Company lists · Data refreshed September 2026

Top 25 Inherited retinal disease companies based in the United States

RevenueBase identified 107 company matches for inherited retinal disease companies associated with the United States as of September 2026 and tracks 10,181 professional contacts across them, including 3,091 with verified work emails. Boston is the largest hub.

This list covers company matches for inherited retinal disease companies associated with the United States, found by RevenueBase SmartSearch using the meaning of business descriptions in its company graph at Exact. Ranked by professionals tracked, largest first. Rows show recorded descriptions where available, Exact search membership and the snapshot date. Data refreshed September 20, 2026.

Published by RevenueBase, a B2B data infrastructure company. This list was built with RevenueBase SmartSearch, the natural-language company search RevenueBase customers use to build their own targeted lists and unlock verified emails and direct dials at the companies on them. How these lists are built and judged.

How to read this list RevenueBase SmartSearch · Exact Recorded Sep 20, 2026 How this list was built
107Companies
10,181Contacts tracked
3,091Verified emails
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The 25 largest inherited retinal disease companies based in the United States

Ranked by team size
Top 25 of 107 company matches for inherited retinal disease companies based in the United States, ordered by professional contacts tracked in RevenueBase, largest first. Recorded Sep 20, 2026. The RevenueBase SmartSearch column shows Exact match membership in this saved search. Click a contact count to view that company's people. Totals use company locations recorded by RevenueBase; the displayed preview is a smaller selection.
#CompanyRevenueBase SmartSearchHeadquartersEmployeesContacts
1Exact matchSan Rafael, CA, United StatesHQ recorded Sep 20, 20261,001-5,0003,943 contacts →

Exact match

“Founded in 1997, BioMarin is a global biotechnology company dedicated to transforming lives through genetic discovery.”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
2Exact matchCambridge, MA, United StatesHQ recorded Sep 20, 2026201-500499 contacts →

Exact match

“BlueRock Therapeutics is a clinical stage cell therapy company focused on creating cellular medicines to treat devastating diseases.”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
3Exact matchAlpharetta, GA, United StatesHQ recorded Sep 20, 202651-200494 contacts →

Exact match

“Alimera is a global pharmaceutical company whose mission is to be invaluable to patients, physicians, and partners concerned with retinal health and maintaining better vision…”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
4Exact matchColumbus, OH, United StatesHQ recorded Sep 20, 2026201-500456 contacts →

Exact match

“Forge, a member of Ajinomoto Bio-Pharma Services, is a gene therapy development engine, focused on enabling access to life changing gene therapies and helping bring them from idea…”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
5Exact matchRockville, MD, United StatesHQ recorded Sep 20, 2026201-500393 contacts →

Exact match

“REGENXBIO is a leading clinical-stage biotechnology company seeking to improve lives through the curative potential of gene therapy.”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
6Exact matchBedford, MA, United StatesHQ recorded Sep 20, 202651-200333 contacts →

Exact match

Recorded description not available.

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
7Exact matchCranbury, NJ, United StatesHQ recorded Sep 20, 2026201-500258 contacts →

Exact match

“Rocket Pharma (NASDAQ: RCKT) is a fully-integrated, clinical-stage company seeking gene therapy cures.”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
8Exact matchBoston, MA, United StatesHQ recorded Sep 20, 202651-200239 contacts →

Exact match

“Headquartered in Boston’s Seaport community, Entrada Therapeutics is a clinical-stage biopharmaceutical company aiming to transform the lives of patients by establishing a new…”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
9Exact matchEmeryville, CA, United StatesHQ recorded Sep 20, 202651-200236 contacts →

Exact match

“4DMT is a leading late-stage biotechnology company advancing durable and disease-targeted therapeutics with potential to transform treatment paradigms and provide unprecedented…”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
10Exact matchMorrisville, NC, United StatesHQ recorded Sep 20, 202651-200211 contacts →

Exact match

“Our mission is to revolutionize medicine, with the ultimate goal of eliminating human suffering and enabling people to live without the burden of disease.”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
11Exact matchRedwood City, CA, United StatesHQ recorded Sep 20, 202651-200177 contacts →

Exact match

“Adverum Biotechnologies (NASDAQ: ADVM) is a clinical-stage company that aims to establish gene therapy as a new standard of care for highly prevalent ocular diseases with the…”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
12Exact matchBoston, MA, United StatesHQ recorded Sep 20, 202651-200160 contacts →

Exact match

“Solid Biosciences is a precision genetic medicine company focused on advancing a portfolio of gene therapy candidates targeting rare neuromuscular and cardiac diseases, including…”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
13Exact matchColumbia, MD, United StatesHQ recorded Sep 20, 202651-200150 contacts →

Exact match

“The urgent mission of the Foundation Fighting Blindness is to drive the research that will provide preventions, treatments and cures for people affected by retinitis pigmentosa…”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
14Exact matchThe Colony, TX, United StatesHQ recorded Sep 20, 20261,001-5,000143 contacts →

Exact match

“Nidek offers a wide array of equipment designed for the diagnosis and treatment of retinal diseases, glaucoma, and other vision-impairing afflictions.”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
15Exact matchMalvern, PA, United StatesHQ recorded Sep 20, 202651-200121 contacts →

Exact match

“Ocugen, Inc.”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
16Exact matchPalo Alto, CA, United StatesHQ recorded Sep 20, 202651-200118 contacts →

Exact match

“Kodiak is a biopharmaceutical company committed to researching, developing and commercializing transformative therapeutics to treat high prevalence retinal diseases.”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
17Exact matchNew York, NY, United StatesHQ recorded Sep 20, 202651-200109 contacts →

Exact match

“Neurogene is accelerating development of new genetic medicines to people with devastating neurological diseases and their families.”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
18Exact matchParsippany, NJ, United StatesHQ recorded Sep 20, 2026201-50085 contacts →

Exact match

“Iveric Bio is now part of Astellas.”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
19Exact matchPhiladelphia, PA, United StatesHQ recorded Sep 20, 2026501-1,00076 contacts →

Exact match

“At Spark® Therapeutics, we believe in a world where no life is limited by disease.”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
20Exact matchNovato, CA, United StatesHQ recorded Sep 20, 20261,001-5,00067 contacts →

Exact match

“Leading with purpose.”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
21Exact matchWaltham, MA, United StatesHQ recorded Sep 20, 202651-20062 contacts →

Exact match

“We are a team with decades of proven success in translating science from bench to bedside across many companies and medicines, in gene therapy and beyond.”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
22Exact matchPalo Alto, CA, United StatesHQ recorded Sep 20, 202611-5061 contacts →

Exact match

“GondolaBio is a clinical-stage biopharmaceutical company focused on developing novel medicines for patients living with genetic diseases.”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
23Exact matchPhiladelphia, PA, United StatesHQ recorded Sep 20, 202651-20056 contacts →

Exact match

“GEMMABio, a new therapeutics company, will serve as the research and innovation arm to speed the research of and global access to life-changing advanced therapies for those living…”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
24Exact matchLake Forest, IL, United StatesHQ recorded Sep 20, 202651-20053 contacts →

Exact match

“Jaguar Gene Therapy, LLC is dedicated to accelerating breakthroughs in gene therapy for patients suffering from severe genetic diseases including those that impact sizeable…”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
25Exact matchAlachua, FL, United StatesHQ recorded Sep 20, 202651-20048 contacts →

Exact match

“AGTC is a clinical-stage biotechnology company that uses its proprietary gene therapy platform to develop products designed to transform the lives of patients with severe…”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase

Showing 25 of 107 inherited retinal disease companies based in the United States

See the full list, filter by size, metro and specialty, and access 3,091 tracked professional contacts with verified work emails. Direct dials are available where recorded.

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Inherited retinal disease companies based in the United States at a glance

As of Sep 20, 2026
30.4%Verified-email coverage
95.1Average contacts per company
11-50Median size (employees)
5.6%Largest-city concentration · Boston
Sep 20, 2026Page data refreshed

Companies by employee count

1-10
44
11-50
27
51-200
21
201-500
7
501-1,000
2
1,001-5,000
5
10001+
1

Email recency for this list is measured worldwide rather than for United States, so it is reported there. Company counts and contact totals on this page are exact for United States, over 107 companies.

How this list was built

The recorded descriptions help you assess these company matches. Check a company’s website for its current services and locations.

Source
The RevenueBase company graph: 60 million companies and 398.9 million professional contacts resolved from primary sources, queried with RevenueBase SmartSearch, the natural-language company search available to every RevenueBase user.
What qualifies
Company records associated with the United States whose business descriptions match “inherited retinal disease companies” by meaning at the Exact setting. Descriptions are compiled in the RevenueBase company graph from public websites, profiles and company information where available; they are not guaranteed quotations from the company's website.
RevenueBase SmartSearch
Describe a niche company in your own words to find businesses by meaning. Exact, Similar, Related and Broad control the breadth of RevenueBase SmartSearch. This saved list uses Exact. Each row's Exact match badge shows inclusion in that search, not an individual score or a service-quality judgment.
Public preview
The public preview omits records without a verified work email. Where headquarters information is recorded, preview rows are also filtered to this page’s location. Dataset totals and geographic summaries describe the full matched records before these preview filters.
Match quality
RevenueBase's August 25, 2026 study assessed 4,198 description/company pairs across matching settings. The publisher reports 86% good or better at Exact. This evaluates the method across queries; it does not audit this individual list. Recorded company descriptions, where available, help you judge each match yourself. Read the full methodology: how the lists are built and what the study measures.
Ranking
Team size, largest first: companies are ordered by the number of professionals RevenueBase tracks at each one. Employee ranges shown are reported bands, for context.
Verification
Every displayed company carries at least one verified work email. RevenueBase tracks 3,091 professional contacts with verified work emails across the full matched dataset. Contacts re-verify on a rolling cadence, and each contact's own verification date is shown inside RevenueBase.
Refresh
This page's figures were pulled from the company graph on September 20, 2026. Lists refresh periodically as the graph is re-checked.
Record context
Company records and descriptions can change. Check the company's website for its current services and locations.

Frequently asked

What is RevenueBase SmartSearch?

RevenueBase SmartSearch finds niche companies by the meaning of their business descriptions in the RevenueBase company graph. Exact, Similar, Related and Broad control how closely companies must fit your description. This list uses Exact for “inherited retinal disease companies”; each Exact match badge shows search membership, not an individual similarity or quality score.

How many inherited retinal disease companies are there based in the United States?

RevenueBase identified 107 company matches for inherited retinal disease companies associated with the United States as of September 2026, using the meaning of business descriptions at Exact. This is the recorded matched set in the RevenueBase company graph.

What is the largest company on this list?

Biomarin Pharmaceutical INC tops the displayed preview by professional contacts tracked in RevenueBase. Recorded headquarters appear in the company rows.

Which city has the most inherited retinal disease companies?

Boston leads with 6 company records, followed by Cambridge (6) and Philadelphia (4).

How do I get contact information for these companies?

A free RevenueBase account lets you run this exact search and work limited free results with 500 credits to start. Upgrading provides access to the 3,091 professional contacts with verified work emails tracked across these 107 companies; direct dials are available where recorded.

How current is this list?

The list refreshes periodically as the company graph is re-checked. This page's figures were pulled on September 20, 2026.

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About this data

RevenueBase is a B2B data infrastructure company. Its company graph covers 60 million companies and 398.9 million professional contacts, with emails verified on a rolling cadence rather than scraped once and left to decay. These company lists are generated directly from that graph with RevenueBase SmartSearch, the same natural-language company search every RevenueBase user has: describe a market in plain words, get the companies that match, and add verified emails and direct dials for the people at them. It is the same data that powers RevenueBase's B2B data products, and a free account includes 500 credits to start. How these lists are built and judged.