Company lists · Data refreshed September 2026
Top 25 Gene therapy venture capital companies based in the United States
RevenueBase identified 254 gene therapy venture capital companies headquartered in the United States as of September 2026 and tracks 9,721 professional contacts across them, including 5,057 with verified work emails and 4,969 with mobile numbers. New York is the largest hub.
This list covers gene therapy venture capital companies headquartered in the United States, matched on what each company actually does as described in its own words. Ranked by team size, largest first. Every row shows the company's own description, how directly it supports the match, and when it was last checked. Data refreshed September 3, 2026.
Published by RevenueBase, a B2B data infrastructure company. This list was built with RevenueBase SmartSearch, the natural-language company search RevenueBase customers use to build their own targeted lists and unlock verified emails and direct dials at the companies on them. How these lists are built and judged.
The 25 largest gene therapy venture capital companies based in the United States
Ranked by team size| # | Company | Contacts | |||
|---|---|---|---|---|---|
| 1 | 821 | ||||
“We exist to bring transformative medicines to people living with genetic conditions.” Source: company website · checked Sep 3, 2026Thanks. The Data Team will review it. | |||||
| 2 | 507 | ||||
“AskBio Inc, a wholly owned and independently operated subsidiary of Bayer AG, is a fully integrated gene therapy company dedicated to developing life-saving medicines and changing…” Source: company website · checked Sep 3, 2026Thanks. The Data Team will review it. | |||||
| 3 | 450 | ||||
“Forge, a member of Ajinomoto Bio-Pharma Services, is a gene therapy development engine, focused on enabling access to life changing gene therapies and helping bring them from idea…” Source: company website · checked Sep 3, 2026Thanks. The Data Team will review it. | |||||
| 4 | RegenxbioStrong evidence | 392 | |||
“REGENXBIO is a leading clinical-stage biotechnology company seeking to improve lives through the curative potential of gene therapy.” Source: company website · checked Sep 3, 2026Thanks. The Data Team will review it. | |||||
| 5 | Sana Biotechnology, INCIndirect evidence | 285 | |||
“Sana Biotechnology is focused on utilizing engineered cells as medicines for patients.” Source: company website · checked Sep 3, 2026Thanks. The Data Team will review it. | |||||
| 6 | Sangamo Therapeutics, INCPartial evidence | 269 | |||
“For Sangamo Therapeutics, science is a means to develop new medicines with the potential to transform the lives of patients living with serious genetic diseases.” Source: company website · checked Sep 3, 2026Thanks. The Data Team will review it. | |||||
| 7 | Rocket PharmaceuticalsStrong evidence | 258 | |||
“Rocket Pharma (NASDAQ: RCKT) is a fully-integrated, clinical-stage company seeking gene therapy cures.” Source: company website · checked Sep 3, 2026Thanks. The Data Team will review it. | |||||
| 8 | 234 | ||||
“4DMT is a leading late-stage biotechnology company advancing durable and disease-targeted therapeutics with potential to transform treatment paradigms and provide unprecedented…” Source: company website · checked Sep 3, 2026Thanks. The Data Team will review it. | |||||
| 9 | 232 | ||||
“Cellectis is a global, clinical-stage biopharmaceutical company.” Source: company website · checked Sep 3, 2026Thanks. The Data Team will review it. | |||||
| 10 | Kriya Therapeutics, INCIndirect evidence | 209 | |||
“Our mission is to revolutionize medicine, with the ultimate goal of eliminating human suffering and enabling people to live without the burden of disease.” Source: company website · checked Sep 3, 2026Thanks. The Data Team will review it. | |||||
| 11 | Voyager Therapeutics, INCPartial evidence | 207 | |||
“Voyager Therapeutics, Inc.(Nasdaq: VYGR) is a biotechnology company dedicated to leveraging the power of human genetics to modify the course of – and ultimately cure –…” Source: company website · checked Sep 3, 2026Thanks. The Data Team will review it. | |||||
| 12 | Verve TherapeuticsPartial evidence | 188 | |||
“Verve Therapeutics, a wholly owned subsidiary of Eli Lilly and Company, is developing a new class of genetic medicines for cardiovascular disease with the potential to transform…” Source: company website · checked Sep 3, 2026Thanks. The Data Team will review it. | |||||
| 13 | 174 | ||||
“Adverum Biotechnologies (NASDAQ: ADVM) is a clinical-stage company that aims to establish gene therapy as a new standard of care for highly prevalent ocular diseases with the…” Source: company website · checked Sep 3, 2026Thanks. The Data Team will review it. | |||||
| 14 | Poseida Therapeutics, INCIndirect evidence | 172 | |||
“Poseida was acquired by Roche in early 2025 and is now part of the Roche Group.” Source: company website · checked Sep 3, 2026Thanks. The Data Team will review it. | |||||
| 15 | Solid BiosciencesStrong evidence | 160 | |||
“Solid Biosciences is a precision genetic medicine company focused on advancing a portfolio of gene therapy candidates targeting rare neuromuscular and cardiac diseases, including…” Source: company website · checked Sep 3, 2026Thanks. The Data Team will review it. | |||||
| 16 | 153 | ||||
“Encoded Therapeutics is creating one-time, disease-modifying gene therapies for pediatric central nervous system (CNS) disorders with its cell-selective targeting and regulation…” Source: company website · checked Sep 3, 2026Thanks. The Data Team will review it. | |||||
| 17 | 124 | ||||
“A2 is dedicated to pushing the boundaries of science to transform medicine and turn the tide on cancer.” Source: company website · checked Sep 3, 2026Thanks. The Data Team will review it. | |||||
| 18 | OcugenIndirect evidence | 120 | |||
“Ocugen, Inc.” Source: company website · checked Sep 3, 2026Thanks. The Data Team will review it. | |||||
| 19 | 116 | ||||
“Curie.Bio is a venture capital firm that helps founders discover and develop important new medicines.” Source: company website · checked Sep 3, 2026Thanks. The Data Team will review it. | |||||
| 20 | 115 | ||||
“Ascend is gene to GMP partner with deep expertise in advanced therapy development and commercialization.” Source: company website · checked Sep 3, 2026Thanks. The Data Team will review it. | |||||
| 21 | Obsidian TherapeuticsStrong evidence | 114 | |||
“Obsidian Therapeutics is pioneering controllable cell and gene therapies to deliver transformative outcomes for patients with intractable diseases.” Source: company website · checked Sep 3, 2026Thanks. The Data Team will review it. | |||||
| 22 | Neurogene INCIndirect evidence | 109 | |||
“Neurogene is accelerating development of new genetic medicines to people with devastating neurological diseases and their families.” Source: company website · checked Sep 3, 2026Thanks. The Data Team will review it. | |||||
| 23 | 108 | ||||
“Capsida Biotherapeutics Inc.” Source: company website · checked Sep 3, 2026Thanks. The Data Team will review it. | |||||
| 24 | 98 | ||||
“Ensoma /en’sōmə/ is derived from the Greek phrase “en soma,” meaning in the body.” Source: company website · checked Sep 3, 2026Thanks. The Data Team will review it. | |||||
| 25 | Spark Therapeutics, INCPartial evidence | 78 | |||
“At Spark® Therapeutics, we believe in a world where no life is limited by disease.” Source: company website · checked Sep 3, 2026Thanks. The Data Team will review it. | |||||
Showing 25 of 254 gene therapy venture capital companies based in the United States
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Gene therapy venture capital companies based in the United States at a glance
As of Sep 3, 2026Companies by employee count
How this list was built
Company categories are rarely black and white. RevenueBase reads each company's own description of its business to decide whether it belongs among gene therapy venture capital companies, so some rows will be adjacent to the category rather than pure plays. The description and evidence rating on every row are there so you can check each match yourself.
- Source
- The RevenueBase company graph: 60 million companies and 398.9 million professional contacts resolved from primary sources, queried with RevenueBase SmartSearch, the natural-language company search available to every RevenueBase user.
- What qualifies
- Companies headquartered in the United States whose own description of what they do matches “gene therapy venture capital companies”. Matching reads each company's description, not its industry code or its name.
- What we exclude
- Companies whose own description does not clearly place them among gene therapy venture capital companies, and records with no verified work email. Companies headquartered outside United States are excluded even when they keep an office there.
- Match quality
- In blind human judging of this matching method, 86% of matched companies were on target. Expect roughly 1 in 7 rows to be adjacent to the category rather than a pure play. Every row shows the company's own description and an evidence rating so you can judge each match yourself. Read the full methodology: how the lists are built, how the judging worked, and what the figure means.
- Ranking
- Team size, largest first: companies are ordered by the number of professionals RevenueBase tracks at each one. Employee ranges shown are reported bands, for context.
- Verification
- Every listed company carries at least one verified work email, 5,057 across the full list. Contacts re-verify on a rolling cadence, and each contact's own verification date is shown inside RevenueBase.
- Refresh
- This page's figures were pulled from the company graph on September 3, 2026. Lists refresh periodically as the graph is re-checked.
- Corrections
- Wrong category, wrong headquarters, or a company that has closed? Use “Report an issue” on any row. Reports go to the RevenueBase Data Team and feed back into the company graph.
Frequently asked
How many gene therapy venture capital companies are there based in the United States?
RevenueBase identified 254 gene therapy venture capital companies headquartered in the United States as of September 2026, matched on each company's own description of what it does rather than its industry code.
What is the largest company on this list?
Bridgebio, headquartered in Palo Alto, tops this list with the largest team on record.
Which city has the most gene therapy venture capital companies?
New York leads with 22 headquartered companies, followed by Boston (21) and Cambridge (18).
How do I get contact information for these companies?
A free RevenueBase account lets you run this exact search and work the top results, verified emails and direct dials included. Upgrading unlocks all 5,057 verified decision-maker contacts tracked across these 254 companies.
How current is this list?
The list refreshes periodically as the company graph is re-checked. This page's figures were pulled on September 3, 2026.
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About this data
RevenueBase is a B2B data infrastructure company. Its company graph covers 60 million companies and 398.9 million professional contacts, with emails verified on a rolling cadence rather than scraped once and left to decay. These company lists are generated directly from that graph with RevenueBase SmartSearch, the same natural-language company search every RevenueBase user has: describe a market in plain words, get the companies that match, and add verified emails and direct dials for the people at them. It is the same data that powers RevenueBase's B2B data products, and a free account includes 500 credits to start. How these lists are built and judged.
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