Company lists · Data refreshed September 2026

Top 25 Familial hypercholesterolemia treatment companies worldwide

RevenueBase identified 61 company matches for familial hypercholesterolemia treatment companies worldwide as of September 2026 and tracks 8,648 professional contacts across them, including 2,258 with verified work emails. The United States is the largest market and Boston the largest hub.

This list covers company matches for familial hypercholesterolemia treatment companies worldwide, found by RevenueBase SmartSearch using the meaning of business descriptions in its company graph at Exact. Ranked by professionals tracked, largest first. Rows show recorded descriptions where available, Exact search membership and the snapshot date. Data refreshed September 20, 2026. Country and city lists for familial hypercholesterolemia treatment companies follow the table.

Published by RevenueBase, a B2B data infrastructure company. This list was built with RevenueBase SmartSearch, the natural-language company search RevenueBase customers use to build their own targeted lists and unlock verified emails and direct dials at the companies on them. How these lists are built and judged.

How to read this list RevenueBase SmartSearch · Exact Recorded Sep 20, 2026 How this list was built
61Companies
8,648Contacts tracked
2,258Verified emails
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The 25 largest familial hypercholesterolemia treatment companies worldwide

Ranked by team size
Top 25 of 61 company matches for familial hypercholesterolemia treatment companies worldwide, ordered by professional contacts tracked in RevenueBase, largest first. Recorded Sep 20, 2026. The RevenueBase SmartSearch column shows Exact match membership in this saved search. Click a contact count to view that company's people. Totals use company locations recorded by RevenueBase; the displayed preview is a smaller selection.
#CompanyRevenueBase SmartSearchHeadquartersEmployeesContacts
1Exact matchSan Rafael, CA, United StatesHQ recorded Sep 20, 20261,001-5,0003,943 contacts →

Exact match

“Founded in 1997, BioMarin is a global biotechnology company dedicated to transforming lives through genetic discovery.”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
2Exact matchCarlsbad, CA, United StatesHQ recorded Sep 20, 2026501-1,0001,313 contacts →

Exact match

“For three decades, Ionis has invented medicines that bring better futures to people with serious diseases.”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
3Exact matchPalo Alto, CA, United StatesHQ recorded Sep 20, 2026501-1,000837 contacts →

Exact match

“We exist to bring transformative medicines to people living with genetic conditions.”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
4Exact matchAnn Arbor, MI, United StatesHQ recorded Sep 20, 2026201-500313 contacts →

Exact match

Recorded description not available.

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
5Exact matchPittsburgh, PA, United StatesHQ recorded Sep 20, 2026201-500300 contacts →

Exact match

“A commercial-stage biotechnology company focused on the discovery, development and commercialization of genetic medicines for high unmet medical needs.”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
6Exact matchEmeryville, CA, United StatesHQ recorded Sep 20, 202651-200236 contacts →

Exact match

“4DMT is a leading late-stage biotechnology company advancing durable and disease-targeted therapeutics with potential to transform treatment paradigms and provide unprecedented…”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
7Exact matchBoston, MA, United StatesHQ recorded Sep 20, 2026201-500189 contacts →

Exact match

“Verve Therapeutics, a wholly owned subsidiary of Eli Lilly and Company, is developing a new class of genetic medicines for cardiovascular disease with the potential to transform…”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
8Exact matchBoston, MA, United StatesHQ recorded Sep 20, 202651-200160 contacts →

Exact match

“Solid Biosciences is a precision genetic medicine company focused on advancing a portfolio of gene therapy candidates targeting rare neuromuscular and cardiac diseases, including…”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
9Exact matchSouth San Francisco, CA, United StatesHQ recorded Sep 20, 202651-200119 contacts →

Exact match

“Tenaya Therapeutics is a clinical stage biotechnology company.”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
10Exact matchAventura, FL, United StatesHQ recorded Sep 20, 202651-20088 contacts →

Exact match

“This page is intended for US audiences.”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
11Exact matchCambridge, MA, United StatesHQ recorded Sep 20, 202651-20084 contacts →

Exact match

“We are a clinical-stage biopharmaceutical company focused on improving the lives of patients with genetically defined diseases in areas of high unmet medical need, with an initial…”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
12Exact matchPalo Alto, CA, United StatesHQ recorded Sep 20, 202611-5061 contacts →

Exact match

“GondolaBio is a clinical-stage biopharmaceutical company focused on developing novel medicines for patients living with genetic diseases.”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
13Exact matchPhiladelphia, PA, United StatesHQ recorded Sep 20, 202651-20056 contacts →

Exact match

“GEMMABio, a new therapeutics company, will serve as the research and innovation arm to speed the research of and global access to life-changing advanced therapies for those living…”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
14Exact matchLake Forest, IL, United StatesHQ recorded Sep 20, 202651-20053 contacts →

Exact match

“Jaguar Gene Therapy, LLC is dedicated to accelerating breakthroughs in gene therapy for patients suffering from severe genetic diseases including those that impact sizeable…”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
15Exact matchUnited StatesHQ recorded Sep 20, 20261,001-5,00035 contacts →

Exact match

“Novartis Gene Therapies (formerly AveXis) is reimagining medicine to transform the lives of people living with rare genetic diseases.”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
16Exact matchSan Diego, CA, United StatesHQ recorded Sep 20, 202651-20025 contacts →

Exact match

“ViaCyte is now part of Vertex Pharmaceuticals.”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
17Exact matchAmsterdam, NetherlandsHQ recorded Sep 20, 20261-1021 contacts →

Exact match

“FH Europe Foundation is an umbrella organisation of international patient organisations, actively working together to secure early identification and diagnosis of Familial…”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
18Exact matchBedford, MA, United StatesHQ recorded Sep 20, 202651-20017 contacts →

Exact match

“Homology Medicines is a genetic medicines company translating proprietary gene editing and gene therapy technologies into novel treatments for patients with rare diseases.”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
19Exact matchNovato, CA, United StatesHQ recorded Sep 20, 20261-1016 contacts →

Exact match

“Cyclarity Therapeutics, Inc, is pursuing a mission to treat the underlying causes of age-related disease.”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
20Exact matchUmeå, SwedenHQ recorded Sep 20, 20261-1012 contacts →

Exact match

“We are lipid biology experts focusing on developing novel therapeutics for patients with lipid related disorders.”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
21Exact matchSyracuse, NY, United StatesHQ recorded Sep 20, 20261-1011 contacts →

Exact match

“Repair Biotechnologies is a preclinical biotechnology company focused on developing drugs for cholesterol and aging-related diseases.”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
22Exact matchKing Of Prussia, PA, United StatesHQ recorded Sep 20, 202611-5010 contacts →

Exact match

“XyloCor Therapeutics is a development-stage, biotechnology company dedicated to developing first-in-class gene therapies for patients with unmet medical need in cardiovascular…”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
23Exact matchMelbourne, AustraliaHQ recorded Sep 20, 20261-1010 contacts →

Exact match

“Percheron Therapeutics Limited (ASX: PER) is an international biotechnology company focused on the development of novel therapies for rare diseases.”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
24Exact matchUnited StatesHQ recorded Sep 20, 20261-108 contacts →

Exact match

“Glafabra is a biotherapeutics development company focused on bringing into the clinic our Live-cel(TM) technology for cell-based gene therapy (Cb-GT).”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase
25Exact matchCincinnati, OH, United StatesHQ recorded Sep 20, 20261-107 contacts →

Exact match

“LIB Therapeutics is a privately held, late-stage biopharmaceutical company dedicated to bringing novel, safe and convenient subcutaneous and oral PCSK9 inhibitors to the millions…”

Recorded in the RevenueBase company graph · Sep 20, 2026 · View company records in RevenueBase

Showing 25 of 61 familial hypercholesterolemia treatment companies worldwide

See the full list, filter by size, metro and specialty, and access 2,258 tracked professional contacts with verified work emails. Direct dials are available where recorded.

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Familial hypercholesterolemia treatment companies worldwide at a glance

As of Sep 20, 2026
26.1%Verified-email coverage
141.8Average contacts per company
11-50Median size (employees)
4.9%Largest-city concentration · Boston
Sep 20, 2026Page data refreshed

Companies by employee count

1-10
28
11-50
13
51-200
11
201-500
4
501-1,000
3
1,001-5,000
2

Email recency is reported on each country list linked below.

How this list was built

The recorded descriptions help you assess these company matches. Check a company’s website for its current services and locations.

Source
The RevenueBase company graph: 60 million companies and 398.9 million professional contacts resolved from primary sources, queried with RevenueBase SmartSearch, the natural-language company search available to every RevenueBase user.
Coverage
Every country. Country and city lists for familial hypercholesterolemia treatment companies are linked below.
What qualifies
Company records worldwide whose business descriptions match “familial hypercholesterolemia treatment companies” by meaning at the Exact setting. Descriptions are compiled in the RevenueBase company graph from public websites, profiles and company information where available; they are not guaranteed quotations from the company's website.
RevenueBase SmartSearch
Describe a niche company in your own words to find businesses by meaning. Exact, Similar, Related and Broad control the breadth of RevenueBase SmartSearch. This saved list uses Exact. Each row's Exact match badge shows inclusion in that search, not an individual score or a service-quality judgment.
Public preview
The public preview omits records without a verified work email. Dataset totals and geographic summaries describe the full matched records before these preview filters.
Match quality
RevenueBase's August 25, 2026 study assessed 4,198 description/company pairs across matching settings. The publisher reports 86% good or better at Exact. This evaluates the method across queries; it does not audit this individual list. Recorded company descriptions, where available, help you judge each match yourself. Read the full methodology: how the lists are built and what the study measures.
Ranking
Team size, largest first: companies are ordered by the number of professionals RevenueBase tracks at each one. Employee ranges shown are reported bands, for context.
Verification
Every displayed company carries at least one verified work email. RevenueBase tracks 2,258 professional contacts with verified work emails across the full matched dataset. Contacts re-verify on a rolling cadence, and each contact's own verification date is shown inside RevenueBase.
Refresh
This page's figures were pulled from the company graph on September 20, 2026. Lists refresh periodically as the graph is re-checked.
Record context
Company records and descriptions can change. Check the company's website for its current services and locations.

Familial hypercholesterolemia treatment companies by location

1 lists · largest first

Every Familial hypercholesterolemia treatment companies list RevenueBase publishes, by country and city. Counts are matching companies in each list as of its own refresh date.

Countries

Frequently asked

What is RevenueBase SmartSearch?

RevenueBase SmartSearch finds niche companies by the meaning of their business descriptions in the RevenueBase company graph. Exact, Similar, Related and Broad control how closely companies must fit your description. This list uses Exact for “familial hypercholesterolemia treatment companies”; each Exact match badge shows search membership, not an individual similarity or quality score.

How many familial hypercholesterolemia treatment companies are there worldwide?

RevenueBase identified 61 company matches for familial hypercholesterolemia treatment companies worldwide as of September 2026, using the meaning of business descriptions at Exact. This is the recorded matched set in the RevenueBase company graph.

What is the largest company on this list?

Biomarin Pharmaceutical INC tops the displayed preview by professional contacts tracked in RevenueBase. Recorded headquarters appear in the company rows.

Which country has the most familial hypercholesterolemia treatment companies?

The United States leads with 34 companies. Every familial hypercholesterolemia treatment companies list by country and city is linked on this page.

Which city has the most familial hypercholesterolemia treatment companies?

Boston leads with 3 company records, followed by Amsterdam (2) and Cambridge (2).

How do I get contact information for these companies?

A free RevenueBase account lets you run this exact search and work limited free results with 500 credits to start. Upgrading provides access to the 2,258 professional contacts with verified work emails tracked across these 61 companies; direct dials are available where recorded.

How current is this list?

The list refreshes periodically as the company graph is re-checked. This page's figures were pulled on September 20, 2026.

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About this data

RevenueBase is a B2B data infrastructure company. Its company graph covers 60 million companies and 398.9 million professional contacts, with emails verified on a rolling cadence rather than scraped once and left to decay. These company lists are generated directly from that graph with RevenueBase SmartSearch, the same natural-language company search every RevenueBase user has: describe a market in plain words, get the companies that match, and add verified emails and direct dials for the people at them. It is the same data that powers RevenueBase's B2B data products, and a free account includes 500 credits to start. How these lists are built and judged.