Company lists · Data refreshed September 2026

Top 25 Immunodeficiency syndromes gene therapy companies based in the United States

RevenueBase identified 89 immunodeficiency syndromes gene therapy companies headquartered in the United States as of September 2026 and tracks 4,440 professional contacts across them, including 2,348 with verified work emails. Boston is the largest hub.

This list covers immunodeficiency syndromes gene therapy companies headquartered in the United States, matched on what each company actually does as described in its own words. Ranked by team size, largest first. Every row shows the company's own description, its RevenueBase Smart Search rating, and when it was last checked. Data refreshed September 19, 2026.

Published by RevenueBase, a B2B data infrastructure company. This list was built with RevenueBase Smart Search, the natural-language company search RevenueBase customers use to build their own targeted lists and unlock verified emails and direct dials at the companies on them. How these lists are built and judged.

How to read this list HQ checked on every row RevenueBase Smart Search rating on every row Refreshed Sep 19, 2026 86% judged on-target in blind review
89Companies
4,440Contacts tracked
2,348Verified emails
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The 25 largest immunodeficiency syndromes gene therapy companies based in the United States

Ranked by team size
Top 25 of 89 immunodeficiency syndromes gene therapy companies based in the United States, ranked by team size, largest first. Data refreshed Sep 19, 2026. RevenueBase Smart Search rates how each company's information relates to immunodeficiency syndromes gene therapy companies: strong evidence (its own description names it), partial (names part of it), indirect (matched on the rest of its profile rather than the description shown). Click a contact count to view that company's people.
#CompanyRevenueBase Smart SearchHeadquartersEmployeesContacts
1Indirect evidenceSan Diego, CA, United StatesHQ checked Sep 19, 2026501-1,000591 contacts →

Indirect evidence

“ImmunityBio, Inc.(formerly NantKwest, Inc.) is developing cell and immunotherapy products that are designed to help strengthen each patient’s natural immune system, potentially…”

Source: RevenueBase Database · checked Sep 19, 2026
2Strong evidenceResearch Triangle Park, NC, United StatesHQ checked Sep 19, 2026501-1,000510 contacts →

Strong evidence

“AskBio Inc, a wholly owned and independently operated subsidiary of Bayer AG, is a fully integrated gene therapy company dedicated to developing life-saving medicines and changing…”

Source: RevenueBase Database · checked Sep 19, 2026
3Strong evidenceColumbus, OH, United StatesHQ checked Sep 19, 2026201-500456 contacts →

Strong evidence

“Forge, a member of Ajinomoto Bio-Pharma Services, is a gene therapy development engine, focused on enabling access to life changing gene therapies and helping bring them from idea…”

Source: RevenueBase Database · checked Sep 19, 2026
4Indirect evidenceSeattle, WA, United StatesHQ checked Sep 19, 2026201-500287 contacts →

Indirect evidence

“Sana Biotechnology is focused on utilizing engineered cells as medicines for patients.”

Source: RevenueBase Database · checked Sep 19, 2026
5Strong evidenceCranbury, NJ, United StatesHQ checked Sep 19, 2026201-500258 contacts →

Strong evidence

“Rocket Pharma (NASDAQ: RCKT) is a fully-integrated, clinical-stage company seeking gene therapy cures.”

Source: RevenueBase Database · checked Sep 19, 2026
6Strong evidenceBoston, MA, United StatesHQ checked Sep 19, 202651-200160 contacts →

Strong evidence

“Solid Biosciences is a precision genetic medicine company focused on advancing a portfolio of gene therapy candidates targeting rare neuromuscular and cardiac diseases, including…”

Source: RevenueBase Database · checked Sep 19, 2026
7Strong evidenceRockville, MD, United StatesHQ checked Sep 19, 202651-200115 contacts →

Strong evidence

“Ascend is gene to GMP partner with deep expertise in advanced therapy development and commercialization.”

Source: RevenueBase Database · checked Sep 19, 2026
8Indirect evidenceNewbury Park, CA, United StatesHQ checked Sep 19, 202651-200109 contacts →

Indirect evidence

“Capsida Biotherapeutics Inc.”

Source: RevenueBase Database · checked Sep 19, 2026
9Partial evidenceBoston, MA, United StatesHQ checked Sep 19, 202611-5066 contacts →

Partial evidence

“Kelonia is pioneering a new wave of genetic medicines using its next generation gene delivery platform.”

Source: RevenueBase Database · checked Sep 19, 2026
10Strong evidenceWaltham, MA, United StatesHQ checked Sep 19, 202651-20062 contacts →

Strong evidence

“We are a team with decades of proven success in translating science from bench to bedside across many companies and medicines, in gene therapy and beyond.”

Source: RevenueBase Database · checked Sep 19, 2026
11Partial evidencePhiladelphia, PA, United StatesHQ checked Sep 19, 202651-20056 contacts →

Partial evidence

“GEMMABio, a new therapeutics company, will serve as the research and innovation arm to speed the research of and global access to life-changing advanced therapies for those living…”

Source: RevenueBase Database · checked Sep 19, 2026
12Strong evidenceLake Forest, IL, United StatesHQ checked Sep 19, 202651-20053 contacts →

Strong evidence

“Jaguar Gene Therapy, LLC is dedicated to accelerating breakthroughs in gene therapy for patients suffering from severe genetic diseases including those that impact sizeable…”

Source: RevenueBase Database · checked Sep 19, 2026
13Indirect evidenceSan Carlos, CA, United StatesHQ checked Sep 19, 202611-5052 contacts →

Indirect evidence

“GigaGen, a subsidiary of Grifols, is advancing transformative antibody drugs for immune deficiency, infectious diseases and checkpoint resistant cancers by leveraging…”

Source: RevenueBase Database · checked Sep 19, 2026
14Partial evidenceSan Marino, CA, United StatesHQ checked Sep 19, 202651-20048 contacts →

Partial evidence

“GenVivo was founded on the idea that we can effectively treat cancer patients with the latest gene delivery technologies.”

Source: RevenueBase Database · checked Sep 19, 2026
15Indirect evidenceMonrovia, CA, United StatesHQ checked Sep 19, 2026n/a35 contacts →

Indirect evidence

“Rampart Bioscience is evolving a new class of medicines for patients with genetically driven diseases.”

Source: RevenueBase Database · checked Sep 19, 2026
16Partial evidenceRockville, MD, United StatesHQ checked Sep 19, 202611-5033 contacts →

Partial evidence

“American Gene Technologies® International Inc.(AGT™) is a private biotechnology company pursuing cures and treatments for infectious diseases, cancers, and monogenic disorders.”

Source: RevenueBase Database · checked Sep 19, 2026
17Strong evidenceGaithersburg, MD, United StatesHQ checked Sep 19, 202611-5029 contacts →

Strong evidence

“Born from purpose and for patient access, Vector BioMed is a Public Benefit Corporation engineering the next frontier of lentivirus-based cell and gene therapy.”

Source: RevenueBase Database · checked Sep 19, 2026
18Partial evidenceWaltham, MA, United StatesHQ checked Sep 19, 202651-20029 contacts →

Partial evidence

“AlloVir, formerly ViraCyte, was founded in 2013 and is the leader in the development of novel cell therapies with a focus on restoring natural immunity against life-threatening…”

Source: RevenueBase Database · checked Sep 19, 2026
19Indirect evidenceWarren, NJ, United StatesHQ checked Sep 19, 2026501-1,00027 contacts →

Indirect evidence

“Tevogen Bio brings together a highly skilled team of preeminent scientists, senior biopharmaceutical leaders, and manufacturing experts with the goal of advancing global health.”

Source: RevenueBase Database · checked Sep 19, 2026
20Partial evidenceOcala, FL, United StatesHQ checked Sep 19, 202611-5025 contacts →

Partial evidence

“AIM ImmunoTech Inc, an immuno-pharma company headquartered in Ocala, Florida, is focused on the research and development of therapeutics to treat multiple types of cancers, as…”

Source: RevenueBase Database · checked Sep 19, 2026
21Strong evidenceWest Palm Beach, FL, United StatesHQ checked Sep 19, 202651-20024 contacts →

Strong evidence

“EXUMA Biotech is a clinical-stage biotechnology company developing next-generation in vivo cell and gene therapies.”

Source: RevenueBase Database · checked Sep 19, 2026
22Indirect evidenceAustin, TX, United StatesHQ checked Sep 19, 202611-5023 contacts →

Indirect evidence

Source: RevenueBase Database · checked Sep 19, 2026
23Indirect evidenceCarrollton, TX, United StatesHQ checked Sep 19, 202611-5021 contacts →

Indirect evidence

“Gradalis is a late-stage clinical biotechnology company developing immunotherapies for multiple cancer indications including an upcoming Phase 3 registration trial in patients…”

Source: RevenueBase Database · checked Sep 19, 2026
24Partial evidenceMilpitas, CA, United StatesHQ checked Sep 19, 202651-20021 contacts →

Partial evidence

“ASC Therapeutics focuses on the development of curative therapies for rare diseases.”

Source: RevenueBase Database · checked Sep 19, 2026
25Strong evidenceCambridge, MA, United StatesHQ checked Sep 19, 202651-20020 contacts →

Strong evidence

“Our vision is to bring personalized gene therapy to the world.”

Source: RevenueBase Database · checked Sep 19, 2026

Showing 25 of 89 immunodeficiency syndromes gene therapy companies based in the United States

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Immunodeficiency syndromes gene therapy companies based in the United States at a glance

As of Sep 19, 2026
52.9%Verified-email coverage
49.9Average contacts per company
11-50Median size (employees)
6.7%Largest-city concentration · Boston
Sep 19, 2026Page data refreshed

Companies by employee count

1-10
39
11-50
22
51-200
16
201-500
8
501-1,000
3
10001+
1

Email recency for this list is measured worldwide rather than for United States, so it is reported there. Company counts and contact totals on this page are exact for United States, over 89 companies.

How this list was built

Company categories are rarely black and white. RevenueBase reads each company's own description of its business to decide whether it belongs among immunodeficiency syndromes gene therapy companies, so some rows will be adjacent to the category rather than pure plays. The description and RevenueBase Smart Search rating on every row are there so you can check each match yourself.

Source
The RevenueBase company graph: 60 million companies and 398.9 million professional contacts resolved from primary sources, queried with RevenueBase Smart Search, the natural-language company search available to every RevenueBase user.
What qualifies
Companies headquartered in the United States whose own description of what they do matches “immunodeficiency syndromes gene therapy companies”. Matching reads each company's description, not its industry code or its name.
RevenueBase Smart Search
RevenueBase Smart Search is how this list is assembled and how each row is rated. RevenueBase's data engine and AI assess a company's LinkedIn profile, information supplied directly by the company, its website and other publicly available information, then relate it to a category defined in a user's own words. Each row is rated strong evidence (its own description names immunodeficiency syndromes gene therapy companies), partial evidence (it names part of the category) or indirect evidence (the description shown names none of it and the match rests on the rest of the company's profile). The description supporting each rating is quoted on the row.
What we exclude
Companies whose own description does not clearly place them among immunodeficiency syndromes gene therapy companies, and records with no verified work email. Companies headquartered outside United States are excluded even when they keep an office there.
Match quality
In blind human judging of this matching method, 86% of matched companies were on target. Expect roughly 1 in 7 rows to be adjacent to the category rather than a pure play. Every row shows the company's own description and its RevenueBase Smart Search rating so you can judge each match yourself. Read the full methodology: how the lists are built, how the judging worked, and what the figure means.
Ranking
Team size, largest first: companies are ordered by the number of professionals RevenueBase tracks at each one. Employee ranges shown are reported bands, for context.
Verification
Every listed company carries at least one verified work email, 2,348 across the full list. Contacts re-verify on a rolling cadence, and each contact's own verification date is shown inside RevenueBase.
Refresh
This page's figures were pulled from the company graph on September 19, 2026. Lists refresh periodically as the graph is re-checked.
Corrections
Wrong category, wrong headquarters, or a company that has closed? Use “Report an issue” on any row. Reports go to the RevenueBase Data Team and feed back into the company graph.

Frequently asked

What is RevenueBase Smart Search?

RevenueBase Smart Search is how RevenueBase decides which companies belong on this list and how strongly each one fits. Its data engine and AI assess a company's LinkedIn profile, information supplied directly by the company, its website and other publicly available information, then relate it to the category the list is about. Each row is rated strong evidence when the company's own description names immunodeficiency syndromes gene therapy companies, partial evidence when it names part of the category, and indirect evidence when the description shown names none of it and the match rests on the rest of the company's profile.

How many immunodeficiency syndromes gene therapy companies are there based in the United States?

RevenueBase identified 89 immunodeficiency syndromes gene therapy companies headquartered in the United States as of September 2026, matched on each company's own description of what it does rather than its industry code.

What is the largest company on this list?

Immunitybio, INC, headquartered in San Diego, tops this list with the largest team on record.

Which city has the most immunodeficiency syndromes gene therapy companies?

Boston leads with 6 headquartered companies, followed by San Francisco (6) and Cambridge (5).

How do I get contact information for these companies?

A free RevenueBase account lets you run this exact search and work the top results, verified emails and direct dials included. Upgrading unlocks all 2,348 verified decision-maker contacts tracked across these 89 companies.

How current is this list?

The list refreshes periodically as the company graph is re-checked. This page's figures were pulled on September 19, 2026.

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About this data

RevenueBase is a B2B data infrastructure company. Its company graph covers 60 million companies and 398.9 million professional contacts, with emails verified on a rolling cadence rather than scraped once and left to decay. These company lists are generated directly from that graph with RevenueBase Smart Search, the same natural-language company search every RevenueBase user has: describe a market in plain words, get the companies that match, and add verified emails and direct dials for the people at them. It is the same data that powers RevenueBase's B2B data products, and a free account includes 500 credits to start. How these lists are built and judged.