Company lists · Data refreshed September 2026

Top 25 Gene therapy venture capital companies worldwide

RevenueBase identified 281 gene therapy venture capital companies worldwide as of September 2026 and tracks 10,726 professional contacts across them, including 5,662 with verified work emails and 4,969 with mobile numbers. The United States is the largest market and New York the largest hub.

This list covers gene therapy venture capital companies worldwide, matched on what each company actually does as described in its own words. Ranked by team size, largest first. Every row shows the company's own description, its RevenueBase Smart Search rating, and when it was last checked. Data refreshed September 3, 2026. Country and city lists for gene therapy venture capital companies follow the table.

Published by RevenueBase, a B2B data infrastructure company. This list was built with RevenueBase Smart Search, the natural-language company search RevenueBase customers use to build their own targeted lists and unlock verified emails and direct dials at the companies on them. How these lists are built and judged.

How to read this list RevenueBase Smart Search rating on every row Refreshed Sep 3, 2026 86% judged on-target in blind review
281Companies
10,726Contacts tracked
5,662Verified emails
4,969Mobile numbers
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The 25 largest gene therapy venture capital companies worldwide

Ranked by team size
Top 25 of 281 gene therapy venture capital companies worldwide, ranked by team size, largest first. Data refreshed Sep 3, 2026. RevenueBase Smart Search rates how each company's information relates to gene therapy venture capital companies: strong evidence (its own description names it), partial (names part of it), indirect (matched on the rest of its profile rather than the description shown). Click a contact count to view that company's people.
#CompanyRevenueBase Smart SearchHeadquartersEmployeesContacts
1Indirect evidencePalo Alto, CA, US501-1,000821 contacts →

Indirect evidence

“We exist to bring transformative medicines to people living with genetic conditions.”

Source: RevenueBase Database · checked Sep 3, 2026
2Strong evidenceUpper Arlington, OH, US501-1,000507 contacts →

Strong evidence

“AskBio Inc, a wholly owned and independently operated subsidiary of Bayer AG, is a fully integrated gene therapy company dedicated to developing life-saving medicines and changing…”

Source: RevenueBase Database · checked Sep 3, 2026
3Strong evidenceColumbus, OH, US201-500450 contacts →

Strong evidence

“Forge, a member of Ajinomoto Bio-Pharma Services, is a gene therapy development engine, focused on enabling access to life changing gene therapies and helping bring them from idea…”

Source: RevenueBase Database · checked Sep 3, 2026
4Indirect evidenceLondon/new York, United KingdomHQ checked Sep 3, 202651-200398 contacts →

Indirect evidence

“MeiraGTx (Nasdaq: MGTX) is a vertically integrated, clinical-stage genetic medicine company with a broad pipeline of late-stage clinical programs supported by end-to-end…”

Source: RevenueBase Database · checked Sep 3, 2026
5Strong evidenceRockville, MD, US201-500392 contacts →

Strong evidence

“REGENXBIO is a leading clinical-stage biotechnology company seeking to improve lives through the curative potential of gene therapy.”

Source: RevenueBase Database · checked Sep 3, 2026
6Indirect evidenceCambridge, MA, US201-500285 contacts →

Indirect evidence

“Sana Biotechnology is focused on utilizing engineered cells as medicines for patients.”

Source: RevenueBase Database · checked Sep 3, 2026
7Partial evidenceRichmond, CA, US201-500269 contacts →

Partial evidence

“For Sangamo Therapeutics, science is a means to develop new medicines with the potential to transform the lives of patients living with serious genetic diseases.”

Source: RevenueBase Database · checked Sep 3, 2026
8Strong evidenceNew York, NY, US201-500258 contacts →

Strong evidence

“Rocket Pharma (NASDAQ: RCKT) is a fully-integrated, clinical-stage company seeking gene therapy cures.”

Source: RevenueBase Database · checked Sep 3, 2026
9Partial evidenceEmeryville, CA, US51-200234 contacts →

Partial evidence

“4DMT is a leading late-stage biotechnology company advancing durable and disease-targeted therapeutics with potential to transform treatment paradigms and provide unprecedented…”

Source: RevenueBase Database · checked Sep 3, 2026
10Indirect evidenceNew York, NY, US51-200232 contacts →

Indirect evidence

“Cellectis is a global, clinical-stage biopharmaceutical company.”

Source: RevenueBase Database · checked Sep 3, 2026
11Strong evidenceLondon, United KingdomHQ checked Sep 3, 202651-200221 contacts →

Strong evidence

“Orchard Therapeutics, a Kyowa Kirin company, is a global gene therapy leader focused on ending the devastation caused by genetic and other severe diseases by discovering…”

Source: RevenueBase Database · checked Sep 3, 2026
12Indirect evidencePalo Alto, CA, US51-200209 contacts →

Indirect evidence

“Our mission is to revolutionize medicine, with the ultimate goal of eliminating human suffering and enabling people to live without the burden of disease.”

Source: RevenueBase Database · checked Sep 3, 2026
13Partial evidenceLexington, MA, US51-200207 contacts →

Partial evidence

“Voyager Therapeutics, Inc.(Nasdaq: VYGR) is a biotechnology company dedicated to leveraging the power of human genetics to modify the course of – and ultimately cure –…”

Source: RevenueBase Database · checked Sep 3, 2026
14Partial evidenceBoston, MA, US201-500188 contacts →

Partial evidence

“Verve Therapeutics, a wholly owned subsidiary of Eli Lilly and Company, is developing a new class of genetic medicines for cardiovascular disease with the potential to transform…”

Source: RevenueBase Database · checked Sep 3, 2026
15Strong evidenceRedwood City, CA, US51-200174 contacts →

Strong evidence

“Adverum Biotechnologies (NASDAQ: ADVM) is a clinical-stage company that aims to establish gene therapy as a new standard of care for highly prevalent ocular diseases with the…”

Source: RevenueBase Database · checked Sep 3, 2026
16Indirect evidenceSan Diego, CA, US201-500172 contacts →

Indirect evidence

“Poseida was acquired by Roche in early 2025 and is now part of the Roche Group.”

Source: RevenueBase Database · checked Sep 3, 2026
17Strong evidenceBoston, MA, US51-200160 contacts →

Strong evidence

“Solid Biosciences is a precision genetic medicine company focused on advancing a portfolio of gene therapy candidates targeting rare neuromuscular and cardiac diseases, including…”

Source: RevenueBase Database · checked Sep 3, 2026
18Strong evidenceSouth San Francisco, CA, US51-200153 contacts →

Strong evidence

“Encoded Therapeutics is creating one-time, disease-modifying gene therapies for pediatric central nervous system (CNS) disorders with its cell-selective targeting and regulation…”

Source: RevenueBase Database · checked Sep 3, 2026
19Indirect evidenceAgoura Hills, CA, US51-200124 contacts →

Indirect evidence

“A2 is dedicated to pushing the boundaries of science to transform medicine and turn the tide on cancer.”

Source: RevenueBase Database · checked Sep 3, 2026
20Indirect evidenceMalvern, PA, US51-200120 contacts →

Indirect evidence

“Ocugen, Inc.”

Source: RevenueBase Database · checked Sep 3, 2026
21Strong evidenceRemote, US51-200116 contacts →

Strong evidence

“Curie.Bio is a venture capital firm that helps founders discover and develop important new medicines.”

Source: RevenueBase Database · checked Sep 3, 2026
22Strong evidenceRockville, MD, US51-200115 contacts →

Strong evidence

“Ascend is gene to GMP partner with deep expertise in advanced therapy development and commercialization.”

Source: RevenueBase Database · checked Sep 3, 2026
23Strong evidenceCambridge, MA, US51-200114 contacts →

Strong evidence

“Obsidian Therapeutics is pioneering controllable cell and gene therapies to deliver transformative outcomes for patients with intractable diseases.”

Source: RevenueBase Database · checked Sep 3, 2026
24Indirect evidenceNew York, NY, US51-200109 contacts →

Indirect evidence

“Neurogene is accelerating development of new genetic medicines to people with devastating neurological diseases and their families.”

Source: RevenueBase Database · checked Sep 3, 2026
25Indirect evidenceNewbury Park, CA, US51-200108 contacts →

Indirect evidence

“Capsida Biotherapeutics Inc.”

Source: RevenueBase Database · checked Sep 3, 2026

Showing 25 of 281 gene therapy venture capital companies worldwide

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Gene therapy venture capital companies worldwide at a glance

As of Sep 3, 2026
52.8%Verified-email coverage
46.3%Mobile-number coverage
38.2Average contacts per company
11-50Median size (employees)
7.8%Largest-city concentration · New York
Sep 3, 2026Page data refreshed

Companies by employee count

1-10
126
11-50
83
51-200
47
201-500
12
501-1,000
4
1,001-5,000
3
5,001-10,000
2

How this list was built

Company categories are rarely black and white. RevenueBase reads each company's own description of its business to decide whether it belongs among gene therapy venture capital companies, so some rows will be adjacent to the category rather than pure plays. The description and RevenueBase Smart Search rating on every row are there so you can check each match yourself.

Source
The RevenueBase company graph: 60 million companies and 398.9 million professional contacts resolved from primary sources, queried with RevenueBase Smart Search, the natural-language company search available to every RevenueBase user.
Coverage
2 countries, largest first: the United States, the United Kingdom. Country and city lists for gene therapy venture capital companies are linked below.
What qualifies
Companies worldwide whose own description of what they do matches “gene therapy venture capital companies”. Matching reads each company's description, not its industry code or its name.
RevenueBase Smart Search
RevenueBase Smart Search is how this list is assembled and how each row is rated. RevenueBase's data engine and AI assess a company's LinkedIn profile, information supplied directly by the company, its website and other publicly available information, then relate it to a category defined in a user's own words. Each row is rated strong evidence (its own description names gene therapy venture capital companies), partial evidence (it names part of the category) or indirect evidence (the description shown names none of it and the match rests on the rest of the company's profile). The description supporting each rating is quoted on the row.
What we exclude
Companies whose own description does not clearly place them among gene therapy venture capital companies, and records with no verified work email.
Match quality
In blind human judging of this matching method, 86% of matched companies were on target. Expect roughly 1 in 7 rows to be adjacent to the category rather than a pure play. Every row shows the company's own description and its RevenueBase Smart Search rating so you can judge each match yourself. Read the full methodology: how the lists are built, how the judging worked, and what the figure means.
Ranking
Team size, largest first: companies are ordered by the number of professionals RevenueBase tracks at each one. Employee ranges shown are reported bands, for context.
Verification
Every listed company carries at least one verified work email, 5,662 across the full list. Contacts re-verify on a rolling cadence, and each contact's own verification date is shown inside RevenueBase.
Refresh
This page's figures were pulled from the company graph between September 3, 2026 and September 14, 2026. Lists refresh periodically as the graph is re-checked.
Corrections
Wrong category, wrong headquarters, or a company that has closed? Use “Report an issue” on any row. Reports go to the RevenueBase Data Team and feed back into the company graph.

Gene therapy venture capital companies by location

2 lists · largest first

Every Gene therapy venture capital companies list RevenueBase publishes, by country and city. Counts are matching companies in each list as of its own refresh date.

Countries

Frequently asked

What is RevenueBase Smart Search?

RevenueBase Smart Search is how RevenueBase decides which companies belong on this list and how strongly each one fits. Its data engine and AI assess a company's LinkedIn profile, information supplied directly by the company, its website and other publicly available information, then relate it to the category the list is about. Each row is rated strong evidence when the company's own description names gene therapy venture capital companies, partial evidence when it names part of the category, and indirect evidence when the description shown names none of it and the match rests on the rest of the company's profile.

How many gene therapy venture capital companies are there worldwide?

RevenueBase identified 281 gene therapy venture capital companies worldwide as of September 2026, matched on each company's own description of what it does rather than its industry code.

What is the largest company on this list?

Bridgebio, headquartered in Palo Alto, tops this list with the largest team on record.

Which country has the most gene therapy venture capital companies?

The United States leads with 254 companies, followed by the United Kingdom (27). Every gene therapy venture capital companies list by country and city is linked on this page.

Which city has the most gene therapy venture capital companies?

New York leads with 22 headquartered companies, followed by Boston (21) and Cambridge (20).

How do I get contact information for these companies?

A free RevenueBase account lets you run this exact search and work the top results, verified emails and direct dials included. Upgrading unlocks all 5,662 verified decision-maker contacts tracked across these 281 companies.

How current is this list?

The list refreshes periodically as the company graph is re-checked. This page's figures were pulled from the company graph between September 3, 2026 and September 14, 2026.

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About this data

RevenueBase is a B2B data infrastructure company. Its company graph covers 60 million companies and 398.9 million professional contacts, with emails verified on a rolling cadence rather than scraped once and left to decay. These company lists are generated directly from that graph with RevenueBase Smart Search, the same natural-language company search every RevenueBase user has: describe a market in plain words, get the companies that match, and add verified emails and direct dials for the people at them. It is the same data that powers RevenueBase's B2B data products, and a free account includes 500 credits to start. How these lists are built and judged.