contacts with verified work emails tracked across these 87 companies; direct dials are available where recorded.
How current is this list?
The list refreshes periodically as the company graph is re-checked. This page's figures were pulled on September 22, 2026.
Ready to reach these companies? Verified emails and direct dials for all 87 sickle cell disease therapy companies based in the United States. Start with a free account, no credit card.
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About this data
RevenueBase is a B2B data infrastructure company. Its company graph covers 60 million companies and 398.9 million professional contacts, with emails verified on a rolling cadence rather than scraped once and left to decay. These company lists are generated directly from that graph with RevenueBase SmartSearch, the same natural-language company search every RevenueBase user has: describe a market in plain words, get the companies that match, and add verified emails and direct dials for the people at them. It is the same data that powers RevenueBase's B2B data products, and a free account includes 500 credits to start. How these lists are built and judged.
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Company intelligence · public preview
Top 25 sickle cell disease therapy companies based in the United States
Find companies in any niche.
Describe the businesses you want in your own words. RevenueBase SmartSearch matches company descriptions by meaning.
RevenueBase records 87 matching company records for sickle cell disease therapy companies based in the United States, with 12,487 tracked contacts and 7,073 verified work emails.
This public preview shows 25 selected records ordered by tracked contacts. RevenueBase SmartSearch finds company descriptions that match by meaning at Exact. Snapshot: September 22, 2026.
RevenueBase compiles business descriptions for niche-company discovery; each row shows a recorded excerpt where available. Adapt this search to find the companies and contacts you want.
Top 25 sickle cell disease therapy companies based in the United States
The public list shows selected company records with contact and verified-email coverage. Reported employee bands provide separate company-size context.
| # | Company | Headquarters on record | Reported employees | RevenueBase SmartSearch | Tracked contacts |
|---|---|---|---|---|---|
| 1 |  Vertex Pharmaceuticalsvrtx.comHQ: Boston, MA, United StatesReported employees: 5,001-10,000 | Boston, MA, United States | 5,001-10,000 | Exact match | 8,099 contacts → |
“Vertex is a global biotechnology company that invests in scientific innovation to create transformative medicines for people with serious diseases and has made significant…” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 2 | Ionis Pharmaceuticals, INCionis.com HQ: Carlsbad, CA, United StatesReported employees: 501-1,000 | Carlsbad, CA, United States | 501-1,000 | Exact match | 1,313 contacts → |
“For three decades, Ionis has invented medicines that bring better futures to people with serious diseases.” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 3 | Intellia Therapeutics, INCintelliatx.com HQ: Cambridge, MA, United StatesReported employees: 201-500 | Cambridge, MA, United States | 201-500 | Exact match | 474 contacts → |
“Intellia Therapeutics is a leading clinical-stage biopharmaceutical company focused on revolutionizing medicine leveraging CRISPR gene editing and other core technologies.” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 4 |  Sana Biotechnology, INCsana.comHQ: Seattle, WA, United StatesReported employees: 201-500 | Seattle, WA, United States | 201-500 | Exact match | 287 contacts → |
“Sana Biotechnology is focused on utilizing engineered cells as medicines for patients.” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 5 |  4d Molecular Therapeutics4dmoleculartherapeutics.comHQ: Emeryville, CA, United StatesReported employees: 51-200 | Emeryville, CA, United States | 51-200 | Exact match | 236 contacts → |
“4DMT is a leading late-stage biotechnology company advancing durable and disease-targeted therapeutics with potential to transform treatment paradigms and provide unprecedented…” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 6 | Disc Medicinediscmedicine.com HQ: Watertown, MA, United StatesReported employees: 51-200 | Watertown, MA, United States | 51-200 | Exact match | 139 contacts → |
“Disc Medicine is a biopharmaceutical company dedicated to transforming the lives of patients with hematologic disorders.” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 7 |  Arbor Biotechnologiesarbor.bioHQ: Cambridge, MA, United StatesReported employees: 51-200 | Cambridge, MA, United States | 51-200 | Exact match | 125 contacts → |
“Arbor Biotechnologies is a next-generation gene editing company focused on discovering and developing potentially curative genomic medicines, with the most extensive toolbox of…” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 8 | Korro Bio, INCkorrobio.com HQ: Cambridge, MA, United StatesReported employees: 51-200 | Cambridge, MA, United States | 51-200 | Exact match | 111 contacts → |
“Korro Bio was founded to turn extraordinary scientific insights into life-altering new treatments for patients.” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 9 | Global Blood Therapeuticsgbt.com HQ: South San Francisco, CA, United StatesReported employees: 201-500 | South San Francisco, CA, United States | 201-500 | Exact match | 82 contacts → |
“Global Blood Therapeutics (GBT) is now part of Pfizer, and we look forward to continuing our mission on behalf of people living with sickle cell disease.” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 10 |  Affinia Therapeuticsaffiniatx.comHQ: Waltham, MA, United StatesReported employees: 51-200 | Waltham, MA, United States | 51-200 | Exact match | 62 contacts → |
“We are a team with decades of proven success in translating science from bench to bedside across many companies and medicines, in gene therapy and beyond.” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 11 | Jasper Therapeuticsjaspertx.com HQ: Redwood City, CA, United StatesReported employees: 51-200 | Redwood City, CA, United States | 51-200 | Exact match | 56 contacts → |
“Jasper Therapeutics is a biotechnology company on a mission to make safer and potentially curative therapy possible for more patients in need.” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 12 |  Ascidian Therapeuticsascidian-tx.comHQ: Boston, MA, United StatesReported employees: 11-50 | Boston, MA, United States | 11-50 | Exact match | 55 contacts → |
“Ascidian Therapeutics is redefining the treatment of disease by rewriting RNA.” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 13 |  Jaguar Gene Therapyjaguargenetherapy.comHQ: Lake Forest, IL, United StatesReported employees: 51-200 | Lake Forest, IL, United States | 51-200 | Exact match | 53 contacts → |
“Jaguar Gene Therapy, LLC is dedicated to accelerating breakthroughs in gene therapy for patients suffering from severe genetic diseases including those that impact sizeable…” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 14 | Emmaus Life Sciences, INCemmausmedical.com HQ: Torrance, CA, United StatesReported employees: 11-50 | Torrance, CA, United States | 11-50 | Exact match | 37 contacts → |
No recorded description excerpt is available for this public record. | |||||
| 15 | Atavistik BIOatavistikbio.com HQ: Cambridge, MA, United StatesReported employees: 11-50 | Cambridge, MA, United States | 11-50 | Exact match | 36 contacts → |
“Atavistik Bio is a clinical stage biotechnology company developing novel allosteric therapeutics, with an internal focus on rare hematology.” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 16 |  Novartis Gene Therapiesnovartis.comHQ: United StatesReported employees: 1,001-5,000 | United States | 1,001-5,000 | Exact match | 35 contacts → |
“Novartis Gene Therapies (formerly AveXis) is reimagining medicine to transform the lives of people living with rare genetic diseases.” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 17 | Syros Pharmaceuticalssyros.com HQ: Cambridge, MA, United StatesReported employees: 51-200 | Cambridge, MA, United States | 51-200 | Exact match | 34 contacts → |
“Syros is committed to developing new standards of care for the frontline treatment of patients with hematologic malignancies.” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 18 | Immix Biopharma Nasdaq Immximmixbio.com HQ: Los Angeles, CA, United StatesReported employees: 11-50 | Los Angeles, CA, United States | 11-50 | Exact match | 34 contacts → |
“Immix Biopharma, Inc.(ImmixBio)(Nasdaq: IMMX) is a clinical-stage biopharmaceutical company trailblazing cell therapies in AL Amyloidosis and other autoimmune diseases.” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 19 |  American Gene Technologies International INCamericangene.comHQ: Rockville, MD, United StatesReported employees: 11-50 | Rockville, MD, United States | 11-50 | Exact match | 33 contacts → |
“American Gene Technologies® International Inc.(AGT™) is a private biotechnology company pursuing cures and treatments for infectious diseases, cancers, and monogenic disorders.” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 20 | Prolong Pharmaceuticalsprolongpharma.com HQ: South Plainfield, NJ, United StatesReported employees: 51-200 | South Plainfield, NJ, United States | 51-200 | Exact match | 24 contacts → |
“Headquartered in South Plainfield, New Jersey, Prolong Pharmaceuticals, LLC is developing products to treat several diseases and their debilitating comorbidities which cause…” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 21 | ASC Therapeuticsasctherapeutics.com HQ: Milpitas, CA, United StatesReported employees: 51-200 | Milpitas, CA, United States | 51-200 | Exact match | 21 contacts → |
“ASC Therapeutics focuses on the development of curative therapies for rare diseases.” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 22 |  Avrobioavrobio.comHQ: Cambridge, MA, United StatesReported employees: 51-200 | Cambridge, MA, United States | 51-200 | Exact match | 20 contacts → |
“Our vision is to bring personalized gene therapy to the world.” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 23 | Expression Therapeutics, INCexpressiontherapeutics.com HQ: Tucker, GA, United StatesReported employees: 11-50 | Tucker, GA, United States | 11-50 | Exact match | 19 contacts → |
No recorded description excerpt is available for this public record. | |||||
| 24 | Homology Medicines, INChomologymedicines.com HQ: Bedford, MA, United StatesReported employees: 51-200 | Bedford, MA, United States | 51-200 | Exact match | 17 contacts → |
“Homology Medicines is a genetic medicines company translating proprietary gene editing and gene therapy technologies into novel treatments for patients with rare diseases.” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 25 | HQ: Hollywood, FL, United StatesReported employees: 11-50 | Hollywood, FL, United States | 11-50 | Exact match | 16 contacts → |
“The Foundation for Sickle Cell Disease Research (FSCDR) is the first outpatient center in the United States exclusively dedicated to on treating patients living with sickle cell…” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
Showing 25 of 87 company matches
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Sickle cell disease therapy companies: dataset insights
September 22, 2026These summaries describe recorded coverage in this saved dataset. This page is derived from saved source records; per-contact mobile coverage and email-recency results are not established by this snapshot.
Reported company sizes
87 records in the displayed employee bands.
0 matching records are outside the displayed bands or do not have a displayed size. Bars show shares of the displayed bands.
Email recency for this list is measured worldwide rather than for United States, so it is reported there. Company counts and contact totals on this page are exact for United States, over 87 companies.
How this company list was built
Describe a niche in your own words: companies installing commercial solar, or manufacturers of sustainable packaging. RevenueBase SmartSearch finds companies whose compiled business descriptions match by meaning. This list is one saved example to adapt.
Where the company descriptions come from
RevenueBase compiles company information from public sources, including company websites and public professional profiles such as LinkedIn, alongside information supplied by companies. The short recorded excerpt shown here is separate from the complete business description used for matching; individual source URLs and collection dates are not provided in this public snapshot.
RevenueBase SmartSearch matching settings
- Exact
- Closest fits to the business described.
- Similar
- Similar businesses with a wider range of fits.
- Related
- Related businesses in and around the category.
- Broad
- A broader set of businesses connected to the description.
RevenueBase SmartSearch · Exact match identifies inclusion in this search's closest semantic matching setting. It is not a per-company confidence score, a literal keyword match, or a quality endorsement.
Selection, ordering and scope
The public list shows selected company records with contact and verified-email coverage. Reported employee bands provide separate company-size context.
This page is derived from saved source records; per-contact mobile coverage and email-recency results are not established by this snapshot.
Recorded company descriptions support research; check company websites for current services. The selected preview is ordered by tracked contacts and is not a list of the best service providers.
Snapshot: September 22, 2026.
RevenueBase is a B2B data infrastructure company. Its September 3, 2026 published methodology describes a graph of 60 million companies and 398.9 million professional contacts; these platform figures differ from this page's totals. Published methodology ↗
Questions about this company list
What does Exact match mean for sickle cell disease therapy companies?
The separate RevenueBase SmartSearch column identifies inclusion at the closest semantic matching preset. It is not a literal keyword match, a per-company confidence score or a quality endorsement. Changing the search form opens a new search in RevenueBase; it does not reclassify these saved rows.
How many sickle cell disease therapy companies did RevenueBase find based in the United States?
The saved snapshot records 87 matching company records, 12,487 tracked contacts and 7,073 verified emails. The public preview displays 25 selected records.
Where do the company descriptions come from?
RevenueBase compiles company information from public sources, including company websites and public professional profiles such as LinkedIn, alongside information supplied by companies. The short recorded excerpt shown here is separate from the complete business description used for matching; individual source URLs and collection dates are not provided in this public snapshot.
How are the public companies ordered?
The selected public records are ordered by contacts tracked in RevenueBase, highest first. Contact coverage is a prospecting measure, not an assessment of the company's services or quality.
How can I get contact information?
Select a company's contact count to open its filtered contacts in RevenueBase. Free signup is required and includes 500 credits and limited free results. Verified emails, direct dials and mobile numbers depend on available coverage.
How current is this list?
Snapshot: September 22, 2026. Review each company's website for current services and locations. A recorded business description does not establish that every company offers every service named in the search.
What do headquarters and employee bands mean?
These are recorded company-level fields, rather than a map of every branch or a count of specialists. Missing headquarters or employee bands are labeled; older records may show a location separately from recorded headquarters.
Build your next target company list
Adapt this niche search and work with available contacts in RevenueBase.
Related lists
Cite this list
RevenueBase Data Team. Top 25 sickle cell disease therapy companies based in the United States. Snapshot: September 22, 2026. https://revenuebase.ai/companies/sickle-cell-disease-therapy-companies/united-states.
This is a selected public preview of saved company records, rather than an independently verified census. Open the source page ↗
More company lists
- All company lists
- Lists by location
- Lists A-Z
- New lists
- AI companies based in the United States
- Cybersecurity companies based in the United States
- Manufacturing companies based in the United States
- Media companies based in the United States
- Oil and gas companies based in the United States
- Real estate companies based in the United States
Company intelligence · public preview
Top 25 sickle cell disease therapy companies based in the United States
RevenueBase records 87 matching company records for sickle cell disease therapy companies based in the United States, with 12,487 tracked contacts and 7,073 verified work emails.
This public preview shows 25 selected records ordered by tracked contacts. RevenueBase SmartSearch finds company descriptions that match by meaning at Exact. Snapshot: September 22, 2026.
RevenueBase compiles business descriptions for niche-company discovery; each row shows a recorded excerpt where available. Adapt this search to find the companies and contacts you want.
Top 25 sickle cell disease therapy companies based in the United States
The public list shows selected company records with contact and verified-email coverage. Reported employee bands provide separate company-size context.
| # | Company | Headquarters on record | Reported employees | RevenueBase SmartSearch | Tracked contacts |
|---|---|---|---|---|---|
| 1 | Vertex Pharmaceuticalsvrtx.com HQ: Boston, MA, United StatesReported employees: 5,001-10,000 | Boston, MA, United States | 5,001-10,000 | Exact match | 8,099 contacts → |
“Vertex is a global biotechnology company that invests in scientific innovation to create transformative medicines for people with serious diseases and has made significant…” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 2 | Ionis Pharmaceuticals, INCionis.com HQ: Carlsbad, CA, United StatesReported employees: 501-1,000 | Carlsbad, CA, United States | 501-1,000 | Exact match | 1,313 contacts → |
“For three decades, Ionis has invented medicines that bring better futures to people with serious diseases.” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 3 | Intellia Therapeutics, INCintelliatx.com HQ: Cambridge, MA, United StatesReported employees: 201-500 | Cambridge, MA, United States | 201-500 | Exact match | 474 contacts → |
“Intellia Therapeutics is a leading clinical-stage biopharmaceutical company focused on revolutionizing medicine leveraging CRISPR gene editing and other core technologies.” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 4 | Sana Biotechnology, INCsana.com HQ: Seattle, WA, United StatesReported employees: 201-500 | Seattle, WA, United States | 201-500 | Exact match | 287 contacts → |
“Sana Biotechnology is focused on utilizing engineered cells as medicines for patients.” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 5 | 4d Molecular Therapeutics4dmoleculartherapeutics.com HQ: Emeryville, CA, United StatesReported employees: 51-200 | Emeryville, CA, United States | 51-200 | Exact match | 236 contacts → |
“4DMT is a leading late-stage biotechnology company advancing durable and disease-targeted therapeutics with potential to transform treatment paradigms and provide unprecedented…” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 6 | Disc Medicinediscmedicine.com HQ: Watertown, MA, United StatesReported employees: 51-200 | Watertown, MA, United States | 51-200 | Exact match | 139 contacts → |
“Disc Medicine is a biopharmaceutical company dedicated to transforming the lives of patients with hematologic disorders.” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 7 | Arbor Biotechnologiesarbor.bio HQ: Cambridge, MA, United StatesReported employees: 51-200 | Cambridge, MA, United States | 51-200 | Exact match | 125 contacts → |
“Arbor Biotechnologies is a next-generation gene editing company focused on discovering and developing potentially curative genomic medicines, with the most extensive toolbox of…” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 8 | Korro Bio, INCkorrobio.com HQ: Cambridge, MA, United StatesReported employees: 51-200 | Cambridge, MA, United States | 51-200 | Exact match | 111 contacts → |
“Korro Bio was founded to turn extraordinary scientific insights into life-altering new treatments for patients.” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 9 | Global Blood Therapeuticsgbt.com HQ: South San Francisco, CA, United StatesReported employees: 201-500 | South San Francisco, CA, United States | 201-500 | Exact match | 82 contacts → |
“Global Blood Therapeutics (GBT) is now part of Pfizer, and we look forward to continuing our mission on behalf of people living with sickle cell disease.” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 10 | Affinia Therapeuticsaffiniatx.com HQ: Waltham, MA, United StatesReported employees: 51-200 | Waltham, MA, United States | 51-200 | Exact match | 62 contacts → |
“We are a team with decades of proven success in translating science from bench to bedside across many companies and medicines, in gene therapy and beyond.” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 11 | Jasper Therapeuticsjaspertx.com HQ: Redwood City, CA, United StatesReported employees: 51-200 | Redwood City, CA, United States | 51-200 | Exact match | 56 contacts → |
“Jasper Therapeutics is a biotechnology company on a mission to make safer and potentially curative therapy possible for more patients in need.” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 12 | Ascidian Therapeuticsascidian-tx.com HQ: Boston, MA, United StatesReported employees: 11-50 | Boston, MA, United States | 11-50 | Exact match | 55 contacts → |
“Ascidian Therapeutics is redefining the treatment of disease by rewriting RNA.” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 13 | Jaguar Gene Therapyjaguargenetherapy.com HQ: Lake Forest, IL, United StatesReported employees: 51-200 | Lake Forest, IL, United States | 51-200 | Exact match | 53 contacts → |
“Jaguar Gene Therapy, LLC is dedicated to accelerating breakthroughs in gene therapy for patients suffering from severe genetic diseases including those that impact sizeable…” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 14 | Emmaus Life Sciences, INCemmausmedical.com HQ: Torrance, CA, United StatesReported employees: 11-50 | Torrance, CA, United States | 11-50 | Exact match | 37 contacts → |
No recorded description excerpt is available for this public record. | |||||
| 15 | Atavistik BIOatavistikbio.com HQ: Cambridge, MA, United StatesReported employees: 11-50 | Cambridge, MA, United States | 11-50 | Exact match | 36 contacts → |
“Atavistik Bio is a clinical stage biotechnology company developing novel allosteric therapeutics, with an internal focus on rare hematology.” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 16 | Novartis Gene Therapiesnovartis.com HQ: United StatesReported employees: 1,001-5,000 | United States | 1,001-5,000 | Exact match | 35 contacts → |
“Novartis Gene Therapies (formerly AveXis) is reimagining medicine to transform the lives of people living with rare genetic diseases.” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 17 | Syros Pharmaceuticalssyros.com HQ: Cambridge, MA, United StatesReported employees: 51-200 | Cambridge, MA, United States | 51-200 | Exact match | 34 contacts → |
“Syros is committed to developing new standards of care for the frontline treatment of patients with hematologic malignancies.” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 18 | Immix Biopharma Nasdaq Immximmixbio.com HQ: Los Angeles, CA, United StatesReported employees: 11-50 | Los Angeles, CA, United States | 11-50 | Exact match | 34 contacts → |
“Immix Biopharma, Inc.(ImmixBio)(Nasdaq: IMMX) is a clinical-stage biopharmaceutical company trailblazing cell therapies in AL Amyloidosis and other autoimmune diseases.” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 19 | American Gene Technologies International INCamericangene.com HQ: Rockville, MD, United StatesReported employees: 11-50 | Rockville, MD, United States | 11-50 | Exact match | 33 contacts → |
“American Gene Technologies® International Inc.(AGT™) is a private biotechnology company pursuing cures and treatments for infectious diseases, cancers, and monogenic disorders.” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 20 | Prolong Pharmaceuticalsprolongpharma.com HQ: South Plainfield, NJ, United StatesReported employees: 51-200 | South Plainfield, NJ, United States | 51-200 | Exact match | 24 contacts → |
“Headquartered in South Plainfield, New Jersey, Prolong Pharmaceuticals, LLC is developing products to treat several diseases and their debilitating comorbidities which cause…” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 21 | ASC Therapeuticsasctherapeutics.com HQ: Milpitas, CA, United StatesReported employees: 51-200 | Milpitas, CA, United States | 51-200 | Exact match | 21 contacts → |
“ASC Therapeutics focuses on the development of curative therapies for rare diseases.” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 22 | Avrobioavrobio.com HQ: Cambridge, MA, United StatesReported employees: 51-200 | Cambridge, MA, United States | 51-200 | Exact match | 20 contacts → |
“Our vision is to bring personalized gene therapy to the world.” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 23 | Expression Therapeutics, INCexpressiontherapeutics.com HQ: Tucker, GA, United StatesReported employees: 11-50 | Tucker, GA, United States | 11-50 | Exact match | 19 contacts → |
No recorded description excerpt is available for this public record. | |||||
| 24 | Homology Medicines, INChomologymedicines.com HQ: Bedford, MA, United StatesReported employees: 51-200 | Bedford, MA, United States | 51-200 | Exact match | 17 contacts → |
“Homology Medicines is a genetic medicines company translating proprietary gene editing and gene therapy technologies into novel treatments for patients with rare diseases.” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 25 | HQ: Hollywood, FL, United StatesReported employees: 11-50 | Hollywood, FL, United States | 11-50 | Exact match | 16 contacts → |
“The Foundation for Sickle Cell Disease Research (FSCDR) is the first outpatient center in the United States exclusively dedicated to on treating patients living with sickle cell…” Recorded description excerpt · September 22, 2026Open company data in RevenueBase ↗Free signup required. | |||||
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Sickle cell disease therapy companies: dataset insights
September 22, 2026These summaries describe recorded coverage in this saved dataset. This page is derived from saved source records; per-contact mobile coverage and email-recency results are not established by this snapshot.
Reported company sizes
87 records in the displayed employee bands.
0 matching records are outside the displayed bands or do not have a displayed size. Bars show shares of the displayed bands.
Email recency for this list is measured worldwide rather than for United States, so it is reported there. Company counts and contact totals on this page are exact for United States, over 87 companies.
How this company list was built
Describe a niche in your own words: companies installing commercial solar, or manufacturers of sustainable packaging. RevenueBase SmartSearch finds companies whose compiled business descriptions match by meaning. This list is one saved example to adapt.
Where the company descriptions come from
RevenueBase compiles company information from public sources, including company websites and public professional profiles such as LinkedIn, alongside information supplied by companies. The short recorded excerpt shown here is separate from the complete business description used for matching; individual source URLs and collection dates are not provided in this public snapshot.
RevenueBase SmartSearch matching settings
- Exact
- Closest fits to the business described.
- Similar
- Similar businesses with a wider range of fits.
- Related
- Related businesses in and around the category.
- Broad
- A broader set of businesses connected to the description.
RevenueBase SmartSearch · Exact match identifies inclusion in this search's closest semantic matching setting. It is not a per-company confidence score, a literal keyword match, or a quality endorsement.
Selection, ordering and scope
The public list shows selected company records with contact and verified-email coverage. Reported employee bands provide separate company-size context.
This page is derived from saved source records; per-contact mobile coverage and email-recency results are not established by this snapshot.
Recorded company descriptions support research; check company websites for current services. The selected preview is ordered by tracked contacts and is not a list of the best service providers.
Snapshot: September 22, 2026.
RevenueBase is a B2B data infrastructure company. Its September 3, 2026 published methodology describes a graph of 60 million companies and 398.9 million professional contacts; these platform figures differ from this page's totals. Published methodology ↗
Questions about this company list
What does Exact match mean for sickle cell disease therapy companies?
The separate RevenueBase SmartSearch column identifies inclusion at the closest semantic matching preset. It is not a literal keyword match, a per-company confidence score or a quality endorsement. Changing the search form opens a new search in RevenueBase; it does not reclassify these saved rows.
How many sickle cell disease therapy companies did RevenueBase find based in the United States?
The saved snapshot records 87 matching company records, 12,487 tracked contacts and 7,073 verified emails. The public preview displays 25 selected records.
Where do the company descriptions come from?
RevenueBase compiles company information from public sources, including company websites and public professional profiles such as LinkedIn, alongside information supplied by companies. The short recorded excerpt shown here is separate from the complete business description used for matching; individual source URLs and collection dates are not provided in this public snapshot.
How are the public companies ordered?
The selected public records are ordered by contacts tracked in RevenueBase, highest first. Contact coverage is a prospecting measure, not an assessment of the company's services or quality.
How can I get contact information?
Select a company's contact count to open its filtered contacts in RevenueBase. Free signup is required and includes 500 credits and limited free results. Verified emails, direct dials and mobile numbers depend on available coverage.
How current is this list?
Snapshot: September 22, 2026. Review each company's website for current services and locations. A recorded business description does not establish that every company offers every service named in the search.
What do headquarters and employee bands mean?
These are recorded company-level fields, rather than a map of every branch or a count of specialists. Missing headquarters or employee bands are labeled; older records may show a location separately from recorded headquarters.
Build your next target company list
Adapt this niche search and work with available contacts in RevenueBase.
Related lists
Cite this list
RevenueBase Data Team. Top 25 sickle cell disease therapy companies based in the United States. Snapshot: September 22, 2026. https://revenuebase.ai/companies/sickle-cell-disease-therapy-companies/united-states.
This is a selected public preview of saved company records, rather than an independently verified census. Open the source page ↗
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