Company lists · Data refreshed September 2026
Top 17 Rare disease biotech companies based in the United Kingdom
RevenueBase identified 29 company matches for rare disease biotech companies associated with the United Kingdom as of September 2026 and tracks 1,396 professional contacts across them, including 977 with verified work emails. London is the largest hub.
This list covers company matches for rare disease biotech companies associated with the United Kingdom, found by RevenueBase SmartSearch using the meaning of business descriptions in its company graph at Exact. Ranked by professionals tracked, largest first. Rows show recorded descriptions where available, Exact search membership and the snapshot date. Data refreshed September 17, 2026.
Published by RevenueBase, a B2B data infrastructure company. This list was built with RevenueBase SmartSearch, the natural-language company search RevenueBase customers use to build their own targeted lists and unlock verified emails and direct dials at the companies on them. How these lists are built and judged.
The 17 largest rare disease biotech companies based in the United Kingdom
Ranked by team size| # | Company | Contacts | |||
|---|---|---|---|---|---|
| 1 | 709 contacts → | ||||
Exact match “Partner of choice in specialty, hospital, and rare disease medicines ADVANZ PHARMA is a global pharmaceutical company with the purpose to improve patients’ lives by providing the…” Recorded in the RevenueBase company graph · Sep 17, 2026 · View company records in RevenueBase | |||||
| 2 | 196 contacts → | ||||
Exact match “We’re committed to supporting patients and their caregivers in every way we can.” Recorded in the RevenueBase company graph · Sep 17, 2026 · View company records in RevenueBase | |||||
| 3 | 100 contacts → | ||||
Exact match “Essential Pharma is an international specialty pharmaceutical company dedicated to maintaining access to clinically differentiated, niche medicines in small patient populations.” Recorded in the RevenueBase company graph · Sep 17, 2026 · View company records in RevenueBase | |||||
| 4 | 70 contacts → | ||||
Exact match “We are committed to transforming the lives of people affected by cancer or rare disease, globally.” Recorded in the RevenueBase company graph · Sep 17, 2026 · View company records in RevenueBase | |||||
| 5 | 60 contacts → | ||||
Exact match “Healx is a mission-driven technology company pioneering the next generation of drug discovery in order to bring novel, effective treatments to rare disease patients around the…” Recorded in the RevenueBase company graph · Sep 17, 2026 · View company records in RevenueBase | |||||
| 6 | 57 contacts → | ||||
Exact match “At Galen, we have purpose and passion in everything we do and encourage our people to dare to be extraordinary so we can benefit the health of all generations.” Recorded in the RevenueBase company graph · Sep 17, 2026 · View company records in RevenueBase | |||||
| 7 | 50 contacts → | ||||
Exact match “As the UK and Ireland affiliate of Sobi, an international biopharmaceutical company, we are transforming life for people with rare diseases.” Recorded in the RevenueBase company graph · Sep 17, 2026 · View company records in RevenueBase | |||||
| 8 | 40 contacts → | ||||
Exact match “Welcome to Mereo BioPharma, we are an agile biopharmaceutical company, focused on finding and bringing to market therapies that will improve the lives of people living with a rare…” Recorded in the RevenueBase company graph · Sep 17, 2026 · View company records in RevenueBase | |||||
| 9 | 11 contacts → | ||||
Exact match “Mironid Limited is an innovative new drug discovery company that develops proprietary drug candidate molecules by modulating the activity of key cell signalling proteins.” Recorded in the RevenueBase company graph · Sep 17, 2026 · View company records in RevenueBase | |||||
| 10 | 5 contacts → | ||||
Exact match “We are an entrepreneurial pharmaceutical company working to drive change in rare diseases.” Recorded in the RevenueBase company graph · Sep 17, 2026 · View company records in RevenueBase | |||||
| 11 | 4 contacts → | ||||
Exact match “At DHT.health, we exist to make a difference in rare and underserved diseases by creating meaningful change through research.” Recorded in the RevenueBase company graph · Sep 17, 2026 · View company records in RevenueBase | |||||
| 12 | 4 contacts → | ||||
Exact match “Bloomsbury Genetic Therapies ("Bloomsbury") is a clinical-stage biotechnology company, developing potentially curative treatments for patients suffering from rare neurological and…” Recorded in the RevenueBase company graph · Sep 17, 2026 · View company records in RevenueBase | |||||
| 13 | 3 contacts → | ||||
Exact match “Oranda Therapeutics is a rare disease company, focused on acquiring, developing and commercialising medicines that improve the lives of patients in areas of high unmet need.” Recorded in the RevenueBase company graph · Sep 17, 2026 · View company records in RevenueBase | |||||
| 14 | 3 contacts → | ||||
Exact match “ASPIRE BIOSCIENCES aims to find new treatments for unaddressed and rare diseases, by creating and nurturing working partnerships between rare disease patient organisations and…” Recorded in the RevenueBase company graph · Sep 17, 2026 · View company records in RevenueBase | |||||
| 15 | 1 contacts → | ||||
Exact match “We help companies developing new therapies for rare and genetic diseases to find and hire executive level talent for their senior medical and commercial roles across Europe.” Recorded in the RevenueBase company graph · Sep 17, 2026 · View company records in RevenueBase | |||||
| 16 | 1 contacts → | ||||
Exact match “ZYTHERA is at the forefront of developing groundbreaking treatments for lysosomal storage diseases (LSDs), a diverse group rare metabolic disorders caused by enzyme deficiencies…” Recorded in the RevenueBase company graph · Sep 17, 2026 · View company records in RevenueBase | |||||
| 17 | 1 contacts → | ||||
Exact match “Inventa Therapeutics is a U.K based Bio-Pharmaceutical Organization.” Recorded in the RevenueBase company graph · Sep 17, 2026 · View company records in RevenueBase | |||||
RevenueBase SmartSearch
Describe a niche business in your own words. RevenueBase SmartSearch compares the meaning of your description with company business descriptions compiled in the RevenueBase company graph. Exact, Similar, Related and Broad control how closely companies must fit.
This list uses Exact for “rare disease biotech companies”. Each Exact match badge shows membership in that saved search; it is not an individual similarity score or a service-quality rating. Recorded descriptions are shown where available.
Showing 17 of 29 rare disease biotech companies based in the United Kingdom
See the full list, filter by size, metro and specialty, and access 977 tracked professional contacts with verified work emails. Direct dials are available where recorded.
Free signup · no credit card
Rare disease biotech companies based in the United Kingdom at a glance
As of Sep 17, 2026Companies by employee count
Email recency for this list is measured worldwide rather than for United Kingdom, so it is reported there. Company counts and contact totals on this page are exact for United Kingdom, over 29 companies.
How this list was built
The recorded descriptions help you assess these company matches. Check a company’s website for its current services and locations.
- Source
- The RevenueBase company graph: 60 million companies and 398.9 million professional contacts resolved from primary sources, queried with RevenueBase SmartSearch, the natural-language company search available to every RevenueBase user.
- What qualifies
- Company records associated with the United Kingdom whose business descriptions match “rare disease biotech companies” by meaning at the Exact setting. Descriptions are compiled in the RevenueBase company graph from public websites, profiles and company information where available; they are not guaranteed quotations from the company's website.
- RevenueBase SmartSearch
- Describe a niche company in your own words to find businesses by meaning. Exact, Similar, Related and Broad control the breadth of RevenueBase SmartSearch. This saved list uses Exact. Each row's Exact match badge shows inclusion in that search, not an individual score or a service-quality judgment.
- Public preview
- The public preview omits records without a verified work email. Where headquarters information is recorded, preview rows are also filtered to this page’s location. Dataset totals and geographic summaries describe the full matched records before these preview filters.
- Match quality
- RevenueBase's August 25, 2026 study assessed 4,198 description/company pairs across matching settings. The publisher reports 86% good or better at Exact. This evaluates the method across queries; it does not audit this individual list. Recorded company descriptions, where available, help you judge each match yourself. Read the full methodology: how the lists are built and what the study measures.
- Ranking
- Team size, largest first: companies are ordered by the number of professionals RevenueBase tracks at each one. Employee ranges shown are reported bands, for context.
- Verification
- Every displayed company carries at least one verified work email. RevenueBase tracks 977 professional contacts with verified work emails across the full matched dataset. Contacts re-verify on a rolling cadence, and each contact's own verification date is shown inside RevenueBase.
- Refresh
- This page's figures were pulled from the company graph on September 17, 2026. Lists refresh periodically as the graph is re-checked.
- Record context
- Company records and descriptions can change. Check the company's website for its current services and locations.
Frequently asked
What is RevenueBase SmartSearch?
RevenueBase SmartSearch finds niche companies by the meaning of their business descriptions in the RevenueBase company graph. Exact, Similar, Related and Broad control how closely companies must fit your description. This list uses Exact for “rare disease biotech companies”; each Exact match badge shows search membership, not an individual similarity or quality score.
How many rare disease biotech companies are there based in the United Kingdom?
RevenueBase identified 29 company matches for rare disease biotech companies associated with the United Kingdom as of September 2026, using the meaning of business descriptions at Exact. This is the recorded matched set in the RevenueBase company graph.
What is the largest company on this list?
Advanz Pharma tops the displayed preview by professional contacts tracked in RevenueBase. Recorded headquarters appear in the company rows.
Which city has the most rare disease biotech companies?
London leads with 7 company records, followed by Cambridge (4) and Craigavon (1).
How do I get contact information for these companies?
A free RevenueBase account lets you run this exact search and work limited free results with 500 credits to start. Upgrading provides access to the 977 professional contacts with verified work emails tracked across these 29 companies; direct dials are available where recorded.
How current is this list?
The list refreshes periodically as the company graph is re-checked. This page's figures were pulled on September 17, 2026.
Ready to reach these companies? Verified emails and direct dials for all 29 rare disease biotech companies based in the United Kingdom. Start with a free account, no credit card.
Download this list →Related lists
Rare disease biotech companies by geography
About this data
RevenueBase is a B2B data infrastructure company. Its company graph covers 60 million companies and 398.9 million professional contacts, with emails verified on a rolling cadence rather than scraped once and left to decay. These company lists are generated directly from that graph with RevenueBase SmartSearch, the same natural-language company search every RevenueBase user has: describe a market in plain words, get the companies that match, and add verified emails and direct dials for the people at them. It is the same data that powers RevenueBase's B2B data products, and a free account includes 500 credits to start. How these lists are built and judged.
More company lists
- All company lists
- Lists by location
- Lists A-Z
- New lists
- Rare disease biotech companies based in France
- Rare disease biotech companies based in the United States
- AI companies based in the United Kingdom
- Cybersecurity companies based in the United Kingdom
- Manufacturing companies based in the United Kingdom
- Media companies based in the United Kingdom
Company intelligence · public preview
Top 17 rare disease biotech companies based in the United Kingdom
Find companies in any niche.
Describe the businesses you want in your own words. RevenueBase SmartSearch matches company descriptions by meaning.
RevenueBase records 29 matching company records for rare disease biotech companies based in the United Kingdom, with 1,396 tracked contacts and 977 verified work emails.
This public preview shows 17 selected records ordered by tracked contacts. RevenueBase SmartSearch finds company descriptions that match by meaning at Exact. Snapshot: September 17, 2026.
RevenueBase compiles business descriptions for niche-company discovery; each row shows a recorded excerpt where available. Adapt this search to find the companies and contacts you want.
Top 17 rare disease biotech companies based in the United Kingdom
The public list shows selected company records with contact and verified-email coverage. Reported employee bands provide separate company-size context.
| # | Company | Headquarters on record | Reported employees | RevenueBase SmartSearch | Tracked contacts |
|---|---|---|---|---|---|
| 1 |  Advanz Pharmaadvanzpharma.comHQ: London, United KingdomReported employees: 501-1,000 | London, United Kingdom | 501-1,000 | Exact match | 709 contacts → |
“Partner of choice in specialty, hospital, and rare disease medicines ADVANZ PHARMA is a global pharmaceutical company with the purpose to improve patients’ lives by providing the…” Recorded description excerpt · September 17, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 2 | Cycle Pharmaceuticalscyclepharma.com HQ: Cambridge, United KingdomReported employees: 51-200 | Cambridge, United Kingdom | 51-200 | Exact match | 196 contacts → |
“We’re committed to supporting patients and their caregivers in every way we can.” Recorded description excerpt · September 17, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 3 |  Essential Pharmaessentialpharmagroup.comHQ: Egham, United KingdomReported employees: 51-200 | Egham, United Kingdom | 51-200 | Exact match | 100 contacts → |
“Essential Pharma is an international specialty pharmaceutical company dedicated to maintaining access to clinically differentiated, niche medicines in small patient populations.” Recorded description excerpt · September 17, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 4 | Eusa Pharmaeusapharma.com HQ: Hemel Hempstead, United KingdomReported employees: 201-500 | Hemel Hempstead, United Kingdom | 201-500 | Exact match | 70 contacts → |
“We are committed to transforming the lives of people affected by cancer or rare disease, globally.” Recorded description excerpt · September 17, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 5 |  HEALXhealx.aiHQ: Cambridge, United KingdomReported employees: 51-200 | Cambridge, United Kingdom | 51-200 | Exact match | 60 contacts → |
“Healx is a mission-driven technology company pioneering the next generation of drug discovery in order to bring novel, effective treatments to rare disease patients around the…” Recorded description excerpt · September 17, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 6 |  Galen LTDgalen-pharma.comHQ: Belfast, United KingdomReported employees: 11-50 | Belfast, United Kingdom | 11-50 | Exact match | 57 contacts → |
“At Galen, we have purpose and passion in everything we do and encourage our people to dare to be extraordinary so we can benefit the health of all generations.” Recorded description excerpt · September 17, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 7 |  Sobi UK & Irelandsobi.comHQ: Great Abington, United KingdomReported employees: 51-200 | Great Abington, United Kingdom | 51-200 | Exact match | 50 contacts → |
“As the UK and Ireland affiliate of Sobi, an international biopharmaceutical company, we are transforming life for people with rare diseases.” Recorded description excerpt · September 17, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 8 |  Mereo Biopharmamereobiopharma.comHQ: London, United KingdomReported employees: 51-200 | London, United Kingdom | 51-200 | Exact match | 40 contacts → |
“Welcome to Mereo BioPharma, we are an agile biopharmaceutical company, focused on finding and bringing to market therapies that will improve the lives of people living with a rare…” Recorded description excerpt · September 17, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 9 | Mironid Limitedmironid.com HQ: Glasgow, United KingdomReported employees: 11-50 | Glasgow, United Kingdom | 11-50 | Exact match | 11 contacts → |
“Mironid Limited is an innovative new drug discovery company that develops proprietary drug candidate molecules by modulating the activity of key cell signalling proteins.” Recorded description excerpt · September 17, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 10 |  Ambrose Healthcareambrosehc.comHQ: Wales, United KingdomReported employees: 1-10 | Wales, United Kingdom | 1-10 | Exact match | 5 contacts → |
“We are an entrepreneurial pharmaceutical company working to drive change in rare diseases.” Recorded description excerpt · September 17, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 11 | dht.healthdht.health HQ: England, United KingdomReported employees: 1-10 | England, United Kingdom | 1-10 | Exact match | 4 contacts → |
“At DHT.health, we exist to make a difference in rare and underserved diseases by creating meaningful change through research.” Recorded description excerpt · September 17, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 12 |  Bloomsbury Genetic Therapiesbloomsburygtx.comHQ: London, United KingdomReported employees: 1-10 | London, United Kingdom | 1-10 | Exact match | 4 contacts → |
“Bloomsbury Genetic Therapies ("Bloomsbury") is a clinical-stage biotechnology company, developing potentially curative treatments for patients suffering from rare neurological and…” Recorded description excerpt · September 17, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 13 | Oranda Therapeuticsorandatherapeutics.com HQ: London, United KingdomReported employees: 1-10 | London, United Kingdom | 1-10 | Exact match | 3 contacts → |
“Oranda Therapeutics is a rare disease company, focused on acquiring, developing and commercialising medicines that improve the lives of patients in areas of high unmet need.” Recorded description excerpt · September 17, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 14 |  Aspire Biosciencesaspire-biosciences.comHQ: Cambridge, United KingdomReported employees: 1-10 | Cambridge, United Kingdom | 1-10 | Exact match | 3 contacts → |
“ASPIRE BIOSCIENCES aims to find new treatments for unaddressed and rare diseases, by creating and nurturing working partnerships between rare disease patient organisations and…” Recorded description excerpt · September 17, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 15 | Newsearch Life Sciences LTDnewsearchlifesciences.com HQ: St. Albans, United KingdomReported employees: 1-10 | St. Albans, United Kingdom | 1-10 | Exact match | 1 contacts → |
“We help companies developing new therapies for rare and genetic diseases to find and hire executive level talent for their senior medical and commercial roles across Europe.” Recorded description excerpt · September 17, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 16 | Zytherazythera.com HQ: Edinburgh, United KingdomReported employees: 1-10 | Edinburgh, United Kingdom | 1-10 | Exact match | 1 contacts → |
“ZYTHERA is at the forefront of developing groundbreaking treatments for lysosomal storage diseases (LSDs), a diverse group rare metabolic disorders caused by enzyme deficiencies…” Recorded description excerpt · September 17, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 17 | Inventa Therapeuticsinventatherapeutics.com HQ: Nottingham, United KingdomReported employees: 1-10 | Nottingham, United Kingdom | 1-10 | Exact match | 1 contacts → |
“Inventa Therapeutics is a U.K based Bio-Pharmaceutical Organization.” Recorded description excerpt · September 17, 2026Open company data in RevenueBase ↗Free signup required. | |||||
Showing 17 of 29 company matches
Build a targeted audience, find relevant contacts and export available records to your workflow.
Free signup · 500 credits · limited free results
Rare disease biotech companies: dataset insights
September 17, 2026These summaries describe recorded coverage in this saved dataset. This page is derived from saved source records; per-contact mobile coverage and email-recency results are not established by this snapshot.
Reported company sizes
29 records in the displayed employee bands.
0 matching records are outside the displayed bands or do not have a displayed size. Bars show shares of the displayed bands.
Email recency for this list is measured worldwide rather than for United Kingdom, so it is reported there. Company counts and contact totals on this page are exact for United Kingdom, over 29 companies.
How this company list was built
Describe a niche in your own words: companies installing commercial solar, or manufacturers of sustainable packaging. RevenueBase SmartSearch finds companies whose compiled business descriptions match by meaning. This list is one saved example to adapt.
Where the company descriptions come from
RevenueBase compiles company information from public sources, including company websites and public professional profiles such as LinkedIn, alongside information supplied by companies. The short recorded excerpt shown here is separate from the complete business description used for matching; individual source URLs and collection dates are not provided in this public snapshot.
RevenueBase SmartSearch matching settings
- Exact
- Closest fits to the business described.
- Similar
- Similar businesses with a wider range of fits.
- Related
- Related businesses in and around the category.
- Broad
- A broader set of businesses connected to the description.
RevenueBase SmartSearch · Exact match identifies inclusion in this search's closest semantic matching setting. It is not a per-company confidence score, a literal keyword match, or a quality endorsement.
Selection, ordering and scope
The public list shows selected company records with contact and verified-email coverage. Reported employee bands provide separate company-size context.
This page is derived from saved source records; per-contact mobile coverage and email-recency results are not established by this snapshot.
Recorded company descriptions support research; check company websites for current services. The selected preview is ordered by tracked contacts and is not a list of the best service providers.
Snapshot: September 17, 2026.
RevenueBase is a B2B data infrastructure company. Its September 3, 2026 published methodology describes a graph of 60 million companies and 398.9 million professional contacts; these platform figures differ from this page's totals. Published methodology ↗
Questions about this company list
What does Exact match mean for rare disease biotech companies?
The separate RevenueBase SmartSearch column identifies inclusion at the closest semantic matching preset. It is not a literal keyword match, a per-company confidence score or a quality endorsement. Changing the search form opens a new search in RevenueBase; it does not reclassify these saved rows.
How many rare disease biotech companies did RevenueBase find based in the United Kingdom?
The saved snapshot records 29 matching company records, 1,396 tracked contacts and 977 verified emails. The public preview displays 17 selected records.
Where do the company descriptions come from?
RevenueBase compiles company information from public sources, including company websites and public professional profiles such as LinkedIn, alongside information supplied by companies. The short recorded excerpt shown here is separate from the complete business description used for matching; individual source URLs and collection dates are not provided in this public snapshot.
How are the public companies ordered?
The selected public records are ordered by contacts tracked in RevenueBase, highest first. Contact coverage is a prospecting measure, not an assessment of the company's services or quality.
How can I get contact information?
Select a company's contact count to open its filtered contacts in RevenueBase. Free signup is required and includes 500 credits and limited free results. Verified emails, direct dials and mobile numbers depend on available coverage.
How current is this list?
Snapshot: September 17, 2026. Review each company's website for current services and locations. A recorded business description does not establish that every company offers every service named in the search.
What do headquarters and employee bands mean?
These are recorded company-level fields, rather than a map of every branch or a count of specialists. Missing headquarters or employee bands are labeled; older records may show a location separately from recorded headquarters.
Build your next target company list
Adapt this niche search and work with available contacts in RevenueBase.
Related lists
Rare disease biotech companies by geography
Cite this list
RevenueBase Data Team. Top 17 rare disease biotech companies based in the United Kingdom. Snapshot: September 17, 2026. https://revenuebase.ai/companies/rare-disease-biotech-companies/united-kingdom.
This is a selected public preview of saved company records, rather than an independently verified census. Open the source page ↗
More company lists
- All company lists
- Lists by location
- Lists A-Z
- New lists
- Rare disease biotech companies based in France
- Rare disease biotech companies based in the United States
- AI companies based in the United Kingdom
- Cybersecurity companies based in the United Kingdom
- Manufacturing companies based in the United Kingdom
- Media companies based in the United Kingdom
Company intelligence · public preview
Top 17 rare disease biotech companies based in the United Kingdom
RevenueBase records 29 matching company records for rare disease biotech companies based in the United Kingdom, with 1,396 tracked contacts and 977 verified work emails.
This public preview shows 17 selected records ordered by tracked contacts. RevenueBase SmartSearch finds company descriptions that match by meaning at Exact. Snapshot: September 17, 2026.
RevenueBase compiles business descriptions for niche-company discovery; each row shows a recorded excerpt where available. Adapt this search to find the companies and contacts you want.
Top 17 rare disease biotech companies based in the United Kingdom
The public list shows selected company records with contact and verified-email coverage. Reported employee bands provide separate company-size context.
| # | Company | Headquarters on record | Reported employees | RevenueBase SmartSearch | Tracked contacts |
|---|---|---|---|---|---|
| 1 | Advanz Pharmaadvanzpharma.com HQ: London, United KingdomReported employees: 501-1,000 | London, United Kingdom | 501-1,000 | Exact match | 709 contacts → |
“Partner of choice in specialty, hospital, and rare disease medicines ADVANZ PHARMA is a global pharmaceutical company with the purpose to improve patients’ lives by providing the…” Recorded description excerpt · September 17, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 2 | Cycle Pharmaceuticalscyclepharma.com HQ: Cambridge, United KingdomReported employees: 51-200 | Cambridge, United Kingdom | 51-200 | Exact match | 196 contacts → |
“We’re committed to supporting patients and their caregivers in every way we can.” Recorded description excerpt · September 17, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 3 | Essential Pharmaessentialpharmagroup.com HQ: Egham, United KingdomReported employees: 51-200 | Egham, United Kingdom | 51-200 | Exact match | 100 contacts → |
“Essential Pharma is an international specialty pharmaceutical company dedicated to maintaining access to clinically differentiated, niche medicines in small patient populations.” Recorded description excerpt · September 17, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 4 | Eusa Pharmaeusapharma.com HQ: Hemel Hempstead, United KingdomReported employees: 201-500 | Hemel Hempstead, United Kingdom | 201-500 | Exact match | 70 contacts → |
“We are committed to transforming the lives of people affected by cancer or rare disease, globally.” Recorded description excerpt · September 17, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 5 | HEALXhealx.ai HQ: Cambridge, United KingdomReported employees: 51-200 | Cambridge, United Kingdom | 51-200 | Exact match | 60 contacts → |
“Healx is a mission-driven technology company pioneering the next generation of drug discovery in order to bring novel, effective treatments to rare disease patients around the…” Recorded description excerpt · September 17, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 6 | Galen LTDgalen-pharma.com HQ: Belfast, United KingdomReported employees: 11-50 | Belfast, United Kingdom | 11-50 | Exact match | 57 contacts → |
“At Galen, we have purpose and passion in everything we do and encourage our people to dare to be extraordinary so we can benefit the health of all generations.” Recorded description excerpt · September 17, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 7 | Sobi UK & Irelandsobi.com HQ: Great Abington, United KingdomReported employees: 51-200 | Great Abington, United Kingdom | 51-200 | Exact match | 50 contacts → |
“As the UK and Ireland affiliate of Sobi, an international biopharmaceutical company, we are transforming life for people with rare diseases.” Recorded description excerpt · September 17, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 8 | Mereo Biopharmamereobiopharma.com HQ: London, United KingdomReported employees: 51-200 | London, United Kingdom | 51-200 | Exact match | 40 contacts → |
“Welcome to Mereo BioPharma, we are an agile biopharmaceutical company, focused on finding and bringing to market therapies that will improve the lives of people living with a rare…” Recorded description excerpt · September 17, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 9 | Mironid Limitedmironid.com HQ: Glasgow, United KingdomReported employees: 11-50 | Glasgow, United Kingdom | 11-50 | Exact match | 11 contacts → |
“Mironid Limited is an innovative new drug discovery company that develops proprietary drug candidate molecules by modulating the activity of key cell signalling proteins.” Recorded description excerpt · September 17, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 10 | Ambrose Healthcareambrosehc.com HQ: Wales, United KingdomReported employees: 1-10 | Wales, United Kingdom | 1-10 | Exact match | 5 contacts → |
“We are an entrepreneurial pharmaceutical company working to drive change in rare diseases.” Recorded description excerpt · September 17, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 11 | dht.healthdht.health HQ: England, United KingdomReported employees: 1-10 | England, United Kingdom | 1-10 | Exact match | 4 contacts → |
“At DHT.health, we exist to make a difference in rare and underserved diseases by creating meaningful change through research.” Recorded description excerpt · September 17, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 12 | Bloomsbury Genetic Therapiesbloomsburygtx.com HQ: London, United KingdomReported employees: 1-10 | London, United Kingdom | 1-10 | Exact match | 4 contacts → |
“Bloomsbury Genetic Therapies ("Bloomsbury") is a clinical-stage biotechnology company, developing potentially curative treatments for patients suffering from rare neurological and…” Recorded description excerpt · September 17, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 13 | Oranda Therapeuticsorandatherapeutics.com HQ: London, United KingdomReported employees: 1-10 | London, United Kingdom | 1-10 | Exact match | 3 contacts → |
“Oranda Therapeutics is a rare disease company, focused on acquiring, developing and commercialising medicines that improve the lives of patients in areas of high unmet need.” Recorded description excerpt · September 17, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 14 | Aspire Biosciencesaspire-biosciences.com HQ: Cambridge, United KingdomReported employees: 1-10 | Cambridge, United Kingdom | 1-10 | Exact match | 3 contacts → |
“ASPIRE BIOSCIENCES aims to find new treatments for unaddressed and rare diseases, by creating and nurturing working partnerships between rare disease patient organisations and…” Recorded description excerpt · September 17, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 15 | Newsearch Life Sciences LTDnewsearchlifesciences.com HQ: St. Albans, United KingdomReported employees: 1-10 | St. Albans, United Kingdom | 1-10 | Exact match | 1 contacts → |
“We help companies developing new therapies for rare and genetic diseases to find and hire executive level talent for their senior medical and commercial roles across Europe.” Recorded description excerpt · September 17, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 16 | Zytherazythera.com HQ: Edinburgh, United KingdomReported employees: 1-10 | Edinburgh, United Kingdom | 1-10 | Exact match | 1 contacts → |
“ZYTHERA is at the forefront of developing groundbreaking treatments for lysosomal storage diseases (LSDs), a diverse group rare metabolic disorders caused by enzyme deficiencies…” Recorded description excerpt · September 17, 2026Open company data in RevenueBase ↗Free signup required. | |||||
| 17 | Inventa Therapeuticsinventatherapeutics.com HQ: Nottingham, United KingdomReported employees: 1-10 | Nottingham, United Kingdom | 1-10 | Exact match | 1 contacts → |
“Inventa Therapeutics is a U.K based Bio-Pharmaceutical Organization.” Recorded description excerpt · September 17, 2026Open company data in RevenueBase ↗Free signup required. | |||||
Showing 17 of 29 company matches
Build a targeted audience, find relevant contacts and export available records to your workflow.
Free signup · 500 credits · limited free results
Rare disease biotech companies: dataset insights
September 17, 2026These summaries describe recorded coverage in this saved dataset. This page is derived from saved source records; per-contact mobile coverage and email-recency results are not established by this snapshot.
Reported company sizes
29 records in the displayed employee bands.
0 matching records are outside the displayed bands or do not have a displayed size. Bars show shares of the displayed bands.
Email recency for this list is measured worldwide rather than for United Kingdom, so it is reported there. Company counts and contact totals on this page are exact for United Kingdom, over 29 companies.
How this company list was built
Describe a niche in your own words: companies installing commercial solar, or manufacturers of sustainable packaging. RevenueBase SmartSearch finds companies whose compiled business descriptions match by meaning. This list is one saved example to adapt.
Where the company descriptions come from
RevenueBase compiles company information from public sources, including company websites and public professional profiles such as LinkedIn, alongside information supplied by companies. The short recorded excerpt shown here is separate from the complete business description used for matching; individual source URLs and collection dates are not provided in this public snapshot.
RevenueBase SmartSearch matching settings
- Exact
- Closest fits to the business described.
- Similar
- Similar businesses with a wider range of fits.
- Related
- Related businesses in and around the category.
- Broad
- A broader set of businesses connected to the description.
RevenueBase SmartSearch · Exact match identifies inclusion in this search's closest semantic matching setting. It is not a per-company confidence score, a literal keyword match, or a quality endorsement.
Selection, ordering and scope
The public list shows selected company records with contact and verified-email coverage. Reported employee bands provide separate company-size context.
This page is derived from saved source records; per-contact mobile coverage and email-recency results are not established by this snapshot.
Recorded company descriptions support research; check company websites for current services. The selected preview is ordered by tracked contacts and is not a list of the best service providers.
Snapshot: September 17, 2026.
RevenueBase is a B2B data infrastructure company. Its September 3, 2026 published methodology describes a graph of 60 million companies and 398.9 million professional contacts; these platform figures differ from this page's totals. Published methodology ↗
Questions about this company list
What does Exact match mean for rare disease biotech companies?
The separate RevenueBase SmartSearch column identifies inclusion at the closest semantic matching preset. It is not a literal keyword match, a per-company confidence score or a quality endorsement. Changing the search form opens a new search in RevenueBase; it does not reclassify these saved rows.
How many rare disease biotech companies did RevenueBase find based in the United Kingdom?
The saved snapshot records 29 matching company records, 1,396 tracked contacts and 977 verified emails. The public preview displays 17 selected records.
Where do the company descriptions come from?
RevenueBase compiles company information from public sources, including company websites and public professional profiles such as LinkedIn, alongside information supplied by companies. The short recorded excerpt shown here is separate from the complete business description used for matching; individual source URLs and collection dates are not provided in this public snapshot.
How are the public companies ordered?
The selected public records are ordered by contacts tracked in RevenueBase, highest first. Contact coverage is a prospecting measure, not an assessment of the company's services or quality.
How can I get contact information?
Select a company's contact count to open its filtered contacts in RevenueBase. Free signup is required and includes 500 credits and limited free results. Verified emails, direct dials and mobile numbers depend on available coverage.
How current is this list?
Snapshot: September 17, 2026. Review each company's website for current services and locations. A recorded business description does not establish that every company offers every service named in the search.
What do headquarters and employee bands mean?
These are recorded company-level fields, rather than a map of every branch or a count of specialists. Missing headquarters or employee bands are labeled; older records may show a location separately from recorded headquarters.
Build your next target company list
Adapt this niche search and work with available contacts in RevenueBase.
Related lists
Rare disease biotech companies by geography
Cite this list
RevenueBase Data Team. Top 17 rare disease biotech companies based in the United Kingdom. Snapshot: September 17, 2026. https://revenuebase.ai/companies/rare-disease-biotech-companies/united-kingdom.
This is a selected public preview of saved company records, rather than an independently verified census. Open the source page ↗
More company lists
- All company lists
- Lists by location
- Lists A-Z
- New lists
- Rare disease biotech companies based in France
- Rare disease biotech companies based in the United States
- AI companies based in the United Kingdom
- Cybersecurity companies based in the United Kingdom
- Manufacturing companies based in the United Kingdom
- Media companies based in the United Kingdom