Company lists · Data refreshed October 2026

Top 25 Muscular dystrophy biotech companies based in the United States

RevenueBase identified 51 company matches for muscular dystrophy biotech companies associated with the United States as of October 2026 and tracks 4,776 professional contacts across them, including 3,283 with verified work emails. Cambridge is the largest hub.

This list covers company matches for muscular dystrophy biotech companies associated with the United States, found by RevenueBase SmartSearch using the meaning of business descriptions in its company graph at Exact. Ranked by professionals tracked, largest first. Rows show recorded descriptions where available, Exact search membership and the snapshot date. Data refreshed October 18, 2026.

Published by RevenueBase, a B2B data infrastructure company. This list was built with RevenueBase SmartSearch, the natural-language company search RevenueBase customers use to build their own targeted lists and unlock verified emails and direct dials at the companies on them. How these lists are built and judged.

How to read this list RevenueBase SmartSearch · Exact Recorded Oct 18, 2026 How this list was built
51Companies
4,776Contacts tracked
3,283Verified emails
Explore this list → Free signup · no credit card · 500 free credits

The 25 largest muscular dystrophy biotech companies based in the United States

Ranked by team size
Top 25 of 51 company matches for muscular dystrophy biotech companies based in the United States, ordered by professional contacts tracked in RevenueBase, largest first. Recorded Oct 18, 2026. The RevenueBase SmartSearch column shows Exact match membership in this saved search. Click a contact count to view that company's people. Totals use company locations recorded by RevenueBase; the displayed preview is a smaller selection.
#CompanyRevenueBase SmartSearchHeadquartersEmployeesContacts
1Exact matchCambridge, MA, United StatesHQ recorded Oct 18, 2026501-1,0001,300 contacts →

Exact match

“Sarepta Therapeutics, headquartered in Cambridge, Massachusetts, is a global biotechnology company on an urgent mission: engineer precision genetic medicine for rare diseases that…”

Recorded in the RevenueBase company graph · Oct 18, 2026 · View company records in RevenueBase
2Exact matchSouth San Francisco, CA, United StatesHQ recorded Oct 18, 2026501-1,000747 contacts →

Exact match

“Cytokinetics is a specialty cardiovascular biopharmaceutical company, building on its over 25 years of pioneering scientific innovations in muscle biology, and advancing a…”

Recorded in the RevenueBase company graph · Oct 18, 2026 · View company records in RevenueBase
3Exact matchResearch Triangle Park, NC, United StatesHQ recorded Oct 18, 2026501-1,000528 contacts →

Exact match

“AskBio Inc, a wholly owned and independently operated subsidiary of Bayer AG, is a fully integrated gene therapy company dedicated to developing life-saving medicines and changing…”

Recorded in the RevenueBase company graph · Oct 18, 2026 · View company records in RevenueBase
4Exact matchCambridge, MA, United StatesHQ recorded Oct 18, 202651-200358 contacts →

Exact match

“Scholar Rock is a biopharmaceutical company that discovers, develops, and delivers life-changing therapies for people with serious diseases that have high unmet need.”

Recorded in the RevenueBase company graph · Oct 18, 2026 · View company records in RevenueBase
5Exact matchWaltham, MA, United StatesHQ recorded Oct 18, 202651-200305 contacts →

Exact match

“Dyne Therapeutics is focused on delivering functional improvement for people living with genetically driven neuromuscular diseases.”

Recorded in the RevenueBase company graph · Oct 18, 2026 · View company records in RevenueBase
6Exact matchSan Diego, CA, United StatesHQ recorded Oct 18, 202651-200293 contacts →

Exact match

“Capricor Therapeutics is a publicly traded (NASDAQ: CAPR) biotechnology company with a mission to develop groundbreaking therapies that make a meaningful impact on patients’ lives.”

Recorded in the RevenueBase company graph · Oct 18, 2026 · View company records in RevenueBase
7Exact matchBoston, MA, United StatesHQ recorded Oct 18, 202651-200241 contacts →

Exact match

“Headquartered in Boston’s Seaport community, Entrada Therapeutics is a clinical-stage biopharmaceutical company aiming to transform the lives of patients by establishing a new…”

Recorded in the RevenueBase company graph · Oct 18, 2026 · View company records in RevenueBase
8Exact matchPittsburgh, PA, United StatesHQ recorded Oct 18, 2026201-500212 contacts →

Exact match

“Cook MyoSite is on a mission to make regenerative medicine a part of everyday medicine.”

Recorded in the RevenueBase company graph · Oct 18, 2026 · View company records in RevenueBase
9Exact matchBoston, MA, United StatesHQ recorded Oct 18, 202651-200183 contacts →

Exact match

“Solid Biosciences is a precision genetic medicine company focused on advancing a portfolio of gene therapy candidates targeting rare neuromuscular and cardiac diseases, including…”

Recorded in the RevenueBase company graph · Oct 18, 2026 · View company records in RevenueBase
10Exact matchParamus, NJ, United StatesHQ recorded Oct 18, 202651-200161 contacts →

Exact match

“NS Pharma, Inc.(NSP) is a biopharmaceutical leader in delivering life-changing care to people living with complex, rare diseases, backed by over 100 years of Nippon Shinyaku Co.”

Recorded in the RevenueBase company graph · Oct 18, 2026 · View company records in RevenueBase
11Exact matchBoulder, CO, United StatesHQ recorded Oct 18, 202651-200152 contacts →

Exact match

“Edgewise Therapeutics, Inc.(Nasdaq: EWTX) is a leading clinical-stage biopharmaceutical company focused on cardiovascular diseases.”

Recorded in the RevenueBase company graph · Oct 18, 2026 · View company records in RevenueBase
12Exact matchWashington Dc, United StatesHQ recorded Oct 18, 202611-5049 contacts →

Exact match

“Parent Project Muscular Dystrophy fights to end Duchenne.”

Recorded in the RevenueBase company graph · Oct 18, 2026 · View company records in RevenueBase
13Exact matchChapel Hill, NC, United StatesHQ recorded Oct 18, 202611-5038 contacts →

Exact match

“Bamboo represents a community of researchers, clinicians, parents, regulatory scientists, and business professionals committed to providing hope to patients suffering from…”

Recorded in the RevenueBase company graph · Oct 18, 2026 · View company records in RevenueBase
14Exact matchNewport Beach, CA, United StatesHQ recorded Oct 18, 202611-5033 contacts →

Exact match

“CureDuchenne is the global leader in Duchenne research, patient care and innovation.”

Recorded in the RevenueBase company graph · Oct 18, 2026 · View company records in RevenueBase
15Exact matchUnited StatesHQ recorded Oct 18, 20261,001-5,00018 contacts →

Exact match

“Novartis Gene Therapies (formerly AveXis) is reimagining medicine to transform the lives of people living with rare genetic diseases.”

Recorded in the RevenueBase company graph · Oct 18, 2026 · View company records in RevenueBase
16Exact matchPlymouth, MA, United StatesHQ recorded Oct 18, 202611-5016 contacts →

Exact match

“In 2001, Christine and Stephen McSherry started Jett Foundation after learning the devastating news that their then five-year-old son, Jett, had Duchenne muscular dystrophy.”

Recorded in the RevenueBase company graph · Oct 18, 2026 · View company records in RevenueBase
17Exact matchSeattle, WA, United StatesHQ recorded Oct 18, 20261-1014 contacts →

Exact match

“Our mission is to orchestrate a cure for muscular dystrophies caused by dysferlin protein deficiency.”

Recorded in the RevenueBase company graph · Oct 18, 2026 · View company records in RevenueBase
18Exact matchSan Diego, CA, United StatesHQ recorded Oct 18, 202611-5011 contacts →

Exact match

“Epirium, a biopharmaceutical company based in San Diego, California, has identified and established an IP-protected platform of orally bioavailable small molecules that constitute…”

Recorded in the RevenueBase company graph · Oct 18, 2026 · View company records in RevenueBase
19Exact matchGlendale, CA, United StatesHQ recorded Oct 18, 20261-107 contacts →

Exact match

“It is simple, the cure is the goal, we don’t just cover symptoms.”

Recorded in the RevenueBase company graph · Oct 18, 2026 · View company records in RevenueBase
20Exact matchScottsdale, AZ, United StatesHQ recorded Oct 18, 20261-105 contacts →

Exact match

“Welcome to Heal DMD, the non-profit organization dedicated to improving the lives of people affected by Duchenne Muscular Dystrophy (DMD).”

Recorded in the RevenueBase company graph · Oct 18, 2026 · View company records in RevenueBase
21Exact matchColumbus, OH, United StatesHQ recorded Oct 18, 20261-104 contacts →

Exact match

Recorded description not available.

Recorded in the RevenueBase company graph · Oct 18, 2026 · View company records in RevenueBase
22Exact matchDublin, OH, United StatesHQ recorded Oct 18, 20261-104 contacts →

Exact match

“Little Hercules Foundation works to improve the lives of those diagnosed with – and families facing – Duchenne Muscular Dystrophy through Advocacy, Awareness, Family Assistance…”

Recorded in the RevenueBase company graph · Oct 18, 2026 · View company records in RevenueBase
23Exact matchReno, NV, United StatesHQ recorded Oct 18, 20261-104 contacts →

Exact match

“Sarcomatrix, Inc.”

Recorded in the RevenueBase company graph · Oct 18, 2026 · View company records in RevenueBase
24Exact matchBellevue, WA, United StatesHQ recorded Oct 18, 20261-104 contacts →

Exact match

“Allysta Pharmaceuticals is a US-based private clinical stage biopharmaceutical with a platform technology targeting treatment of fibrotic diseases offering broad applicability…”

Recorded in the RevenueBase company graph · Oct 18, 2026 · View company records in RevenueBase
25Exact matchBaltimore, MD, United StatesHQ recorded Oct 18, 20261-102 contacts →

Exact match

“Twine is working to develop targeted therapies to improve three key affected areas in people living with Duchenne muscular dystrophy (DMD) or related muscle diseases.”

Recorded in the RevenueBase company graph · Oct 18, 2026 · View company records in RevenueBase

Showing 25 of 51 muscular dystrophy biotech companies based in the United States

See the full list, filter by size, metro and specialty, and access 3,283 tracked professional contacts with verified work emails. Direct dials are available where recorded.

Free signup · no credit card

View the full list →

Muscular dystrophy biotech companies based in the United States at a glance

As of Oct 18, 2026
68.7%Verified-email coverage
93.6Average contacts per company
1-10Median size (employees)
9.8%Largest-city concentration · Cambridge
Oct 18, 2026Page data refreshed

Companies by employee count

1-10
29
11-50
7
51-200
8
201-500
2
501-1,000
3
1,001-5,000
2

Email recency for this list is measured worldwide rather than for United States, so it is reported there. Company counts and contact totals on this page are exact for United States, over 51 companies.

How this list was built

The recorded descriptions help you assess these company matches. Check a company’s website for its current services and locations.

Source
The RevenueBase company graph: 60 million companies and 398.9 million professional contacts resolved from primary sources, queried with RevenueBase SmartSearch, the natural-language company search available to every RevenueBase user.
What qualifies
Company records associated with the United States whose business descriptions match “muscular dystrophy biotech companies” by meaning at the Exact setting. Descriptions are compiled in the RevenueBase company graph from public websites, profiles and company information where available; they are not guaranteed quotations from the company's website.
RevenueBase SmartSearch
Describe a niche company in your own words to find businesses by meaning. Exact, Similar, Related and Broad control the breadth of RevenueBase SmartSearch. This saved list uses Exact. Each row's Exact match badge shows inclusion in that search, not an individual score or a service-quality judgment.
Public preview
The public preview omits records without a verified work email. Where headquarters information is recorded, preview rows are also filtered to this page’s location. Dataset totals and geographic summaries describe the full matched records before these preview filters.
Match quality
RevenueBase's August 25, 2026 study assessed 4,198 description/company pairs across matching settings. The publisher reports 86% good or better at Exact. This evaluates the method across queries; it does not audit this individual list. Recorded company descriptions, where available, help you judge each match yourself. Read the full methodology: how the lists are built and what the study measures.
Ranking
Team size, largest first: companies are ordered by the number of professionals RevenueBase tracks at each one. Employee ranges shown are reported bands, for context.
Verification
Every displayed company carries at least one verified work email. RevenueBase tracks 3,283 professional contacts with verified work emails across the full matched dataset. Contacts re-verify on a rolling cadence, and each contact's own verification date is shown inside RevenueBase.
Refresh
This page's figures were pulled from the company graph on October 18, 2026. Lists refresh periodically as the graph is re-checked.
Record context
Company records and descriptions can change. Check the company's website for its current services and locations.

Frequently asked

What is RevenueBase SmartSearch?

RevenueBase SmartSearch finds niche companies by the meaning of their business descriptions in the RevenueBase company graph. Exact, Similar, Related and Broad control how closely companies must fit your description. This list uses Exact for “muscular dystrophy biotech companies”; each Exact match badge shows search membership, not an individual similarity or quality score.

How many muscular dystrophy biotech companies are there based in the United States?

RevenueBase identified 51 company matches for muscular dystrophy biotech companies associated with the United States as of October 2026, using the meaning of business descriptions at Exact. This is the recorded matched set in the RevenueBase company graph.

What is the largest company on this list?

Sarepta Therapeutics tops the displayed preview by professional contacts tracked in RevenueBase. Recorded headquarters appear in the company rows.

Which city has the most muscular dystrophy biotech companies?

Cambridge leads with 5 company records, followed by Boston (3) and Reno (3).

How do I get contact information for these companies?

A free RevenueBase account lets you run this exact search and work limited free results with 500 credits to start. Upgrading provides access to the 3,283 professional contacts with verified work emails tracked across these 51 companies; direct dials are available where recorded.

How current is this list?

The list refreshes periodically as the company graph is re-checked. This page's figures were pulled on October 18, 2026.

Ready to reach these companies? Verified emails and direct dials for all 51 muscular dystrophy biotech companies based in the United States. Start with a free account, no credit card.

Download this list →

Related lists

About this data

RevenueBase is a B2B data infrastructure company. Its company graph covers 60 million companies and 398.9 million professional contacts, with emails verified on a rolling cadence rather than scraped once and left to decay. These company lists are generated directly from that graph with RevenueBase SmartSearch, the same natural-language company search every RevenueBase user has: describe a market in plain words, get the companies that match, and add verified emails and direct dials for the people at them. It is the same data that powers RevenueBase's B2B data products, and a free account includes 500 credits to start. How these lists are built and judged.