Company lists · Data refreshed September 2026

Top 25 Sickle cell disease therapy companies worldwide

RevenueBase identified 170 sickle cell disease therapy companies worldwide as of September 2026 and tracks 13,746 professional contacts across them, including 7,753 with verified work emails. The United States is the largest market and Cambridge the largest hub.

This list covers sickle cell disease therapy companies worldwide, matched on what each company actually does as described in its own words. Ranked by team size, largest first. Every row shows the company's own description, its RevenueBase Smart Search rating, and when it was last checked. Data refreshed September 22, 2026. Country and city lists for sickle cell disease therapy companies follow the table.

Published by RevenueBase, a B2B data infrastructure company. This list was built with RevenueBase Smart Search, the natural-language company search RevenueBase customers use to build their own targeted lists and unlock verified emails and direct dials at the companies on them. How these lists are built and judged.

How to read this list HQ checked on every row RevenueBase Smart Search rating on every row Refreshed Sep 22, 2026 86% judged on-target in blind review
170Companies
13,746Contacts tracked
7,753Verified emails
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The 25 largest sickle cell disease therapy companies worldwide

Ranked by team size
Top 25 of 170 sickle cell disease therapy companies worldwide, ranked by team size, largest first. Data refreshed Sep 22, 2026. RevenueBase Smart Search rates how each company's information relates to sickle cell disease therapy companies: strong evidence (its own description names it), partial (names part of it), indirect (matched on the rest of its profile rather than the description shown). Click a contact count to view that company's people.
#CompanyRevenueBase Smart SearchHeadquartersEmployeesContacts
1Partial evidenceBoston, MA, United StatesHQ checked Sep 22, 20265,001-10,0008,099 contacts →

Partial evidence

“Vertex is a global biotechnology company that invests in scientific innovation to create transformative medicines for people with serious diseases and has made significant…”

Source: RevenueBase Database · checked Sep 22, 2026
2Partial evidenceCarlsbad, CA, United StatesHQ checked Sep 22, 2026501-1,0001,313 contacts →

Partial evidence

“For three decades, Ionis has invented medicines that bring better futures to people with serious diseases.”

Source: RevenueBase Database · checked Sep 22, 2026
3Partial evidenceCambridge, MA, United StatesHQ checked Sep 22, 2026201-500474 contacts →

Partial evidence

“Intellia Therapeutics is a leading clinical-stage biopharmaceutical company focused on revolutionizing medicine leveraging CRISPR gene editing and other core technologies.”

Source: RevenueBase Database · checked Sep 22, 2026
4Partial evidenceAmsterdam, United StatesHQ checked Sep 22, 202651-200349 contacts →

Partial evidence

“uniQure is delivering on the promise of gene therapy - single treatments with potentially curative results.”

Source: RevenueBase Database · checked Sep 22, 2026
5Partial evidenceSeattle, WA, United StatesHQ checked Sep 22, 2026201-500287 contacts →

Partial evidence

“Sana Biotechnology is focused on utilizing engineered cells as medicines for patients.”

Source: RevenueBase Database · checked Sep 22, 2026
6Strong evidenceBrisbane, CA, AustraliaHQ checked Sep 22, 2026201-500270 contacts →

Strong evidence

“For Sangamo Therapeutics, science is a means to develop new medicines with the potential to transform the lives of patients living with serious genetic diseases.”

Source: RevenueBase Database · checked Sep 22, 2026
7Strong evidenceEmeryville, CA, United StatesHQ checked Sep 22, 202651-200236 contacts →

Strong evidence

“4DMT is a leading late-stage biotechnology company advancing durable and disease-targeted therapeutics with potential to transform treatment paradigms and provide unprecedented…”

Source: RevenueBase Database · checked Sep 22, 2026
8Strong evidenceLondon, United KingdomHQ checked Sep 22, 202651-200221 contacts →

Strong evidence

“Orchard Therapeutics, a Kyowa Kirin company, is a global gene therapy leader focused on ending the devastation caused by genetic and other severe diseases by discovering…”

Source: RevenueBase Database · checked Sep 22, 2026
9Strong evidenceBergisch Gladbach, GermanyHQ checked Sep 22, 202651-200154 contacts →

Strong evidence

“Miltenyi Biomedicine is a biopharmaceutical company that develops innovative cell and gene therapies.”

Source: RevenueBase Database · checked Sep 22, 2026
10Indirect evidenceWatertown, MA, United StatesHQ checked Sep 22, 202651-200139 contacts →

Indirect evidence

“Disc Medicine is a biopharmaceutical company dedicated to transforming the lives of patients with hematologic disorders.”

Source: RevenueBase Database · checked Sep 22, 2026
11Indirect evidenceCambridge, MA, United StatesHQ checked Sep 22, 202651-200125 contacts →

Indirect evidence

“Arbor Biotechnologies is a next-generation gene editing company focused on discovering and developing potentially curative genomic medicines, with the most extensive toolbox of…”

Source: RevenueBase Database · checked Sep 22, 2026
12Indirect evidenceCambridge, MA, United StatesHQ checked Sep 22, 202651-200111 contacts →

Indirect evidence

“Korro Bio was founded to turn extraordinary scientific insights into life-altering new treatments for patients.”

Source: RevenueBase Database · checked Sep 22, 2026
13Strong evidenceSouth San Francisco, CA, United StatesHQ checked Sep 22, 2026201-50082 contacts →

Strong evidence

“Global Blood Therapeutics (GBT) is now part of Pfizer, and we look forward to continuing our mission on behalf of people living with sickle cell disease.”

Source: RevenueBase Database · checked Sep 22, 2026
14Partial evidenceWaltham, MA, United StatesHQ checked Sep 22, 202651-20062 contacts →

Partial evidence

“We are a team with decades of proven success in translating science from bench to bedside across many companies and medicines, in gene therapy and beyond.”

Source: RevenueBase Database · checked Sep 22, 2026
15Partial evidenceRedwood City, CA, United StatesHQ checked Sep 22, 202651-20056 contacts →

Partial evidence

“Jasper Therapeutics is a biotechnology company on a mission to make safer and potentially curative therapy possible for more patients in need.”

Source: RevenueBase Database · checked Sep 22, 2026
16Strong evidenceBoston, MA, United StatesHQ checked Sep 22, 202611-5055 contacts →

Strong evidence

“Ascidian Therapeutics is redefining the treatment of disease by rewriting RNA.”

Source: RevenueBase Database · checked Sep 22, 2026
17Strong evidenceLake Forest, IL, United StatesHQ checked Sep 22, 202651-20053 contacts →

Strong evidence

“Jaguar Gene Therapy, LLC is dedicated to accelerating breakthroughs in gene therapy for patients suffering from severe genetic diseases including those that impact sizeable…”

Source: RevenueBase Database · checked Sep 22, 2026
18Indirect evidenceModi'in, IsraelHQ checked Sep 22, 202611-5053 contacts →

Indirect evidence

“About BioLineRx BioLineRx Ltd.”

Source: RevenueBase Database · checked Sep 22, 2026
19Indirect evidenceTorrance, CA, United StatesHQ checked Sep 22, 202611-5037 contacts →

Indirect evidence

Source: RevenueBase Database · checked Sep 22, 2026
20Partial evidenceCambridge, MA, United StatesHQ checked Sep 22, 202611-5036 contacts →

Partial evidence

“Atavistik Bio is a clinical stage biotechnology company developing novel allosteric therapeutics, with an internal focus on rare hematology.”

Source: RevenueBase Database · checked Sep 22, 2026
21Partial evidenceDresden, GermanyHQ checked Sep 22, 202611-5035 contacts →

Partial evidence

“Seamless Therapeutics is changing the paradigm of gene editing through a pioneering approach to restore health in patients with severe conditions in a safe and precise manner.”

Source: RevenueBase Database · checked Sep 22, 2026
22Strong evidenceUnited StatesHQ checked Sep 22, 20261,001-5,00035 contacts →

Strong evidence

“Novartis Gene Therapies (formerly AveXis) is reimagining medicine to transform the lives of people living with rare genetic diseases.”

Source: RevenueBase Database · checked Sep 22, 2026
23Indirect evidenceCambridge, MA, United StatesHQ checked Sep 22, 202651-20034 contacts →

Indirect evidence

“Syros is committed to developing new standards of care for the frontline treatment of patients with hematologic malignancies.”

Source: RevenueBase Database · checked Sep 22, 2026
24Strong evidenceLos Angeles, CA, United StatesHQ checked Sep 22, 202611-5034 contacts →

Strong evidence

“Immix Biopharma, Inc.(ImmixBio)(Nasdaq: IMMX) is a clinical-stage biopharmaceutical company trailblazing cell therapies in AL Amyloidosis and other autoimmune diseases.”

Source: RevenueBase Database · checked Sep 22, 2026
25Partial evidenceRockville, MD, United StatesHQ checked Sep 22, 202611-5033 contacts →

Partial evidence

“American Gene Technologies® International Inc.(AGT™) is a private biotechnology company pursuing cures and treatments for infectious diseases, cancers, and monogenic disorders.”

Source: RevenueBase Database · checked Sep 22, 2026

Showing 25 of 170 sickle cell disease therapy companies worldwide

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Sickle cell disease therapy companies worldwide at a glance

As of Sep 22, 2026
56.4%Verified-email coverage
80.9Average contacts per company
11-50Median size (employees)
3.5%Largest-city concentration · Cambridge
Sep 22, 2026Page data refreshed

Companies by employee count

1-10
79
11-50
48
51-200
24
201-500
13
501-1,000
2
1,001-5,000
2
5,001-10,000
2

Email recency is reported on each country list linked below.

How this list was built

Company categories are rarely black and white. RevenueBase reads each company's own description of its business to decide whether it belongs among sickle cell disease therapy companies, so some rows will be adjacent to the category rather than pure plays. The description and RevenueBase Smart Search rating on every row are there so you can check each match yourself.

Source
The RevenueBase company graph: 60 million companies and 398.9 million professional contacts resolved from primary sources, queried with RevenueBase Smart Search, the natural-language company search available to every RevenueBase user.
Coverage
Every country. Country and city lists for sickle cell disease therapy companies are linked below.
What qualifies
Companies worldwide whose own description of what they do matches “sickle cell disease therapy companies”. Matching reads each company's description, not its industry code or its name.
RevenueBase Smart Search
RevenueBase Smart Search is how this list is assembled and how each row is rated. RevenueBase's data engine and AI assess a company's LinkedIn profile, information supplied directly by the company, its website and other publicly available information, then relate it to a category defined in a user's own words. Each row is rated strong evidence (its own description names sickle cell disease therapy companies), partial evidence (it names part of the category) or indirect evidence (the description shown names none of it and the match rests on the rest of the company's profile). The description supporting each rating is quoted on the row.
What we exclude
Companies whose own description does not clearly place them among sickle cell disease therapy companies, and records with no verified work email.
Match quality
In blind human judging of this matching method, 86% of matched companies were on target. Expect roughly 1 in 7 rows to be adjacent to the category rather than a pure play. Every row shows the company's own description and its RevenueBase Smart Search rating so you can judge each match yourself. Read the full methodology: how the lists are built, how the judging worked, and what the figure means.
Ranking
Team size, largest first: companies are ordered by the number of professionals RevenueBase tracks at each one. Employee ranges shown are reported bands, for context.
Verification
Every listed company carries at least one verified work email, 7,753 across the full list. Contacts re-verify on a rolling cadence, and each contact's own verification date is shown inside RevenueBase.
Refresh
This page's figures were pulled from the company graph on September 22, 2026. Lists refresh periodically as the graph is re-checked.
Corrections
Wrong category, wrong headquarters, or a company that has closed? Use “Report an issue” on any row. Reports go to the RevenueBase Data Team and feed back into the company graph.

Sickle cell disease therapy companies by location

1 lists · largest first

Every Sickle cell disease therapy companies list RevenueBase publishes, by country and city. Counts are matching companies in each list as of its own refresh date.

Countries

Frequently asked

What is RevenueBase Smart Search?

RevenueBase Smart Search is how RevenueBase decides which companies belong on this list and how strongly each one fits. Its data engine and AI assess a company's LinkedIn profile, information supplied directly by the company, its website and other publicly available information, then relate it to the category the list is about. Each row is rated strong evidence when the company's own description names sickle cell disease therapy companies, partial evidence when it names part of the category, and indirect evidence when the description shown names none of it and the match rests on the rest of the company's profile.

How many sickle cell disease therapy companies are there worldwide?

RevenueBase identified 170 sickle cell disease therapy companies worldwide as of September 2026, matched on each company's own description of what it does rather than its industry code.

What is the largest company on this list?

Vertex Pharmaceuticals, headquartered in Boston, tops this list with the largest team on record.

Which country has the most sickle cell disease therapy companies?

The United States leads with 87 companies. Every sickle cell disease therapy companies list by country and city is linked on this page.

Which city has the most sickle cell disease therapy companies?

Cambridge leads with 6 headquartered companies, followed by London (4) and San Francisco (4).

How do I get contact information for these companies?

A free RevenueBase account lets you run this exact search and work the top results, verified emails and direct dials included. Upgrading unlocks all 7,753 verified decision-maker contacts tracked across these 170 companies.

How current is this list?

The list refreshes periodically as the company graph is re-checked. This page's figures were pulled on September 22, 2026.

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About this data

RevenueBase is a B2B data infrastructure company. Its company graph covers 60 million companies and 398.9 million professional contacts, with emails verified on a rolling cadence rather than scraped once and left to decay. These company lists are generated directly from that graph with RevenueBase Smart Search, the same natural-language company search every RevenueBase user has: describe a market in plain words, get the companies that match, and add verified emails and direct dials for the people at them. It is the same data that powers RevenueBase's B2B data products, and a free account includes 500 credits to start. How these lists are built and judged.