Company lists · Data refreshed September 2026

Top 25 Ex vivo gene therapy companies worldwide

RevenueBase identified 274 ex vivo gene therapy companies worldwide as of September 2026 and tracks 12,460 professional contacts across them, including 6,380 with verified work emails and 0 with mobile numbers. The United States is the largest market and Cambridge the largest hub.

This list covers ex vivo gene therapy companies worldwide, matched on what each company actually does as described in its own words. Ranked by team size, largest first. Every row shows the company's own description, its RevenueBase Smart Search rating, and when it was last checked. Data refreshed September 19, 2026. Country and city lists for ex vivo gene therapy companies follow the table.

Published by RevenueBase, a B2B data infrastructure company. This list was built with RevenueBase Smart Search, the natural-language company search RevenueBase customers use to build their own targeted lists and unlock verified emails and direct dials at the companies on them. How these lists are built and judged.

How to read this list HQ checked on every row RevenueBase Smart Search rating on every row Refreshed Sep 19, 2026 86% judged on-target in blind review
274Companies
12,460Contacts tracked
6,380Verified emails
0Mobile numbers
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The 25 largest ex vivo gene therapy companies worldwide

Ranked by team size
Top 25 of 274 ex vivo gene therapy companies worldwide, ranked by team size, largest first. Data refreshed Sep 19, 2026. RevenueBase Smart Search rates how each company's information relates to ex vivo gene therapy companies: strong evidence (its own description names it), partial (names part of it), indirect (matched on the rest of its profile rather than the description shown). Click a contact count to view that company's people.
#CompanyRevenueBase Smart SearchHeadquartersEmployeesContacts
1Strong evidenceResearch Triangle Park, NC, United StatesHQ checked Sep 19, 2026501-1,000510 contacts →

Strong evidence

“AskBio Inc, a wholly owned and independently operated subsidiary of Bayer AG, is a fully integrated gene therapy company dedicated to developing life-saving medicines and changing…”

Source: RevenueBase Database · checked Sep 19, 2026
2Strong evidenceCambridge, MA, United StatesHQ checked Sep 19, 2026201-500474 contacts →

Strong evidence

“Intellia Therapeutics is a leading clinical-stage biopharmaceutical company focused on revolutionizing medicine leveraging CRISPR gene editing and other core technologies.”

Source: RevenueBase Database · checked Sep 19, 2026
3Strong evidenceColumbus, OH, United StatesHQ checked Sep 19, 2026201-500456 contacts →

Strong evidence

“Forge, a member of Ajinomoto Bio-Pharma Services, is a gene therapy development engine, focused on enabling access to life changing gene therapies and helping bring them from idea…”

Source: RevenueBase Database · checked Sep 19, 2026
4Indirect evidenceLondon/new York, United KingdomHQ checked Sep 19, 202651-200398 contacts →

Indirect evidence

“MeiraGTx (Nasdaq: MGTX) is a vertically integrated, clinical-stage genetic medicine company with a broad pipeline of late-stage clinical programs supported by end-to-end…”

Source: RevenueBase Database · checked Sep 19, 2026
5Strong evidenceRockville, MD, United StatesHQ checked Sep 19, 2026201-500393 contacts →

Strong evidence

“REGENXBIO is a leading clinical-stage biotechnology company seeking to improve lives through the curative potential of gene therapy.”

Source: RevenueBase Database · checked Sep 19, 2026
6Partial evidenceAbingdon, United KingdomHQ checked Sep 19, 2026201-500313 contacts →

Partial evidence

“Adaptimmune is a fully integrated cell therapy company, designed and built from the ground up with four U.K- and U.S-based biotechnology hub locations.”

Source: RevenueBase Database · checked Sep 19, 2026
7Indirect evidenceThe Woodlands, TX, United StatesHQ checked Sep 19, 202651-200311 contacts →

Indirect evidence

“Corporate Overview Lexicon Pharmaceuticals is a biopharmaceutical company that has harnessed the power of genetics for drug discovery.”

Source: RevenueBase Database · checked Sep 19, 2026
8Indirect evidenceSeattle, WA, United StatesHQ checked Sep 19, 2026201-500287 contacts →

Indirect evidence

“Sana Biotechnology is focused on utilizing engineered cells as medicines for patients.”

Source: RevenueBase Database · checked Sep 19, 2026
9Partial evidenceBrisbane, CA, AustraliaHQ checked Sep 19, 2026201-500270 contacts →

Partial evidence

“For Sangamo Therapeutics, science is a means to develop new medicines with the potential to transform the lives of patients living with serious genetic diseases.”

Source: RevenueBase Database · checked Sep 19, 2026
10Strong evidenceCranbury, NJ, United StatesHQ checked Sep 19, 2026201-500258 contacts →

Strong evidence

“Rocket Pharma (NASDAQ: RCKT) is a fully-integrated, clinical-stage company seeking gene therapy cures.”

Source: RevenueBase Database · checked Sep 19, 2026
11Partial evidenceSan Diego, CA, United StatesHQ checked Sep 19, 202651-200237 contacts →

Partial evidence

“Capricor Therapeutics is a publicly traded (NASDAQ: CAPR) biotechnology company with a mission to develop groundbreaking therapies that make a meaningful impact on patients’ lives.”

Source: RevenueBase Database · checked Sep 19, 2026
12Partial evidenceEmeryville, CA, United StatesHQ checked Sep 19, 202651-200236 contacts →

Partial evidence

“4DMT is a leading late-stage biotechnology company advancing durable and disease-targeted therapeutics with potential to transform treatment paradigms and provide unprecedented…”

Source: RevenueBase Database · checked Sep 19, 2026
13Strong evidenceLondon, United KingdomHQ checked Sep 19, 202651-200221 contacts →

Strong evidence

“Orchard Therapeutics, a Kyowa Kirin company, is a global gene therapy leader focused on ending the devastation caused by genetic and other severe diseases by discovering…”

Source: RevenueBase Database · checked Sep 19, 2026
14Indirect evidenceMorrisville, NC, United StatesHQ checked Sep 19, 202651-200211 contacts →

Indirect evidence

“Our mission is to revolutionize medicine, with the ultimate goal of eliminating human suffering and enabling people to live without the burden of disease.”

Source: RevenueBase Database · checked Sep 19, 2026
15Partial evidenceLexington, MA, United StatesHQ checked Sep 19, 202651-200208 contacts →

Partial evidence

“Voyager Therapeutics, Inc.(Nasdaq: VYGR) is a biotechnology company dedicated to leveraging the power of human genetics to modify the course of – and ultimately cure –…”

Source: RevenueBase Database · checked Sep 19, 2026
16Partial evidenceCleveland, OH, United StatesHQ checked Sep 19, 2026201-500207 contacts →

Partial evidence

“Abeona Therapeutics Inc.”

Source: RevenueBase Database · checked Sep 19, 2026
17Partial evidenceEmeryville, CA, United StatesHQ checked Sep 19, 202651-200200 contacts →

Partial evidence

“Metagenomi is a precision genetic medicines company committed to developing curative therapeutics for patients using our proprietary, comprehensive metagenomics-derived genome…”

Source: RevenueBase Database · checked Sep 19, 2026
18Partial evidenceThousand Oaks, CA, United StatesHQ checked Sep 19, 2026201-500194 contacts →

Partial evidence

“Atara Biotherapeutics Inc, is a leading allogeneic T-cell immunotherapy company pioneering the development of transformative off-the-shelf therapies for patients with serious…”

Source: RevenueBase Database · checked Sep 19, 2026
19Partial evidenceBoston, MA, United StatesHQ checked Sep 19, 2026201-500189 contacts →

Partial evidence

“Verve Therapeutics, a wholly owned subsidiary of Eli Lilly and Company, is developing a new class of genetic medicines for cardiovascular disease with the potential to transform…”

Source: RevenueBase Database · checked Sep 19, 2026
20Partial evidenceBrisbane, CA, AustraliaHQ checked Sep 19, 202651-200178 contacts →

Partial evidence

“Mammoth Biosciences is a biotechnology company focused on leveraging its proprietary ultracompact CRISPR systems to develop long-term curative therapies, as well as other…”

Source: RevenueBase Database · checked Sep 19, 2026
21Strong evidenceRedwood City, CA, United StatesHQ checked Sep 19, 202651-200177 contacts →

Strong evidence

“Adverum Biotechnologies (NASDAQ: ADVM) is a clinical-stage company that aims to establish gene therapy as a new standard of care for highly prevalent ocular diseases with the…”

Source: RevenueBase Database · checked Sep 19, 2026
22Indirect evidenceSan Diego, CA, United StatesHQ checked Sep 19, 2026201-500172 contacts →

Indirect evidence

“Poseida was acquired by Roche in early 2025 and is now part of the Roche Group.”

Source: RevenueBase Database · checked Sep 19, 2026
23Partial evidenceSouth San Francisco, CA, United StatesHQ checked Sep 19, 202651-200167 contacts →

Partial evidence

“Nkarta is a clinical-stage biotechnology company advancing the development of allogeneic natural killer (NK) cell therapies.”

Source: RevenueBase Database · checked Sep 19, 2026
24Strong evidenceBoston, MA, United StatesHQ checked Sep 19, 202651-200160 contacts →

Strong evidence

“Solid Biosciences is a precision genetic medicine company focused on advancing a portfolio of gene therapy candidates targeting rare neuromuscular and cardiac diseases, including…”

Source: RevenueBase Database · checked Sep 19, 2026
25Strong evidencePhiladelphia, PA, United StatesHQ checked Sep 19, 202651-200155 contacts →

Strong evidence

“Century Therapeutics is an innovative biotechnology company that is building an industry-leading, allogeneic, iPSC-derived cell therapy platform that integrates cutting-edge gene…”

Source: RevenueBase Database · checked Sep 19, 2026

Showing 25 of 274 ex vivo gene therapy companies worldwide

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Ex vivo gene therapy companies worldwide at a glance

As of Sep 19, 2026
51.2%Verified-email coverage
45.5Average contacts per company
11-50Median size (employees)
9.5%Largest-city concentration · Cambridge
Sep 19, 2026Page data refreshed

Companies by employee count

1-10
105
11-50
83
51-200
62
201-500
17
501-1,000
5
1,001-5,000
1
10001+
1

How this list was built

Company categories are rarely black and white. RevenueBase reads each company's own description of its business to decide whether it belongs among ex vivo gene therapy companies, so some rows will be adjacent to the category rather than pure plays. The description and RevenueBase Smart Search rating on every row are there so you can check each match yourself.

Source
The RevenueBase company graph: 60 million companies and 398.9 million professional contacts resolved from primary sources, queried with RevenueBase Smart Search, the natural-language company search available to every RevenueBase user.
Coverage
2 countries, largest first: the United States, the United Kingdom. Country and city lists for ex vivo gene therapy companies are linked below.
What qualifies
Companies worldwide whose own description of what they do matches “ex vivo gene therapy companies”. Matching reads each company's description, not its industry code or its name.
RevenueBase Smart Search
RevenueBase Smart Search is how this list is assembled and how each row is rated. RevenueBase's data engine and AI assess a company's LinkedIn profile, information supplied directly by the company, its website and other publicly available information, then relate it to a category defined in a user's own words. Each row is rated strong evidence (its own description names ex vivo gene therapy companies), partial evidence (it names part of the category) or indirect evidence (the description shown names none of it and the match rests on the rest of the company's profile). The description supporting each rating is quoted on the row.
What we exclude
Companies whose own description does not clearly place them among ex vivo gene therapy companies, and records with no verified work email.
Match quality
In blind human judging of this matching method, 86% of matched companies were on target. Expect roughly 1 in 7 rows to be adjacent to the category rather than a pure play. Every row shows the company's own description and its RevenueBase Smart Search rating so you can judge each match yourself. Read the full methodology: how the lists are built, how the judging worked, and what the figure means.
Ranking
Team size, largest first: companies are ordered by the number of professionals RevenueBase tracks at each one. Employee ranges shown are reported bands, for context.
Verification
Every listed company carries at least one verified work email, 6,380 across the full list. Contacts re-verify on a rolling cadence, and each contact's own verification date is shown inside RevenueBase.
Refresh
This page's figures were pulled from the company graph on September 19, 2026. Lists refresh periodically as the graph is re-checked.
Corrections
Wrong category, wrong headquarters, or a company that has closed? Use “Report an issue” on any row. Reports go to the RevenueBase Data Team and feed back into the company graph.

Ex vivo gene therapy companies by location

2 lists · largest first

Every Ex vivo gene therapy companies list RevenueBase publishes, by country and city. Counts are matching companies in each list as of its own refresh date.

Countries

Frequently asked

What is RevenueBase Smart Search?

RevenueBase Smart Search is how RevenueBase decides which companies belong on this list and how strongly each one fits. Its data engine and AI assess a company's LinkedIn profile, information supplied directly by the company, its website and other publicly available information, then relate it to the category the list is about. Each row is rated strong evidence when the company's own description names ex vivo gene therapy companies, partial evidence when it names part of the category, and indirect evidence when the description shown names none of it and the match rests on the rest of the company's profile.

How many ex vivo gene therapy companies are there worldwide?

RevenueBase identified 274 ex vivo gene therapy companies worldwide as of September 2026, matched on each company's own description of what it does rather than its industry code.

What is the largest company on this list?

Askbio INC, headquartered in Research Triangle Park, tops this list with the largest team on record.

Which country has the most ex vivo gene therapy companies?

The United States leads with 249 companies, followed by the United Kingdom (25). Every ex vivo gene therapy companies list by country and city is linked on this page.

Which city has the most ex vivo gene therapy companies?

Cambridge leads with 26 headquartered companies, followed by Boston (16) and Philadelphia (12).

How do I get contact information for these companies?

A free RevenueBase account lets you run this exact search and work the top results, verified emails and direct dials included. Upgrading unlocks all 6,380 verified decision-maker contacts tracked across these 274 companies.

How current is this list?

The list refreshes periodically as the company graph is re-checked. This page's figures were pulled on September 19, 2026.

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About this data

RevenueBase is a B2B data infrastructure company. Its company graph covers 60 million companies and 398.9 million professional contacts, with emails verified on a rolling cadence rather than scraped once and left to decay. These company lists are generated directly from that graph with RevenueBase Smart Search, the same natural-language company search every RevenueBase user has: describe a market in plain words, get the companies that match, and add verified emails and direct dials for the people at them. It is the same data that powers RevenueBase's B2B data products, and a free account includes 500 credits to start. How these lists are built and judged.