Company lists · Data refreshed September 2026

Top 25 Inherited neurological disease companies based in the United States

RevenueBase identified 175 inherited neurological disease companies headquartered in the United States as of September 2026 and tracks 5,687 professional contacts across them, including 3,354 with verified work emails. Boston is the largest hub.

This list covers inherited neurological disease companies headquartered in the United States, matched on what each company actually does as described in its own words. Ranked by team size, largest first. Every row shows the company's own description, its RevenueBase Smart Search rating, and when it was last checked. Data refreshed September 20, 2026.

Published by RevenueBase, a B2B data infrastructure company. This list was built with RevenueBase Smart Search, the natural-language company search RevenueBase customers use to build their own targeted lists and unlock verified emails and direct dials at the companies on them. How these lists are built and judged.

How to read this list HQ checked on every row RevenueBase Smart Search rating on every row Refreshed Sep 20, 2026 86% judged on-target in blind review
175Companies
5,687Contacts tracked
3,354Verified emails
Explore this list → Free signup · no credit card · 500 free credits

The 25 largest inherited neurological disease companies based in the United States

Ranked by team size
Top 25 of 175 inherited neurological disease companies based in the United States, ranked by team size, largest first. Data refreshed Sep 20, 2026. RevenueBase Smart Search rates how each company's information relates to inherited neurological disease companies: strong evidence (its own description names it), partial (names part of it), indirect (matched on the rest of its profile rather than the description shown). Click a contact count to view that company's people.
#CompanyRevenueBase Smart SearchHeadquartersEmployeesContacts
1Partial evidenceCambridge, MA, United StatesHQ checked Sep 20, 2026501-1,0001,359 contacts →

Partial evidence

“Sarepta Therapeutics, headquartered in Cambridge, Massachusetts, is a global biotechnology company on an urgent mission: engineer precision genetic medicine for rare diseases that…”

Source: RevenueBase Database · checked Sep 20, 2026
2Indirect evidenceResearch Triangle Park, NC, United StatesHQ checked Sep 20, 2026501-1,000510 contacts →

Indirect evidence

“AskBio Inc, a wholly owned and independently operated subsidiary of Bayer AG, is a fully integrated gene therapy company dedicated to developing life-saving medicines and changing…”

Source: RevenueBase Database · checked Sep 20, 2026
3Partial evidenceVoorhees, NJ, United StatesHQ checked Sep 20, 2026501-1,000275 contacts →

Partial evidence

“NeurAbilities Healthcare is the premier provider of neurological, behavioral and neurodevelopmental services in New Jersey and Pennsylvania, offering comfort, hope and answers…”

Source: RevenueBase Database · checked Sep 20, 2026
4Partial evidenceWaltham, MA, United StatesHQ checked Sep 20, 202651-200256 contacts →

Partial evidence

“Dyne Therapeutics is focused on delivering functional improvement for people living with genetically driven neuromuscular diseases.”

Source: RevenueBase Database · checked Sep 20, 2026
5Indirect evidenceBoston, MA, United StatesHQ checked Sep 20, 202651-200239 contacts →

Indirect evidence

“Headquartered in Boston’s Seaport community, Entrada Therapeutics is a clinical-stage biopharmaceutical company aiming to transform the lives of patients by establishing a new…”

Source: RevenueBase Database · checked Sep 20, 2026
6Partial evidencePearl River, NY, United StatesHQ checked Sep 20, 2026201-500229 contacts →

Partial evidence

“Acorda Therapeutics is a publicly traded (NASDAQ: ACOR) biotechnology company whose mission is to develop therapies that restore neurological function and improve the lives of…”

Source: RevenueBase Database · checked Sep 20, 2026
7Indirect evidenceLexington, MA, United StatesHQ checked Sep 20, 202651-200208 contacts →

Indirect evidence

“Voyager Therapeutics, Inc.(Nasdaq: VYGR) is a biotechnology company dedicated to leveraging the power of human genetics to modify the course of – and ultimately cure –…”

Source: RevenueBase Database · checked Sep 20, 2026
8Indirect evidenceBoston, MA, United StatesHQ checked Sep 20, 2026201-500203 contacts →

Indirect evidence

“Praxis Precision Medicines is a fully integrated, leading central nervous system (CNS) precision neuroscience biopharmaceutical company, translating insights from genetic…”

Source: RevenueBase Database · checked Sep 20, 2026
9Indirect evidenceSouth San Francisco, CA, United StatesHQ checked Sep 20, 202651-200192 contacts →

Indirect evidence

“We are a late-stage clinical biotechnology company with a mission to make degenerative brain disorders history.”

Source: RevenueBase Database · checked Sep 20, 2026
10Partial evidenceBoston, MA, United StatesHQ checked Sep 20, 202651-200160 contacts →

Partial evidence

“Solid Biosciences is a precision genetic medicine company focused on advancing a portfolio of gene therapy candidates targeting rare neuromuscular and cardiac diseases, including…”

Source: RevenueBase Database · checked Sep 20, 2026
11Strong evidenceNew York, NY, United StatesHQ checked Sep 20, 202651-200109 contacts →

Strong evidence

“Neurogene is accelerating development of new genetic medicines to people with devastating neurological diseases and their families.”

Source: RevenueBase Database · checked Sep 20, 2026
12Indirect evidenceNutley, NJ, United StatesHQ checked Sep 20, 20261,001-5,00082 contacts →

Indirect evidence

“Eisai U.S.”

Source: RevenueBase Database · checked Sep 20, 2026
13Indirect evidenceCambridge, MA, United StatesHQ checked Sep 20, 202651-20071 contacts →

Indirect evidence

“At QurAlis, we are neuro pioneers on a quest to cure, boldly seeking to translate scientific breakthroughs into powerful precision medicines.”

Source: RevenueBase Database · checked Sep 20, 2026
14Partial evidenceBoston, MA, United StatesHQ checked Sep 20, 202651-20069 contacts →

Partial evidence

“Driven by our proprietary Enhanced Delivery Oligonucleotide (EDO) platform, we are creating a pipeline of disease-modifying therapeutics with the potential to safely and…”

Source: RevenueBase Database · checked Sep 20, 2026
15Partial evidenceBoston, MA, United StatesHQ checked Sep 20, 202651-20064 contacts →

Partial evidence

“Atalanta Therapeutics is a biotechnology company developing treatments for intractable diseases of the central nervous system using RNA interference.”

Source: RevenueBase Database · checked Sep 20, 2026
16Partial evidenceGainesville, FL, United StatesHQ checked Sep 20, 2026201-50062 contacts →

Partial evidence

“An institute of world-renowned experts delivering breakthroughs in neurological and neurodegenerative disorders”

Source: RevenueBase Database · checked Sep 20, 2026
17Indirect evidenceNew Haven, CT, United StatesHQ checked Sep 20, 202651-20057 contacts →

Indirect evidence

“The Institute for Neurodegenerative Disorders (IND), founded in is an independent 501(c)3 nonprofit research institute based in New Haven, Connecticut.”

Source: RevenueBase Database · checked Sep 20, 2026
18Indirect evidenceBoston, MA, United StatesHQ checked Sep 20, 202611-5053 contacts →

Indirect evidence

“Prilenia is a clinical-stage biotech company focused on developing novel treatments for neurodegenerative and neurodevelopmental disorders.”

Source: RevenueBase Database · checked Sep 20, 2026
19Partial evidencePhiladelphia, PA, United StatesHQ checked Sep 20, 202651-20051 contacts →

Partial evidence

“We are a clinical stage genetic medicines company on a mission to improve the lives of patients with neurodegenerative diseases.”

Source: RevenueBase Database · checked Sep 20, 2026
20Indirect evidenceBoston, MA, United StatesHQ checked Sep 20, 202651-20042 contacts →

Indirect evidence

Source: RevenueBase Database · checked Sep 20, 2026
21Indirect evidenceCambridge, MA, United StatesHQ checked Sep 20, 2026201-50040 contacts →

Indirect evidence

“Cerevel Therapeutics is a biopharmaceutical company focused on developing new therapies to treat disorders of the central nervous system (CNS).”

Source: RevenueBase Database · checked Sep 20, 2026
22Strong evidenceBothell, WA, United StatesHQ checked Sep 20, 202651-20037 contacts →

Strong evidence

“At Athira, we aim to restore neuronal health for those suffering from neurological diseases, including Alzheimer’s, Parkinson’s disease dementia, and dementia with Lewy bodies.”

Source: RevenueBase Database · checked Sep 20, 2026
23Indirect evidencePurchase, NY, United StatesHQ checked Sep 20, 202611-5037 contacts →

Indirect evidence

Source: RevenueBase Database · checked Sep 20, 2026
24Partial evidenceChicago, IL, United StatesHQ checked Sep 20, 202611-5035 contacts →

Partial evidence

“Vanqua Bio is helping usher in a new era of hope for the millions of people living with neurodegenerative diseases.”

Source: RevenueBase Database · checked Sep 20, 2026
25Indirect evidenceAustin, TX, United StatesHQ checked Sep 20, 202611-5033 contacts →

Indirect evidence

“IntraBio Inc is a pharmaceutical company located in Austin, Texas focusing on drug discovery, development, and commercialization related to rare and common neurodegenerative and…”

Source: RevenueBase Database · checked Sep 20, 2026

Showing 25 of 175 inherited neurological disease companies based in the United States

See the full list, filter by size, metro and specialty, and get verified emails and direct dials for all 3,354 reachable decision-makers.

Free signup · no credit card

View the full list →

Inherited neurological disease companies based in the United States at a glance

As of Sep 20, 2026
59.0%Verified-email coverage
32.5Average contacts per company
11-50Median size (employees)
8.0%Largest-city concentration · Boston
Sep 20, 2026Page data refreshed

Companies by employee count

1-10
81
11-50
58
51-200
22
201-500
4
501-1,000
4
1,001-5,000
3
10001+
1

Email recency for this list is measured worldwide rather than for United States, so it is reported there. Company counts and contact totals on this page are exact for United States, over 175 companies.

How this list was built

Company categories are rarely black and white. RevenueBase reads each company's own description of its business to decide whether it belongs among inherited neurological disease companies, so some rows will be adjacent to the category rather than pure plays. The description and RevenueBase Smart Search rating on every row are there so you can check each match yourself.

Source
The RevenueBase company graph: 60 million companies and 398.9 million professional contacts resolved from primary sources, queried with RevenueBase Smart Search, the natural-language company search available to every RevenueBase user.
What qualifies
Companies headquartered in the United States whose own description of what they do matches “inherited neurological disease companies”. Matching reads each company's description, not its industry code or its name.
RevenueBase Smart Search
RevenueBase Smart Search is how this list is assembled and how each row is rated. RevenueBase's data engine and AI assess a company's LinkedIn profile, information supplied directly by the company, its website and other publicly available information, then relate it to a category defined in a user's own words. Each row is rated strong evidence (its own description names inherited neurological disease companies), partial evidence (it names part of the category) or indirect evidence (the description shown names none of it and the match rests on the rest of the company's profile). The description supporting each rating is quoted on the row.
What we exclude
Companies whose own description does not clearly place them among inherited neurological disease companies, and records with no verified work email. Companies headquartered outside United States are excluded even when they keep an office there.
Match quality
In blind human judging of this matching method, 86% of matched companies were on target. Expect roughly 1 in 7 rows to be adjacent to the category rather than a pure play. Every row shows the company's own description and its RevenueBase Smart Search rating so you can judge each match yourself. Read the full methodology: how the lists are built, how the judging worked, and what the figure means.
Ranking
Team size, largest first: companies are ordered by the number of professionals RevenueBase tracks at each one. Employee ranges shown are reported bands, for context.
Verification
Every listed company carries at least one verified work email, 3,354 across the full list. Contacts re-verify on a rolling cadence, and each contact's own verification date is shown inside RevenueBase.
Refresh
This page's figures were pulled from the company graph on September 20, 2026. Lists refresh periodically as the graph is re-checked.
Corrections
Wrong category, wrong headquarters, or a company that has closed? Use “Report an issue” on any row. Reports go to the RevenueBase Data Team and feed back into the company graph.

Frequently asked

What is RevenueBase Smart Search?

RevenueBase Smart Search is how RevenueBase decides which companies belong on this list and how strongly each one fits. Its data engine and AI assess a company's LinkedIn profile, information supplied directly by the company, its website and other publicly available information, then relate it to the category the list is about. Each row is rated strong evidence when the company's own description names inherited neurological disease companies, partial evidence when it names part of the category, and indirect evidence when the description shown names none of it and the match rests on the rest of the company's profile.

How many inherited neurological disease companies are there based in the United States?

RevenueBase identified 175 inherited neurological disease companies headquartered in the United States as of September 2026, matched on each company's own description of what it does rather than its industry code.

What is the largest company on this list?

Sarepta Therapeutics, headquartered in Cambridge, tops this list with the largest team on record.

Which city has the most inherited neurological disease companies?

Boston leads with 14 headquartered companies, followed by San Diego (9) and Cambridge (7).

How do I get contact information for these companies?

A free RevenueBase account lets you run this exact search and work the top results, verified emails and direct dials included. Upgrading unlocks all 3,354 verified decision-maker contacts tracked across these 175 companies.

How current is this list?

The list refreshes periodically as the company graph is re-checked. This page's figures were pulled on September 20, 2026.

Ready to reach these companies? Verified emails and direct dials for all 175 inherited neurological disease companies based in the United States. Start with a free account, no credit card.

Download this list →

Related lists

About this data

RevenueBase is a B2B data infrastructure company. Its company graph covers 60 million companies and 398.9 million professional contacts, with emails verified on a rolling cadence rather than scraped once and left to decay. These company lists are generated directly from that graph with RevenueBase Smart Search, the same natural-language company search every RevenueBase user has: describe a market in plain words, get the companies that match, and add verified emails and direct dials for the people at them. It is the same data that powers RevenueBase's B2B data products, and a free account includes 500 credits to start. How these lists are built and judged.